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Fulvio Mavilio, PhD
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Journal Articles

Editing a γ-Globin Repressor Binding Site Restores Fetal Hemoglobin Synthesis and Corrects the Phenotype of Sickle Cell Disease Erythrocytes

Leslie Weber, Giacomo Frati, Tristan Felix, Clara Wollenschlaeger, Antonio Casini, Vasco Meneghini, Cecile Masson, Anne De Cian, Anne Chalumeau, Fulvio Mavilio, PhD, Mario Amendola, Isabelle André, PhD, Anna Cereseto, Wassim El Nemer, PhD, Jean-Paul Concordet, Carine Giovannangeli, Marina Cavazzana, Annarita Miccio, PhD
Journal: Blood
Blood (2019) 134 (Supplement_1): 4635.
https://doi.org/10.1182/blood-2019-123192
Published: 2019
Journal Articles

Induction of Fetal Hemoglobin Synthesis By Crispr/Cas9-Mediated Disruption of the β-Globin Locus Architecture

Chiara Antoniani, MSc, Vasco Meneghini, Annalisa Lattanzi, PhD, Giulia Pavani, PhD, Tristan Felix, MSc, Fatima Amor, MSc, Oriana Romano, Elisa Magrin, PhD, Leslie Weber, MSc, Thomas Cradick, Ante S Lundberg, MD, Matthew Porteus, MD PhD, Mario Amendola, Marina Cavazzana, MD PhD, Fulvio Mavilio, PhD, Annarita Miccio, PhD
Journal: Blood
Blood (2016) 128 (22): 321.
https://doi.org/10.1182/blood.V128.22.321.321
Published: 2016
Journal Articles

Preclinical Development of Gene Therapy for X-Linked Severe Combined Immunodeficiency (SCID-X1)

Valentina Poletti, PhD, Sabine Charrier, PhD, Samia Martin, Bernard Gjata, Alban Vignaud, PhD, Fang Zhang, PhD, Karen Buckland, PhD, Michael Rothe, PhD, Axel Schambach, MD PhD, Sung-Yun Pai, MD, David A. Williams, MD, H. Bobby Gaspar, MD PhD, Adrian J Thrasher, MD PhD, Fulvio Mavilio, PhD
Journal: Blood
Blood (2016) 128 (22): 4705.
https://doi.org/10.1182/blood.V128.22.4705.4705
Published: 2016
Journal Articles

Re-Creating Hereditary Persistence of Fetal Hemoglobin (HPFH) to Treat Sickle Cell Disease (SCD) and β-Thalassemia

Michelle I Lin, PhD, Elizabeth J Paik, PhD, Bibhu P Mishra, PhD, Song Chou, PhD, Ying Zhang, PhD, Kaleigh Tomkinson, MS, Michael A Pettiglio, BS, Andrew Sanginario, BS, Amanda Woo, BS, Min Jin Lee, BS, Melanie Allen, MS, Thomas J Cradick, PhD, Tirtha Chakraborty, PhD, Matthew Porteus, MD PhD, Ciaran M Lee, PhD, Gang Bao, PhD, Annarita Miccio, PhD, Annalisa Lattanzi, PhD, Fulvio Mavilio, PhD, Chad A Cowan, PhD, Rodger Novak, MD, Ante S Lundberg, MD
Journal: Blood
Blood (2016) 128 (22): 4708.
https://doi.org/10.1182/blood.V128.22.4708.4708
Published: 2016
Journal Articles

Gene Editing with Crispr-Cas9 for Treating Beta-Hemoglobinopathies

Ciaran Lee, PhD, Gang Bao, PhD, Matthew H. Porteus, MD PhD, Tatjana Cornu, PhD, Annarita Miccio, PhD, Thomas Cradick, Toni Cathomen, PhD, Ante Lundberg, MD, Fulvio Mavilio, PhD
Journal: Blood
Blood (2015) 126 (23): 3376.
https://doi.org/10.1182/blood.V126.23.3376.3376
Published: 2015
Journal Articles

The Importance of Be(ginn)Ing Naïve: Implications for Cancer Immune-Gene Therapy

Nicoletta Cieri, MD, Barbara Camisa, Fabienne Cocchiarella, Elena Provasi, PhD, Zulma Magnani, Attilio Bondanza, MD, PhD, Anna Mondino, PhD, Fulvio Mavilio, PhD, Silvio Bicciato, PhD, Alessandra Recchia, PhD, Chiara Bonini
Journal: Blood
Blood (2011) 118 (21): 2052.
https://doi.org/10.1182/blood.V118.21.2052.2052
Published: 2011
Journal Articles

Gamma-Retroviral and Lentiviral Vectors Have Different Preferences for Specific Classes of Genes and Specific Genomic Features in Human Hematopoietic Cells

Alessandra Recchia, PhD, Anna Testa, PhD, Davide Cittaro, Barbara Felice, Claudia Cattoglio, Lucilla Luzi, PhD, Fulvio Mavilio, PhD
Journal: Blood
Blood (2007) 110 (11): 3732.
https://doi.org/10.1182/blood.V110.11.3732.3732
Published: 2007
Journal Articles

Retroviral Vector Integration Deregulates Gene Expression but Has No Consequences on the Biology and Function of Transplanted T Cells.

Alessandra Recchia, PhD, Chiara Bonini, MD, Zulma Magnani, Fabrizia Urbinati, PhD, Daniela Sartori, Sara Muraro, Fabio Ciceri, MD, Claudio Bordignon, MD, Fulvio Mavilio, PhD
Journal: Blood
Blood (2005) 106 (11): 462.
https://doi.org/10.1182/blood.V106.11.462.462
Published: 2005
Journal Articles

Molecular Follow-Up of Patients Treated with HSV-TK/ΔLNGFR Engineered Donor Lymphocytes after Allogeneic Stem Cell Transplantation.

Chiara Bonini, MD, Zulma Magnani, PhD, Alessandra Recchia, PhD, Fabrizia Urbinati, PhD, Sara Muraro, PhD, Serenella Sartori Tech, Fabio Ciceri, MD, Massimo Bernardi, MD, Alessandra Pescarollo, MD, Corrado Gallo-Stampino, MD, Marco Bregni, MD, Claudio Bordignon, MD, Fulvio Mavilio, PhD
Journal: Blood
Blood (2004) 104 (11): 1741.
https://doi.org/10.1182/blood.V104.11.1741.1741
Published: 2004