Table 4.

Estimated OS and EFS for whole cohort and IEI subgroups

GroupNOSNEFS
6 mo (95% CI)1 y (95% CI)5 y (95% CI)6 mo (95% CI)1 y (95% CI)5 y (95% CI)
Whole cohort 329 83% (79-87) 78% (74-83) 71% (66-76) 319 70% (65-75) 65% (60-71) 62% (56-67) 
CID 163 80% (74-86) 76% (69-83) 68% (61-76) 157 68% (61-75) 64% (56-71) 58% (50-67) 
PD∗ 127 93% (88-97) 87% (81-93) 78% (71-86) 123 77% (70-85) 72% (64-80) 69% (61-77) 
CGD alone† 83 92% (86-98%) 83% (75-91%) 77% (67-86%) 80 74% (64-83%) 69% (59-79%) 67% (57-78%) 
PAD‡ 39 64% (49-79) 59% (44-74) 59% (44-74) 39 54% (38-69) 51% (36-67) 51% (36-67) 
CVID alone§ 27 56% (37-74) 48% (29-67) 48% (29-67) 27 44% (26-63) 41% (22-59) 41% (22-59) 
GroupNOSNEFS
6 mo (95% CI)1 y (95% CI)5 y (95% CI)6 mo (95% CI)1 y (95% CI)5 y (95% CI)
Whole cohort 329 83% (79-87) 78% (74-83) 71% (66-76) 319 70% (65-75) 65% (60-71) 62% (56-67) 
CID 163 80% (74-86) 76% (69-83) 68% (61-76) 157 68% (61-75) 64% (56-71) 58% (50-67) 
PD∗ 127 93% (88-97) 87% (81-93) 78% (71-86) 123 77% (70-85) 72% (64-80) 69% (61-77) 
CGD alone† 83 92% (86-98%) 83% (75-91%) 77% (67-86%) 80 74% (64-83%) 69% (59-79%) 67% (57-78%) 
PAD‡ 39 64% (49-79) 59% (44-74) 59% (44-74) 39 54% (38-69) 51% (36-67) 51% (36-67) 
CVID alone§ 27 56% (37-74) 48% (29-67) 48% (29-67) 27 44% (26-63) 41% (22-59) 41% (22-59) 

PD including CGD.

Subset of PD.

PAD including CVID.

§

Subset of PAD.

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