Table 1 Patients treated with engineered... | American Society of Hematology

Table 1

Patients treated with engineered HSCs

Disease	Vector type	LTR-driven	No. of treated patients
ADA	γRV	+	40
Gaucher	αRV	+	3
X-SCID	γRV/SIN-γRV	+/−	20/3
CGD	γRV	+	6
ALD	SIN-LV	+	4
WAS	γRV/SIN-LV	+/−	10/3
β-thal	SIN-LV	−	2
MLD	SIN-LV	−	4

Disease	Vector type	LTR-driven	No. of treated patients
ADA	γRV	+	40
Gaucher	αRV	+	3
X-SCID	γRV/SIN-γRV	+/−	20/3
CGD	γRV	+	6
ALD	SIN-LV	+	4
WAS	γRV/SIN-LV	+/−	10/3
β-thal	SIN-LV	−	2
MLD	SIN-LV	−	4