Table 1.

Patient characteristics

Characteristicsn (%)
No. of transplants 944 
No. of patients 874 
No. of transplants per patient  
807 
64 
Median age (range) at first transplant, y 3.11 (0.04-17.73) 
Recipient’s sex  
Male 534 (61.10) 
Diagnoses  
Acute leukemia 206 (23.57) 
Acute lymphoblastic leukemia 119 
Acute myeloid leukemia 82 
Mixed lineage leukemia 
Acute promyelocytic leukemia 
CML in blast crisis 
Other malignant hematological diseases 58 (6.64) 
Juvenile myelomonocytic leukemia 23 
Myelodysplastic syndrome 21 
Chronic myeloid leukemia 
Myeloproliferative disorder 
Lymphoma 
Nonfocal histiocytic sarcoma 
Primary immune deficiencies 355 (40.62) 
SCID 137 
Non-SCID 219 
Histiocytic disease 67 (7.67) 
Metabolic disease 72 (8.24) 
MPS I-II-VI 32 
Osteopetrosis 19 
ALD 10 
Alpha-mannosidosis 
Others 
Autoimmunity disorders 7 (0.80) 
Aplastic anemias 75 (8.58) 
Acquired aplastic anemia 32 
BM failure syndromes 43 
Fanconi anemia 17 
Severe congenital neutropenia 
Dyskeratosis congenita 
Diamond-Blackfan anemia 
Congenital amegakaryocytic thrombocytopenia 
Shwachman-Diamond syndrome 
Paroxysmal nocturnal hemoglobinuria 
Congenital BM failure (other/unspecified) 10 
Hemoglobinopathies 9 (1.03) 
Glanzmann thrombasthenia 6 (0.69) 
Gastroenterology 19 (2.17) 
Characteristicsn (%)
No. of transplants 944 
No. of patients 874 
No. of transplants per patient  
807 
64 
Median age (range) at first transplant, y 3.11 (0.04-17.73) 
Recipient’s sex  
Male 534 (61.10) 
Diagnoses  
Acute leukemia 206 (23.57) 
Acute lymphoblastic leukemia 119 
Acute myeloid leukemia 82 
Mixed lineage leukemia 
Acute promyelocytic leukemia 
CML in blast crisis 
Other malignant hematological diseases 58 (6.64) 
Juvenile myelomonocytic leukemia 23 
Myelodysplastic syndrome 21 
Chronic myeloid leukemia 
Myeloproliferative disorder 
Lymphoma 
Nonfocal histiocytic sarcoma 
Primary immune deficiencies 355 (40.62) 
SCID 137 
Non-SCID 219 
Histiocytic disease 67 (7.67) 
Metabolic disease 72 (8.24) 
MPS I-II-VI 32 
Osteopetrosis 19 
ALD 10 
Alpha-mannosidosis 
Others 
Autoimmunity disorders 7 (0.80) 
Aplastic anemias 75 (8.58) 
Acquired aplastic anemia 32 
BM failure syndromes 43 
Fanconi anemia 17 
Severe congenital neutropenia 
Dyskeratosis congenita 
Diamond-Blackfan anemia 
Congenital amegakaryocytic thrombocytopenia 
Shwachman-Diamond syndrome 
Paroxysmal nocturnal hemoglobinuria 
Congenital BM failure (other/unspecified) 10 
Hemoglobinopathies 9 (1.03) 
Glanzmann thrombasthenia 6 (0.69) 
Gastroenterology 19 (2.17) 

ALD, adrenoleukodystrophy; BM, bone marrow; MPS, mucopolysaccharidosis; SCID, severe combined immunodeficiency.

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