Patient characteristics at baseline
| Baseline characteristic . | Value . |
|---|---|
| Age, y | |
| Median | 44 |
| Range | 17-77 |
| Sex, n (%) | |
| Male | 24 (56) |
| Female | 19 (44) |
| Ethnic group, n (%) | |
| White | 20 (47) |
| Black | 13 (30) |
| Hispanic | 9 (21) |
| Asian | 1 (2) |
| Time since last IST, mo | |
| Median | 9 |
| Range | 6-117 |
| Prior number of courses of IST | |
| Median | 2 |
| Range | 1-4 |
| Response to prior IST, n (%) | |
| Primary refractory | 33 (77) |
| Relapsed refractory | 10 (23) |
| Transfusion dependency, n (%) | |
| Red cells | 40 (93) |
| Platelets | 42 (98) |
| PNH clones, n (%) | |
| Yes | 26 (60) |
| No | 17 (40) |
| Laboratory parameters | |
| Platelets (×10−3/mm3) | |
| Median | 8 |
| Range | 2-22 |
| Hemoglobin (g/dL) | |
| Median | 7.9 |
| Range | 6-13.3 |
| Neutrophils (×10−3/mm3) | |
| Median | 0.57 |
| Range | 0.07-2.8 |
| Baseline characteristic . | Value . |
|---|---|
| Age, y | |
| Median | 44 |
| Range | 17-77 |
| Sex, n (%) | |
| Male | 24 (56) |
| Female | 19 (44) |
| Ethnic group, n (%) | |
| White | 20 (47) |
| Black | 13 (30) |
| Hispanic | 9 (21) |
| Asian | 1 (2) |
| Time since last IST, mo | |
| Median | 9 |
| Range | 6-117 |
| Prior number of courses of IST | |
| Median | 2 |
| Range | 1-4 |
| Response to prior IST, n (%) | |
| Primary refractory | 33 (77) |
| Relapsed refractory | 10 (23) |
| Transfusion dependency, n (%) | |
| Red cells | 40 (93) |
| Platelets | 42 (98) |
| PNH clones, n (%) | |
| Yes | 26 (60) |
| No | 17 (40) |
| Laboratory parameters | |
| Platelets (×10−3/mm3) | |
| Median | 8 |
| Range | 2-22 |
| Hemoglobin (g/dL) | |
| Median | 7.9 |
| Range | 6-13.3 |
| Neutrophils (×10−3/mm3) | |
| Median | 0.57 |
| Range | 0.07-2.8 |