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Journal Articles

Hematopoietic Stem Cell Therapy In Eight Patients with Metachromatic Leukodystrophy – Relevance of Post-Transplant Medication.

Judith Böhringer, Birgit Kustermann-Kuhn, PhD, Friederike Gieseke, PhD, Annika Erbacher, PhD, Michaela Döring, MD, Christiane Kehrer, MD, Peter Lang, MD, Ingeborg Krägeloh-Mann, MD, Rupert Handgretinger, MD, PhD, Ingo Müller, MD

Blood (2010) 116 (21): 3727.

https://doi.org/10.1182/blood.V116.21.3727.3727

Published: 2010

Journal Articles

Genz-112638 for Gaucher Disease Type 1: Phase 2 Clinical Trial Results After 18 Months of Treatment.

Judith Peterschmitt, MD, Elena Lukina, PhD, MD, Nora Patricia Watman, MD, Elsa Avila Arreguin, MD, Maryam Banikazemi, MD, Gregory Pastores, MD, Marcelo Iastrebner, MD, Marta Dragosky, MD, Hanna Rosenbaum, MD, Mici Phillips, MD, Mathilde Kaper, Tejdip Singh, MD, Ana Cristina Puga, MD, PhD

Blood (2009) 114 (22): 1349.

https://doi.org/10.1182/blood.V114.22.1349.1349

Published: 2009

Journal Articles

Long-Term Data From the ICGG Gaucher Registry: Clinical Parameters After 10 Years of Treatment with Imiglucerase.

Neal J. Weinreb, MD, Stephan vom Dahl, MD, Maria Domenica Cappellini

Blood (2009) 114 (22): 3590.

https://doi.org/10.1182/blood.V114.22.3590.3590

Published: 2009

Journal Articles

Comparative Results of Gene Therapy for Adenosine Deaminase Deficiency with or without PEG-ADA Withdrawal and Myelosuppressive Chemotherapy.

Robert Sokolic, MD, Greg Podsakoff, MD, Linda Muul, PhD, Barbara Engel, MD, Jayashree Jagadeesh, BS, Elizabeth Garabedian, RN, MSLS, Denise Carbonaro, Laura Tuschong, BS, Joanna Ireland, Michael Hershfield, MD, John Tisdale, MD, Cynthia Dunbar, MD, Alan Wayne, MD, Donald Kohn, MD, Fabio Candotti, MD

Blood (2007) 110 (11): 501.

https://doi.org/10.1182/blood.V110.11.501.501

Published: 2007

Journal Articles

Characterization of an Immunodeficient Mucopolysaccharidosis Type I (MPS-I) Mouse Model Suitable for Preclinical Testing of Human Stem Cell and Gene Therapy.

Mayra F. Quito-Rivera, BS, Leah E. Colvin-Wanshura, BS, Matthew S. Nelson, BS, Zhenhong Nan, PhD, Shaukat A. Khan, PhD, Tyson B. Rogers, MS, Indrani Maitra, PhD, Walter C. Low, PhD, Pankaj Gupta, MD

Blood (2005) 106 (11): 1265.

https://doi.org/10.1182/blood.V106.11.1265.1265

Published: 2005

Journal Articles

Antibody responses to bacteriophage phi X174 in patients with adenosine deaminase deficiency

HD Ochs, RH Buckley, RH Kobayashi, AL Kobayashi, RU Sorensen, SD Douglas, BL Hamilton, MS Hershfield

Blood (1992) 80 (5): 1163–1171.

https://doi.org/10.1182/blood.V80.5.1163.1163

Published: 1992

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Hematopoietic Stem Cell Therapy In Eight Patients with Metachromatic Leukodystrophy – Relevance of Post-Transplant Medication.

Genz-112638 for Gaucher Disease Type 1: Phase 2 Clinical Trial Results After 18 Months of Treatment.

Long-Term Data From the ICGG Gaucher Registry: Clinical Parameters After 10 Years of Treatment with Imiglucerase.

Comparative Results of Gene Therapy for Adenosine Deaminase Deficiency with or without PEG-ADA Withdrawal and Myelosuppressive Chemotherapy.

Characterization of an Immunodeficient Mucopolysaccharidosis Type I (MPS-I) Mouse Model Suitable for Preclinical Testing of Human Stem Cell and Gene Therapy.

Antibody responses to bacteriophage phi X174 in patients with adenosine deaminase deficiency

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ASH Publications

American Society of Hematology

Hematopoietic Stem Cell Therapy In Eight Patients with Metachromatic Leukodystrophy – Relevance of Post-Transplant Medication.

Genz-112638 for Gaucher Disease Type 1: Phase 2 Clinical Trial Results After 18 Months of Treatment.

Long-Term Data From the ICGG Gaucher Registry: Clinical Parameters After 10 Years of Treatment with Imiglucerase.

Comparative Results of Gene Therapy for Adenosine Deaminase Deficiency with or without PEG-ADA Withdrawal and Myelosuppressive Chemotherapy.

Characterization of an Immunodeficient Mucopolysaccharidosis Type I (MPS-I) Mouse Model Suitable for Preclinical Testing of Human Stem Cell and Gene Therapy.

Antibody responses to bacteriophage phi X174 in patients with adenosine deaminase deficiency

Email alerts

ASH Publications

American Society of Hematology

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