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Valentino Bezzerri, PhD
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Journal Articles

Breakthroughs in Preclinical Development of Ataluren (PTC124) As Therapeutic Option for Patients Affected By Shwachman-Diamond Syndrome: Towards the First Clinical Trial

Valentino Bezzerri, PhD, Antonio Vella, PhD, Elisabetta D'Aversa, PhD, Martina Api, PhD, Marisole Allegri, MSc, Elena Marinelli Busilacchi, PhD, Giovanna D'Amico, BSc, PhD MSc, Roberto Gambari, PhD, Claudio Sorio, MD PhD, Benedetta Fabrizzi, MD, Vincenzo Bronte, MD, Antonella Poloni, PhD MD, Monica Borgatti, PhD, Marco Cipolli, MD
Journal: Blood
Blood (2019) 134 (Supplement_1): 451.
https://doi.org/10.1182/blood-2019-127866
Published: 2019
Journal Articles

A Signature of Differentially Expressed Micrornas in Lymphoblastoid Cells from Shwachman-Diamond Syndrome Patients Indicates Possible Molecular Targets for Mirna Therapeutics

Jessica Gasparello, PhD, Chiara Papi, Giulia Breveglieri, PhD, Elisabetta D'Aversa, PhD, Valentino Bezzerri, PhD, Giovanna D'Amico, BSc, PhD MSc, Marco Cipolli, MD, Roberto Gambari, PhD, Monica Borgatti, PhD, Alessia Finotti, PhD
Journal: Blood
Blood (2019) 134 (Supplement_1): 2504.
https://doi.org/10.1182/blood-2019-128607
Published: 2019
Journal Articles

Further Insights into the Hematological Disorders Observed in Shwachman-Diamond Syndrome: mTOR and STAT3 Hyper-Phosphorylation in CD4+ and CD8+ T Cells and Efficacy of Rapamycin Treatment

Valentino Bezzerri, PhD, Antonio Vella, Ilaria Meneghelli, Marco Cipolli, Claudio Sorio, MD PhD
Journal: Blood
Blood (2016) 128 (22): 2675.
https://doi.org/10.1182/blood.V128.22.2675.2675
Published: 2016