Table 1.

Summary of patients who died after HSCT

Patient IDDiseaseRemission at HSCTDonorConditioningOnset to HSCT (d)Cause of death
07-01-001 FHL3 Complete MUD RT-MAC (Mel, dose na) 108 Reactivated HLH 
22-08-001 FHL2 No MRD RT-MAC (Treo 39 g/m2115 Infection 
22-09-002 CHS Complete Haplo (post-Cy) RT-MAC (Bu AUC 72 mg × h/L) 45 Infection 
22-16-001 FHL2 Complete Haplo (CD3 depl) RT-MAC (Treo 40 g/m295 HSCT related 
22-22-003 GS-2 Complete Haplo (αβ T depl) RT-MAC (Treo 37 g/m295 HSCT related 
22-28-001 FHL3 Complete MMUD RT-MAC (Treo 45 g/m2131 Infection 
22-35-001 FHL3 Partial MMUD RT-MAC (Treo 38 g/m260 Persistent HLH 
26-03-008 Undefined na Haplo (post-Cy) RT-MAC (Bu, dose na) na Persistent HLH 
26-03-009 FHL3 na Haplo (na) na na na 
Patient IDDiseaseRemission at HSCTDonorConditioningOnset to HSCT (d)Cause of death
07-01-001 FHL3 Complete MUD RT-MAC (Mel, dose na) 108 Reactivated HLH 
22-08-001 FHL2 No MRD RT-MAC (Treo 39 g/m2115 Infection 
22-09-002 CHS Complete Haplo (post-Cy) RT-MAC (Bu AUC 72 mg × h/L) 45 Infection 
22-16-001 FHL2 Complete Haplo (CD3 depl) RT-MAC (Treo 40 g/m295 HSCT related 
22-22-003 GS-2 Complete Haplo (αβ T depl) RT-MAC (Treo 37 g/m295 HSCT related 
22-28-001 FHL3 Complete MMUD RT-MAC (Treo 45 g/m2131 Infection 
22-35-001 FHL3 Partial MMUD RT-MAC (Treo 38 g/m260 Persistent HLH 
26-03-008 Undefined na Haplo (post-Cy) RT-MAC (Bu, dose na) na Persistent HLH 
26-03-009 FHL3 na Haplo (na) na na na 

AUC, area under the curve; Bu, busulfan; GS-2, Griscelli syndrome type 2; haplo, haploidentical; MMUD, mismatched unrelated donor; Mel, melphalan; MRD, matched related donor; MUD, matched unrelated donor; na, not available; RT-MAC, reduced-toxicity myeloablative conditioning; Treo, treosulfan.

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