Current limitations of thalassemia care
| Limitation . | Potential solutions . |
|---|---|
| Regular transfusion appointments | Reduce transfusion requirement Stem cell transplantation |
| Iron overload | Reduce transfusion requirement Block intestinal iron absorption Escalate chelation |
| Iron chelator toxicity | Reduce transfusion requirement Block intestinal iron absorption Additional chelation options |
| Lack of allogeneic stem cell donor | Genetically modified autologous transplantation Nontransplant therapies that preclude desirability of transplant |
| Limitation . | Potential solutions . |
|---|---|
| Regular transfusion appointments | Reduce transfusion requirement Stem cell transplantation |
| Iron overload | Reduce transfusion requirement Block intestinal iron absorption Escalate chelation |
| Iron chelator toxicity | Reduce transfusion requirement Block intestinal iron absorption Additional chelation options |
| Lack of allogeneic stem cell donor | Genetically modified autologous transplantation Nontransplant therapies that preclude desirability of transplant |