Table 2.

Favorable and adverse effects of chronic hydroxyurea (HU) therapy for adults with sickle cell anemia with high disease severity.37,38 

Favorable EffectsAdverse Effects
  • Decreased pain events

  • Decreased acute chest syndrome

  • Decreased need for transfusion

  • Decreased mortality

  • Decreased hemolysis

 
  • Transient decreases in blood counts

  • ? unknown long-term exposure risk

  • ? teratogenic effects

 
Favorable EffectsAdverse Effects
  • Decreased pain events

  • Decreased acute chest syndrome

  • Decreased need for transfusion

  • Decreased mortality

  • Decreased hemolysis

 
  • Transient decreases in blood counts

  • ? unknown long-term exposure risk

  • ? teratogenic effects

 
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