Patient characteristics
| No. of patients | N = 100 |
| Age at diagnosis | |
| Years, median (range) | 10.9 (1.4-17.3) |
| Gender, n (%) | |
| Male | 54 (54) |
| Female | 46 (46) |
| Blood count at diagnosis | |
| Hb | |
| g/dL, median (range), n = 92 | 10.5 (3.9-16) |
| n (%) | |
| ≥12 g/dL | 24 (24) |
| 10 to <12 g/dL | 35 (35) |
| 7 to <10 g/dL | 20 (20) |
| <7 g/dL | 13 (13) |
| RBC transfused, no data on Hb before transfusion | 7 (7) |
| Not evaluable (no data about transfusion) | 1 (1) |
| White blood cell count | |
| × 109/L, median (range), n = 99 | 3.5 (0.3-7.7) |
| ANCs | |
| × 109/L, median (range), n = 92 | 1.1 (0-4.8) |
| n (%) | |
| ≥1.5 × 109/L | 28 (28) |
| 1.0 to <1.5 × 109/L | 21 (21) |
| 0.5 to <1.0 × 109/L | 34 (34) |
| <0.5 × 109/L | 9 (0) |
| No data | 8 (8) |
| PLT count | |
| × 109/L, median (range), n = 85 | 56 (1-427) |
| n (%) | |
| ≥150 × 109/L | 11 (11) |
| 100 to <150 × 109/L | 12 (12) |
| 50 to <100 × 109/L | 23 (23) |
| 20 to <50 × 109/L | 29 (29) |
| <20 × 109/L | 10 (10) |
| PLT transfused (no data on PLT count before transfusion) | 14 (14) |
| No data of PLT count | 1 (1) |
| MCV, n (%) | |
| Normal for age | 45 (45) |
| Elevated for age | 43 (43) |
| RBC transfused | 7 (7) |
| No data of MCV | 5 (5) |
| BM cellularity at diagnosis, n (%) | |
| Hypocellular | 84 (84) |
| Normocellular | 12 (12) |
| Hypercellular | 4 (4) |
| Karyotype, n (%) | |
| Normal by metaphase analysis | 95 (95) |
| No metaphase; FISH: absence of −7, del(7), +8 | 4 (4) |
| No result | 1 (1) |
| Median follow-up | |
| Years (range) | 7.2 (2.0-18.4) |
| No. of patients | N = 100 |
| Age at diagnosis | |
| Years, median (range) | 10.9 (1.4-17.3) |
| Gender, n (%) | |
| Male | 54 (54) |
| Female | 46 (46) |
| Blood count at diagnosis | |
| Hb | |
| g/dL, median (range), n = 92 | 10.5 (3.9-16) |
| n (%) | |
| ≥12 g/dL | 24 (24) |
| 10 to <12 g/dL | 35 (35) |
| 7 to <10 g/dL | 20 (20) |
| <7 g/dL | 13 (13) |
| RBC transfused, no data on Hb before transfusion | 7 (7) |
| Not evaluable (no data about transfusion) | 1 (1) |
| White blood cell count | |
| × 109/L, median (range), n = 99 | 3.5 (0.3-7.7) |
| ANCs | |
| × 109/L, median (range), n = 92 | 1.1 (0-4.8) |
| n (%) | |
| ≥1.5 × 109/L | 28 (28) |
| 1.0 to <1.5 × 109/L | 21 (21) |
| 0.5 to <1.0 × 109/L | 34 (34) |
| <0.5 × 109/L | 9 (0) |
| No data | 8 (8) |
| PLT count | |
| × 109/L, median (range), n = 85 | 56 (1-427) |
| n (%) | |
| ≥150 × 109/L | 11 (11) |
| 100 to <150 × 109/L | 12 (12) |
| 50 to <100 × 109/L | 23 (23) |
| 20 to <50 × 109/L | 29 (29) |
| <20 × 109/L | 10 (10) |
| PLT transfused (no data on PLT count before transfusion) | 14 (14) |
| No data of PLT count | 1 (1) |
| MCV, n (%) | |
| Normal for age | 45 (45) |
| Elevated for age | 43 (43) |
| RBC transfused | 7 (7) |
| No data of MCV | 5 (5) |
| BM cellularity at diagnosis, n (%) | |
| Hypocellular | 84 (84) |
| Normocellular | 12 (12) |
| Hypercellular | 4 (4) |
| Karyotype, n (%) | |
| Normal by metaphase analysis | 95 (95) |
| No metaphase; FISH: absence of −7, del(7), +8 | 4 (4) |
| No result | 1 (1) |
| Median follow-up | |
| Years (range) | 7.2 (2.0-18.4) |
BM, bone marrow; FISH, florescence in situ hybridization; PLT, platelet; RBC, red blood cell.