Table 3.

Actively enrolling clinical trials

NCT No.TitleDrugEnrollmentRandomizationStudy phase
NCT03593915 A Phase 1b/2 Study of Alvocidib Plus Decitabine in Patients With MDS Decitabine 49 None 1| 2 
NCT03045510 Efficacy and Safety of Ultra Small Dose Decitabine for the Lower Risk MDS Patients With Transfusion Dependent Decitabine 50 None 
NCT02781883 Clinical Trial of BP1001(Liposomal Grb2 Antisense Oligonucleotide) in Combination With Decitabine in AML / High Risk MDS Decitabine 108 None 
NCT03855371 Mutant p53-based Personalized Trial Using Decitabine and Arsenic Trioxide on AML/MDS Decitabine None 
NCT02269280 Phase II Decitabine (DAC) Versus Azacitidine (AZA) in Myelodysplastic Syndrome (MDS) Decitabine/Azacitidine 240 Yes 
NCT03066648 Study of PDR001 and/or MBG453 in Combination With Decitabine in Patients With AML or High Risk MDS Decitabine/Azacitidine 235 None 
NCT01211457 Study of Sapacitabine in Acute Myeloid Leukemia (AML) or Myelodysplastic Syndromes (MDS) Decitabine 65 None 1|2 
NCT01515527 Cladribine Plus Low Dose Cytarabine (LDAC) Alternating With Decitabine in Patients With Acute Myeloid Leukemia (AML) or High-Risk Myelodysplastic Syndrome (MDS) Decitabine 160 None 
NCT03502668 Phase 1-2 Study of Low Dose ASTX727 (ASTX727 LD) in Lower Risk MDS Decitabine 160 Yes 1|2 
NCT02890329 Ipilimumab and Decitabine in Treating Patients With Relapsed or Refractory Myelodysplastic Syndrome or Acute Myeloid Leukemia Decitabine 48 None 
NCT03358719 DEC-205/NY-ESO-1 Fusion Protein CDX-1401, Poly ICLC, Decitabine, and Nivolumab in Treating Patients With Myelodysplastic Syndrome or Acute Myeloid Leukemia Decitabine 18 None 
NCT03946670 A Study of MBG453 in Combination With Hypomethylating Agents in Subjects With IPSS-R Intermediate, High or Very High Risk Myelodysplastic Syndrome (MDS). Decitabine/Azacitidine 120 Yes 
NCT03404193 Venetoclax in Combination With Decitabine in r/r AML and MDS Decitabine 280 None 
NCT03661307 Quizartinib, Decitabine, and Venetoclax in Treating Participants With Untreated or Relapsed Acute Myeloid Leukemia or High Risk Myelodysplastic Syndrome Decitabine/Azacitidine 52 None 1|2 
NCT03356080 DLAAG in the Treatment of Acute Myeloid Leukemia (AML) and Myelodysplastic Syndrome With Blast Excess Decitabine 50 None 
NCT04013880 ASTX727 and FT-2102 in Treating IDH1-Mutated Recurrent/Refractory Myelodysplastic Syndrome or Acute Myeloid Leukemia Decitabine 80 None 1|2 
NCT03906695 Phase 1 Trial of ASTX727 in Subjects With Lower-risk Myelodysplastic Syndromes Decitabine 30 None 
NCT03745716 APR-246 & Azacitidine for the Treatment of TP53 Mutant Myelodysplastic Syndromes (MDS) Azacitidine 156 Yes 
NCT02942290 A Study Evaluating Venetoclax in Combination With Azacitidine in Subjects With Treatment-Naive Higher-Risk Myelodysplastic Syndromes (MDS) Azacitidine 80 None 
NCT02985190 A Study of Azacitidine in Myelodysplastic Syndrome (MDS) Associated to Systemic Auto-immune and Inflammatory Disorders Azacitidine 30 None 
NCT03978364 A Study of Azacitidine with or without homoharringtonine for Patients With Int/High -Risk MDS and AML-MRC Azacitidine 100 Yes 
NCT03113643 SL-401 in Combination With Azacitidine or Azacitidine/Venetoclax in Acute Myeloid Leukemia (AML) or High-Risk Myelodysplastic Syndrome (MDS) Azacitidine 56 None 
NCT02530463 Nivolumab and Ipilimumab With 5-azacitidine in Patients With Myelodysplastic Syndromes (MDS) Azacitidine 120 None 
NCT03564873 Omacetaxine + Azacitidine in Untreated Patients With High Grade MDS Azacitidine 51 None 1|2 
NCT03094637 Azacitidine and Pembrolizumab in Treating Patients With Myelodysplastic Syndrome Azacitidine 40 None 
NCT03338348 Study of Vosaroxin With Azacitidine in Patients With Newly Diagnosed Acute Myeloid Leukemia or Myelodysplastic Syndrome With Excess Blasts-2 Azacitidine 168 None 
NCT02750995 Peptide Vaccination in Combination With Azacitidine for Patients With MDS and AML Azacitidine 15 None 
NCT03217903 High Risk Myelodysplasia Treated by Azacytidine: Genetic and Epigenetic (MYRAGE) Azacitidine 32 None Not applicable 
NCT02719574 Open-label Study of FT-2102 With or Without Azacitidine or Cytarabine in Patients With AML or MDS With an IDH1 Mutation Azacitidine 500 Yes 1|2 
NCT02319369 Safety, Tolerability and Pharmacokinetics of Milademetan Alone and With 5-Azacitidine (AZA) in Acute Myelogenous Leukemia (AML) or High-Risk Myelodysplastic Syndrome (MDS) Azacitidine 156 None 
NCT03268954 Pevonedistat Plus Azacitidine Versus Single-Agent Azacitidine as First-Line Treatment for Participants With Higher-Risk Myelodysplastic Syndromes (HR MDS), Chronic Myelomonocytic Leukemia (CMML), or Low-Blast Acute Myelogenous Leukemia (AML) Azacitidine 450 Yes 
NCT02807558 A Biomarker-Directed phase 2 Trial of SY-1425 in Patients With Acute Myeloid Leukemia or Myelodysplastic Syndrome Azacitidine 162 None 
NCT03397173 TET2 Mutations in Myelodysplastic Syndromes and Acute Myeloid Leukemia With Azacitidine + Ascorbic Acid Azacitidine 28 None 
NCT02553941 Ibrutinib and Azacitidine for Treatment of Higher Risk Myelodysplastic Syndrome Azacitidine 24 None 
NCT04022785 PLX51107 and Azacitidine in Treating Patients With Acute Myeloid Leukemia or Myelodysplastic Syndrome Azacitidine 32 None 
NCT03814005 A Study of Pevonedistat in Combination With Azacitidine in Participants With Higher-risk Myelodysplastic Syndromes (HR MDS), Chronic Myelomonocytic Leukemia (CMML), or Acute Myelogenous Leukemia (AML) With Severe Renal Impairment or Mild Hepatic Impairment Azacitidine 60 None 
NCT03047993 Glutaminase Inhibitor CB-839 and Azacitidine in Treating Patients With Advanced Myelodysplastic Syndrome Azacitidine 40 None 1|2 
NCT03248479 Hu5F9-G4 Monotherapy or Hu5F9-G4 in Combination With Azacitidine in Patients With Hematological Malignancies Azacitidine 96 None 
NCT03383575 Azacitidine and Enasidenib in Treating Patients With IDH2-Mutant Myelodysplastic Syndrome Azacitidine 105 None 
NCT03999723 Combining Active and Passive DNA Hypomethylation (Azacitidine and Vitamin C) in MDS, CMML, AML Azacitidine 182 Yes 
NCT03873311 Azacytidine + HAG Regimen in Elderly Patients With Myeloid Malignancy. Azacitidine 120 None 
NCT01812252 Chemotherapy in Treating Patients With Myelodysplastic Syndrome Before Donor Stem Cell Transplant Decitabine/Azacitidine 60 Yes 
NCT01787487 Ruxolitinib Phosphate and Azacytidine in Treating Patients With Myelofibrosis or Myelodysplastic Syndrome/Myeloproliferative Neoplasm Azacitidine 125 None 
NCT02981615 Phase 3 Multicenter Randomized Double-blind Placebo Controlled Study With Antibacterial Prophylaxis in Azacitidine Treated MDS Patients Azacitidine 170 Yes 
NCT03493646 Evaluating in Vivo AZA Incorporation in Mononuclear Cells Following Vidaza or CC486 Azacitidine 60 None 
NCT03326310 Study of MEK Inhibitor Selumetinib in Combination With Azacitidine in Patients With Higher Risk Chronic Myeloid Neoplasia Azacitidine 18 None 
NCT03358719 DEC-205/NY-ESO-1 Fusion Protein CDX-1401, Poly ICLC, Decitabine, and Nivolumab in Treating Patients With Myelodysplastic Syndrome or Acute Myeloid Leukemia Azacitidine 18 None 
NCT03471260 Ivosidenib and Venetoclax With or Without Azacitidine in Treating Participants With IDH1 Mutated Hematologic Malignancies Azacitidine 48 None 1|2 
NCT02038777 A Study Of PF-04449913 In Japanese Patients With Select Hematologic Malignancies Azacitidine 49 None 
NCT No.TitleDrugEnrollmentRandomizationStudy phase
NCT03593915 A Phase 1b/2 Study of Alvocidib Plus Decitabine in Patients With MDS Decitabine 49 None 1| 2 
NCT03045510 Efficacy and Safety of Ultra Small Dose Decitabine for the Lower Risk MDS Patients With Transfusion Dependent Decitabine 50 None 
NCT02781883 Clinical Trial of BP1001(Liposomal Grb2 Antisense Oligonucleotide) in Combination With Decitabine in AML / High Risk MDS Decitabine 108 None 
NCT03855371 Mutant p53-based Personalized Trial Using Decitabine and Arsenic Trioxide on AML/MDS Decitabine None 
NCT02269280 Phase II Decitabine (DAC) Versus Azacitidine (AZA) in Myelodysplastic Syndrome (MDS) Decitabine/Azacitidine 240 Yes 
NCT03066648 Study of PDR001 and/or MBG453 in Combination With Decitabine in Patients With AML or High Risk MDS Decitabine/Azacitidine 235 None 
NCT01211457 Study of Sapacitabine in Acute Myeloid Leukemia (AML) or Myelodysplastic Syndromes (MDS) Decitabine 65 None 1|2 
NCT01515527 Cladribine Plus Low Dose Cytarabine (LDAC) Alternating With Decitabine in Patients With Acute Myeloid Leukemia (AML) or High-Risk Myelodysplastic Syndrome (MDS) Decitabine 160 None 
NCT03502668 Phase 1-2 Study of Low Dose ASTX727 (ASTX727 LD) in Lower Risk MDS Decitabine 160 Yes 1|2 
NCT02890329 Ipilimumab and Decitabine in Treating Patients With Relapsed or Refractory Myelodysplastic Syndrome or Acute Myeloid Leukemia Decitabine 48 None 
NCT03358719 DEC-205/NY-ESO-1 Fusion Protein CDX-1401, Poly ICLC, Decitabine, and Nivolumab in Treating Patients With Myelodysplastic Syndrome or Acute Myeloid Leukemia Decitabine 18 None 
NCT03946670 A Study of MBG453 in Combination With Hypomethylating Agents in Subjects With IPSS-R Intermediate, High or Very High Risk Myelodysplastic Syndrome (MDS). Decitabine/Azacitidine 120 Yes 
NCT03404193 Venetoclax in Combination With Decitabine in r/r AML and MDS Decitabine 280 None 
NCT03661307 Quizartinib, Decitabine, and Venetoclax in Treating Participants With Untreated or Relapsed Acute Myeloid Leukemia or High Risk Myelodysplastic Syndrome Decitabine/Azacitidine 52 None 1|2 
NCT03356080 DLAAG in the Treatment of Acute Myeloid Leukemia (AML) and Myelodysplastic Syndrome With Blast Excess Decitabine 50 None 
NCT04013880 ASTX727 and FT-2102 in Treating IDH1-Mutated Recurrent/Refractory Myelodysplastic Syndrome or Acute Myeloid Leukemia Decitabine 80 None 1|2 
NCT03906695 Phase 1 Trial of ASTX727 in Subjects With Lower-risk Myelodysplastic Syndromes Decitabine 30 None 
NCT03745716 APR-246 & Azacitidine for the Treatment of TP53 Mutant Myelodysplastic Syndromes (MDS) Azacitidine 156 Yes 
NCT02942290 A Study Evaluating Venetoclax in Combination With Azacitidine in Subjects With Treatment-Naive Higher-Risk Myelodysplastic Syndromes (MDS) Azacitidine 80 None 
NCT02985190 A Study of Azacitidine in Myelodysplastic Syndrome (MDS) Associated to Systemic Auto-immune and Inflammatory Disorders Azacitidine 30 None 
NCT03978364 A Study of Azacitidine with or without homoharringtonine for Patients With Int/High -Risk MDS and AML-MRC Azacitidine 100 Yes 
NCT03113643 SL-401 in Combination With Azacitidine or Azacitidine/Venetoclax in Acute Myeloid Leukemia (AML) or High-Risk Myelodysplastic Syndrome (MDS) Azacitidine 56 None 
NCT02530463 Nivolumab and Ipilimumab With 5-azacitidine in Patients With Myelodysplastic Syndromes (MDS) Azacitidine 120 None 
NCT03564873 Omacetaxine + Azacitidine in Untreated Patients With High Grade MDS Azacitidine 51 None 1|2 
NCT03094637 Azacitidine and Pembrolizumab in Treating Patients With Myelodysplastic Syndrome Azacitidine 40 None 
NCT03338348 Study of Vosaroxin With Azacitidine in Patients With Newly Diagnosed Acute Myeloid Leukemia or Myelodysplastic Syndrome With Excess Blasts-2 Azacitidine 168 None 
NCT02750995 Peptide Vaccination in Combination With Azacitidine for Patients With MDS and AML Azacitidine 15 None 
NCT03217903 High Risk Myelodysplasia Treated by Azacytidine: Genetic and Epigenetic (MYRAGE) Azacitidine 32 None Not applicable 
NCT02719574 Open-label Study of FT-2102 With or Without Azacitidine or Cytarabine in Patients With AML or MDS With an IDH1 Mutation Azacitidine 500 Yes 1|2 
NCT02319369 Safety, Tolerability and Pharmacokinetics of Milademetan Alone and With 5-Azacitidine (AZA) in Acute Myelogenous Leukemia (AML) or High-Risk Myelodysplastic Syndrome (MDS) Azacitidine 156 None 
NCT03268954 Pevonedistat Plus Azacitidine Versus Single-Agent Azacitidine as First-Line Treatment for Participants With Higher-Risk Myelodysplastic Syndromes (HR MDS), Chronic Myelomonocytic Leukemia (CMML), or Low-Blast Acute Myelogenous Leukemia (AML) Azacitidine 450 Yes 
NCT02807558 A Biomarker-Directed phase 2 Trial of SY-1425 in Patients With Acute Myeloid Leukemia or Myelodysplastic Syndrome Azacitidine 162 None 
NCT03397173 TET2 Mutations in Myelodysplastic Syndromes and Acute Myeloid Leukemia With Azacitidine + Ascorbic Acid Azacitidine 28 None 
NCT02553941 Ibrutinib and Azacitidine for Treatment of Higher Risk Myelodysplastic Syndrome Azacitidine 24 None 
NCT04022785 PLX51107 and Azacitidine in Treating Patients With Acute Myeloid Leukemia or Myelodysplastic Syndrome Azacitidine 32 None 
NCT03814005 A Study of Pevonedistat in Combination With Azacitidine in Participants With Higher-risk Myelodysplastic Syndromes (HR MDS), Chronic Myelomonocytic Leukemia (CMML), or Acute Myelogenous Leukemia (AML) With Severe Renal Impairment or Mild Hepatic Impairment Azacitidine 60 None 
NCT03047993 Glutaminase Inhibitor CB-839 and Azacitidine in Treating Patients With Advanced Myelodysplastic Syndrome Azacitidine 40 None 1|2 
NCT03248479 Hu5F9-G4 Monotherapy or Hu5F9-G4 in Combination With Azacitidine in Patients With Hematological Malignancies Azacitidine 96 None 
NCT03383575 Azacitidine and Enasidenib in Treating Patients With IDH2-Mutant Myelodysplastic Syndrome Azacitidine 105 None 
NCT03999723 Combining Active and Passive DNA Hypomethylation (Azacitidine and Vitamin C) in MDS, CMML, AML Azacitidine 182 Yes 
NCT03873311 Azacytidine + HAG Regimen in Elderly Patients With Myeloid Malignancy. Azacitidine 120 None 
NCT01812252 Chemotherapy in Treating Patients With Myelodysplastic Syndrome Before Donor Stem Cell Transplant Decitabine/Azacitidine 60 Yes 
NCT01787487 Ruxolitinib Phosphate and Azacytidine in Treating Patients With Myelofibrosis or Myelodysplastic Syndrome/Myeloproliferative Neoplasm Azacitidine 125 None 
NCT02981615 Phase 3 Multicenter Randomized Double-blind Placebo Controlled Study With Antibacterial Prophylaxis in Azacitidine Treated MDS Patients Azacitidine 170 Yes 
NCT03493646 Evaluating in Vivo AZA Incorporation in Mononuclear Cells Following Vidaza or CC486 Azacitidine 60 None 
NCT03326310 Study of MEK Inhibitor Selumetinib in Combination With Azacitidine in Patients With Higher Risk Chronic Myeloid Neoplasia Azacitidine 18 None 
NCT03358719 DEC-205/NY-ESO-1 Fusion Protein CDX-1401, Poly ICLC, Decitabine, and Nivolumab in Treating Patients With Myelodysplastic Syndrome or Acute Myeloid Leukemia Azacitidine 18 None 
NCT03471260 Ivosidenib and Venetoclax With or Without Azacitidine in Treating Participants With IDH1 Mutated Hematologic Malignancies Azacitidine 48 None 1|2 
NCT02038777 A Study Of PF-04449913 In Japanese Patients With Select Hematologic Malignancies Azacitidine 49 None 
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