Table 3.

Patient outcomes

OutcomeStudy population (n = 20)
Response at 1 mo  
 Complete response 12 (60%) 
 Partial response 3 (15%) 
 Stable disease 3 (15%) 
 Progressive disease 1 (5%) 
 Unknown 1 (5%) 
Best response  
 Complete response 15 (75%) 
 Partial response 1 (5%) 
 Stable disease 1 (5%) 
 Progressive disease 3 (15%) 
Acute GVHD 17 (85%) 
Chronic GVHD 9 (45%) 
PFS, median, y 1.57 (95 CI, 0.22-6.94) 
OS, median, y 6.45 (1.10 lower limit; upper limit does not exist) 
OutcomeStudy population (n = 20)
Response at 1 mo  
 Complete response 12 (60%) 
 Partial response 3 (15%) 
 Stable disease 3 (15%) 
 Progressive disease 1 (5%) 
 Unknown 1 (5%) 
Best response  
 Complete response 15 (75%) 
 Partial response 1 (5%) 
 Stable disease 1 (5%) 
 Progressive disease 3 (15%) 
Acute GVHD 17 (85%) 
Chronic GVHD 9 (45%) 
PFS, median, y 1.57 (95 CI, 0.22-6.94) 
OS, median, y 6.45 (1.10 lower limit; upper limit does not exist) 

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