Hematological parameters of Townes mice transduced with 2 × 1013 vg/kg rAAV8-hHPX or 1 × 1014 vg/kg rAAV8-mHPX vector compared with mice treated with the control vector
| . | rAAV8-mHPX (n = 16) . | rAAV8-Empty (n = 10) . | P value∗ . |
|---|---|---|---|
| 28th Week | |||
| Leukocytes (×103/μL) | 12.0 (8.5-14.4) | 12.1 (9.4-17.2) | .84 |
| Hb (g/dL) | 4.5 (4.0-5.5) | 4.5 (4.2-6.2) | .36 |
| Platelets (×103/μL) | 810 (573-1063) | 865 (735-1090) | .46 |
| . | rAAV8-mHPX (n = 16) . | rAAV8-Empty (n = 10) . | P value∗ . |
|---|---|---|---|
| 28th Week | |||
| Leukocytes (×103/μL) | 12.0 (8.5-14.4) | 12.1 (9.4-17.2) | .84 |
| Hb (g/dL) | 4.5 (4.0-5.5) | 4.5 (4.2-6.2) | .36 |
| Platelets (×103/μL) | 810 (573-1063) | 865 (735-1090) | .46 |
| . | rAAV8-hHPX (n = 7) . | rAAV8-Empty (n = 3) . | P value∗ . |
|---|---|---|---|
| 34th Week | |||
| Leukocytes (×103/μL) | 7.1 (4.1-9.0) | 10.1 (5.0-18.7) | .47 |
| Hb (g/dL) | 4.2 (3.2-5.6) | 4.0 (2.3-5.2) | .77 |
| Platelets (×103/μL) | 392 (302-698) | 455 (235-663) | .91 |
| . | rAAV8-hHPX (n = 7) . | rAAV8-Empty (n = 3) . | P value∗ . |
|---|---|---|---|
| 34th Week | |||
| Leukocytes (×103/μL) | 7.1 (4.1-9.0) | 10.1 (5.0-18.7) | .47 |
| Hb (g/dL) | 4.2 (3.2-5.6) | 4.0 (2.3-5.2) | .77 |
| Platelets (×103/μL) | 392 (302-698) | 455 (235-663) | .91 |
Results shown as median and interquartile range.
Mann-Whitney U test.