Characteristics of participants with SCD
| . | Pre-HSCT (SCD) . | Post-HSCT . |
|---|---|---|
| Total N (%) | 6 | 5 |
| Sex | ||
| Male | 2 (33%) | 4 (80%) |
| Female | 4 (67%) | 1 (20%) |
| Age (median, range) | 41.5 (26-61) | 31 (19-54) |
| Hydroxyrea use (at time of study) | 4 (67%) | 0 |
| Type of transplant | ||
| Matched related donor | NA | 3 (60%) |
| Haploidentitical | NA | 2 (40%) |
| Stem cell donor genotype | ||
| AS | NA | 4 (80%) |
| AA | NA | 1 (20%) |
| Chimerism at time of enrollment | ||
| Full DMC | NA | 3 (60%) |
| Mixed DMC | NA | 2 (40%) |
| Hematologic data, average | ||
| WBC (K/mcL) | 8.9 | 6.9 |
| RBC (M/mcL) | 3 | 4.1 |
| Hemoglobin (g/dL) | 8.9 | 12.4 |
| Hematocrit (%) | 25.2 | 36.6 |
| MCV (fL) | 86 | 90.2 |
| Platelet count (K/mcL) | 406.4 | 277 |
| ARC (K/mcL) | 191.6 | 175 |
| HbF (%) | 10.2 | 1 |
| HbA (%) | 0 | 56.8 |
| HbA2 (%) | 3.7 | 3.1 |
| HbS (%) | 68.8 | 39.1 |
| HbC (%) | 43.3 | NA |
| AST (U/L) | 26.3 | 27.5 |
| Total bilirubin (mg/dL) | 1.7 | 1.2 |
| LDH (U/L) | 324.9 | 271.5 |
| Time from transplant mean ± SD (mo) | NA | 29.8 ± 17.3 |
| . | Pre-HSCT (SCD) . | Post-HSCT . |
|---|---|---|
| Total N (%) | 6 | 5 |
| Sex | ||
| Male | 2 (33%) | 4 (80%) |
| Female | 4 (67%) | 1 (20%) |
| Age (median, range) | 41.5 (26-61) | 31 (19-54) |
| Hydroxyrea use (at time of study) | 4 (67%) | 0 |
| Type of transplant | ||
| Matched related donor | NA | 3 (60%) |
| Haploidentitical | NA | 2 (40%) |
| Stem cell donor genotype | ||
| AS | NA | 4 (80%) |
| AA | NA | 1 (20%) |
| Chimerism at time of enrollment | ||
| Full DMC | NA | 3 (60%) |
| Mixed DMC | NA | 2 (40%) |
| Hematologic data, average | ||
| WBC (K/mcL) | 8.9 | 6.9 |
| RBC (M/mcL) | 3 | 4.1 |
| Hemoglobin (g/dL) | 8.9 | 12.4 |
| Hematocrit (%) | 25.2 | 36.6 |
| MCV (fL) | 86 | 90.2 |
| Platelet count (K/mcL) | 406.4 | 277 |
| ARC (K/mcL) | 191.6 | 175 |
| HbF (%) | 10.2 | 1 |
| HbA (%) | 0 | 56.8 |
| HbA2 (%) | 3.7 | 3.1 |
| HbS (%) | 68.8 | 39.1 |
| HbC (%) | 43.3 | NA |
| AST (U/L) | 26.3 | 27.5 |
| Total bilirubin (mg/dL) | 1.7 | 1.2 |
| LDH (U/L) | 324.9 | 271.5 |
| Time from transplant mean ± SD (mo) | NA | 29.8 ± 17.3 |
AST, aspartate transaminase; HbA, adult hemoglobin; HbA2, hemoglobin A2; HbC, hemoglobin C; HbS, sickle hemoglobin; MCV, mean corpuscular volume; TBI, total body irradiation; WBC, white blood cell count.