Patient characteristics
| Characteristic . | Total cohort (N = 304) . | Moderate hemophilia (n = 70) . | Mild hemophilia (n = 234) . |
|---|---|---|---|
| Age, y | 38 (25-49) | 39 (26-48) | 37 (25-49) |
| Hemophilia type | |||
| Hemophilia A | 248 (82) | 55 (79) | 193 (82) |
| Hemophilia B | 56 (18) | 15 (21) | 41 (18) |
| Baseline factor activity, IU/mL | 0.12 (0.05-0.21) | 0.03 (0.02-0.04) | 0.15 (0.09-0.22) |
| Blood group | |||
| O | 92 (30) | 29 (41) | 63 (27) |
| Non-O | 104 (34) | 18 (26) | 86 (37) |
| Unknown | 108 (36) | 23 (33) | 85 (36) |
| Body mass index, kg/m2* | 25 (22-28) | 26 (23-29) | 24 (22-28) |
| VWF activity level, IU/mL† | 0.92 (0.73-1.15) | 1.06 (0.75-1.15) | 0.90 (0.73-1.15) |
| Family history of hemophilia | |||
| Positive | 236 (78) | 58 (83) | 178 (76) |
| Negative | 25 (8) | 2 (3) | 23 (10) |
| Unknown | 43 (14) | 10 (14) | 33 (14) |
| Treatment regimen | |||
| Prophylaxis | 12 (4) | 10 (14) | 2 (1) |
| Intermittent prophylaxis | 6 (2) | 4 (6) | 2 (1) |
| On-demand | 286 (94) | 56 (80) | 230 (98) |
| History of prophylaxis | |||
| Yes | 28 (9) | 23 (33) | 5 (2) |
| No | 260 (86) | 44 (63) | 216 (92) |
| Unknown | 16 (5) | 3 (4) | 13 (6) |
| Characteristic . | Total cohort (N = 304) . | Moderate hemophilia (n = 70) . | Mild hemophilia (n = 234) . |
|---|---|---|---|
| Age, y | 38 (25-49) | 39 (26-48) | 37 (25-49) |
| Hemophilia type | |||
| Hemophilia A | 248 (82) | 55 (79) | 193 (82) |
| Hemophilia B | 56 (18) | 15 (21) | 41 (18) |
| Baseline factor activity, IU/mL | 0.12 (0.05-0.21) | 0.03 (0.02-0.04) | 0.15 (0.09-0.22) |
| Blood group | |||
| O | 92 (30) | 29 (41) | 63 (27) |
| Non-O | 104 (34) | 18 (26) | 86 (37) |
| Unknown | 108 (36) | 23 (33) | 85 (36) |
| Body mass index, kg/m2* | 25 (22-28) | 26 (23-29) | 24 (22-28) |
| VWF activity level, IU/mL† | 0.92 (0.73-1.15) | 1.06 (0.75-1.15) | 0.90 (0.73-1.15) |
| Family history of hemophilia | |||
| Positive | 236 (78) | 58 (83) | 178 (76) |
| Negative | 25 (8) | 2 (3) | 23 (10) |
| Unknown | 43 (14) | 10 (14) | 33 (14) |
| Treatment regimen | |||
| Prophylaxis | 12 (4) | 10 (14) | 2 (1) |
| Intermittent prophylaxis | 6 (2) | 4 (6) | 2 (1) |
| On-demand | 286 (94) | 56 (80) | 230 (98) |
| History of prophylaxis | |||
| Yes | 28 (9) | 23 (33) | 5 (2) |
| No | 260 (86) | 44 (63) | 216 (92) |
| Unknown | 16 (5) | 3 (4) | 13 (6) |