Characteristics of Wiskott-Aldrich syndrome patients receiving transplants between 1979 and 2001 in 19 European centers and surviving at least 2 years after HSCT
Donor group . | Median age, y (range) . | Median follow-up, y (range) . | Disease severity score, no. patients . | Splenectomy, no. patients . | |
---|---|---|---|---|---|
2-3 . | 4-5 . | ||||
MSD, n = 45 | 2.3 (0.5-13.5) | 8 (2-25) | 25 | 20 | 7 |
URD, n = 32 | 2.6 (0.33-17.7) | 4.5 (2-14) | 12 | 20 | 12 |
MMRD, n = 19 | 1.8 (0.5-17) | 11 (2-18) | 4 | 15 | 9 |
Donor group . | Median age, y (range) . | Median follow-up, y (range) . | Disease severity score, no. patients . | Splenectomy, no. patients . | |
---|---|---|---|---|---|
2-3 . | 4-5 . | ||||
MSD, n = 45 | 2.3 (0.5-13.5) | 8 (2-25) | 25 | 20 | 7 |
URD, n = 32 | 2.6 (0.33-17.7) | 4.5 (2-14) | 12 | 20 | 12 |
MMRD, n = 19 | 1.8 (0.5-17) | 11 (2-18) | 4 | 15 | 9 |