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Journal Articles

Excellent Outcomes in Children and Young Adults Using Reduced-Intensity Conditioning for Patients with Inborn Errors of Immunity, Hematopoiesis, and Metabolism with Single-Unit Cord Blood or Bone Marrow

Mark Vander Lugt, MD, Hey Jin Chong, MD PhD, Xiaohua Chen, MDPhD, Randy M. Windreich, MD, Rakesh Goyal, MD MRCP, Maria Escolar, MD, Paul Szabolcs, MD
Journal: Blood
Blood (2015) 126 (23): 4329.
https://doi.org/10.1182/blood.V126.23.4329.4329
Published: 2015
Journal Articles

Preimplantation Genetic Diagnosis for Benign Hematological Disorders Combined with HLA Matching and Stem Cells Development.

Gheona Altarescu, Deborah Elstein, Ari Zimran, MD, Talia Eldar Geva, Ephrat Levy Lahad, Paul Renbaum
Journal: Blood
Blood (2012) 120 (21): 3167.
https://doi.org/10.1182/blood.V120.21.3167.3167
Published: 2012
Journal Articles

Post Transplant Autoimmune Hemolytic Anemia and Other Cytopenias Are Increased in Very Young Babies after Unrelated Donor Umbilical Cord Blood Transplantation.

Kristin M. Page, MD, Adam Mendizabal, MS, Paul Szabolcs, MD, Susan Wood, PNP, Vinod Prasad, MD, Joanne Kurtzberg, MD
Journal: Blood
Blood (2007) 110 (11): 1054.
https://doi.org/10.1182/blood.V110.11.1054.1054
Published: 2007
Journal Articles

Brain Sparing Conditioning Regimen and Umbilical Cord Blood Transplantation for Inherited High Risk Neurologic Metabolic Diseases.

Jakub Tolar, MD, PhD, Pamala Jacobson, Ph.D., Lawrence Charnas, M.D., Ph.D., Paul J. Orchard, M.D.
Journal: Blood
Blood (2007) 110 (11): 3009.
https://doi.org/10.1182/blood.V110.11.3009.3009
Published: 2007
Journal Articles

Unique Reversible but Serious Adverse Events in Very Young Infants Undergoing Unrelated Donor Umbilical Cord Blood Transplantation for Non-Malignant Conditions: Increased Autoimmune Cytopenias and Hypertrophic Cardiomyopathy.

Sonali Lakshminarayanan, MD, Paul Szabolcs, MD, Suhag Parikh, MD, Susan J. Wood, MN, CPNP, June Allison, RN, CPON, Joanne Kurtzberg, MD
Journal: Blood
Blood (2005) 106 (11): 5456.
https://doi.org/10.1182/blood.V106.11.5456.5456
Published: 2005
Journal Articles

Cord Blood Transplantation for Lysosomal Storage Diseases Demonstrates the Potential of Cord Blood Cells for Future Cellular Therapies.

Joanne Kurtzberg, MD, William Krivit, MD
Journal: Blood
Blood (2004) 104 (11): 3602.
https://doi.org/10.1182/blood.V104.11.3602.3602
Published: 2004
Journal Articles

Allogeneic BMT Followed by Substrate Deprivation Therapy with N-butyldeoxynojirimycin in a Child with Tay-Sachs Disease.

Hans J.F.M. Jacobs, Michel M.A.A.P. Willemsen, Ph.D., M.D., Jacqueline J.J. Groot-Loonen, Ph.D. M.D., Ron R.A. Wevers, Ph.D. M.D., Peter P.M. Hoogerbrugge, Ph.D. M.D.
Journal: Blood
Blood (2004) 104 (11): 5158.
https://doi.org/10.1182/blood.V104.11.5158.5158
Published: 2004