Table 2

Characteristics of patients who evolved while on eltrombopag

Patient #Age (y)ResponseBaselineAt evolutionTime on eltrombopag (mo)DysplasiaOutcomeTime posttransplant (mo)
60 NR 46XY[20] −7[20] Died of progressive cytopenias N/A 
18 NR 46XX[6] +8[9]/46XX[11] Transplanted successfully 31 
19 20 NR 46XY[20] −7[5]t(1;16) [3]/46XY[12] Transplanted successfully 18 
26 67 46XY[20] del(13)[19]/46XY[1] 13 Mild dyserythropoeisis Transplanted 
31 41 NR 46XY[20] +21[3]/46XY[17] −7[2]/46XY[19] 3
Mild dyserythropoeisis Awaiting transplant N/A 
32 66 46XY[20] 46XYdel13q[2]/46XY[18] Under observation N/A 
36 23 NR 46XY[20] −7[5],XY[15] Transplanted successfully 
42 17 NR No metaphases +1,der(1;7) [4]/46XY[16] Transplanted successfully 
Patient #Age (y)ResponseBaselineAt evolutionTime on eltrombopag (mo)DysplasiaOutcomeTime posttransplant (mo)
60 NR 46XY[20] −7[20] Died of progressive cytopenias N/A 
18 NR 46XX[6] +8[9]/46XX[11] Transplanted successfully 31 
19 20 NR 46XY[20] −7[5]t(1;16) [3]/46XY[12] Transplanted successfully 18 
26 67 46XY[20] del(13)[19]/46XY[1] 13 Mild dyserythropoeisis Transplanted 
31 41 NR 46XY[20] +21[3]/46XY[17] −7[2]/46XY[19] 3
Mild dyserythropoeisis Awaiting transplant N/A 
32 66 46XY[20] 46XYdel13q[2]/46XY[18] Under observation N/A 
36 23 NR 46XY[20] −7[5],XY[15] Transplanted successfully 
42 17 NR No metaphases +1,der(1;7) [4]/46XY[16] Transplanted successfully 

N/A, not applicable; NR, nonresponder; R, responder.

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