Patients reporting PNH-related symptoms
| Symptom . | Study 201, n (%), N = 26 . | Study 103, n (%), N = 13 . | ||
|---|---|---|---|---|
| Baseline . | Day 253 . | Baseline . | Day 169 . | |
| Fatigue | 18 (69.2) | 6 (23.1) | 9 (69.2) | 7 (53.8) |
| Dyspnea | 9 (34.6) | 1 (3.8) | 7 (53.8) | 4 (30.8) |
| Abdominal pain | 3 (11.5) | 0 | 3 (23.1) | 0 |
| Chest pain | 3 (11.5) | 0 | 3 (23.1) | 1 (7.7) |
| Erectile dysfunction | 5 (19.2) | 1 (3.8) | 2 (15.4) | 1 (7.7) |
| Dysphagia | 3 (11.5) | 0 | 1 (7.7) | 0 |
| Symptom . | Study 201, n (%), N = 26 . | Study 103, n (%), N = 13 . | ||
|---|---|---|---|---|
| Baseline . | Day 253 . | Baseline . | Day 169 . | |
| Fatigue | 18 (69.2) | 6 (23.1) | 9 (69.2) | 7 (53.8) |
| Dyspnea | 9 (34.6) | 1 (3.8) | 7 (53.8) | 4 (30.8) |
| Abdominal pain | 3 (11.5) | 0 | 3 (23.1) | 0 |
| Chest pain | 3 (11.5) | 0 | 3 (23.1) | 1 (7.7) |
| Erectile dysfunction | 5 (19.2) | 1 (3.8) | 2 (15.4) | 1 (7.7) |
| Dysphagia | 3 (11.5) | 0 | 1 (7.7) | 0 |