Page 1 | Search Results | Blood | American Society of Hematology

1-20 of 35

Sort by

Sort Order Select

Journal Articles

Favorable Outcomes in Pediatric Patients in the Phase 3 Hgb-207 (Northstar-2) and Hgb-212 (Northstar-3) Studies of Betibeglogene Autotemcel Gene Therapy for the Treatment of Transfusion-Dependent β-Thalassemia

Alexis A. Thompson, MD, Janet L. Kwiatkowski, MD MSCE, John B. Porter, MA, MD, FRCP, FRCPath, Suradej Hongeng, MD, Evangelia Yannaki, MD, Andreas E. Kulozik, MD PhD, Martin G. Sauer, MD, Adrian J. Thrasher, MBBS, PhD FMedSci, Isabelle Thuret, MD, Ashutosh Lal, MD, Ruiting Guo, MS, Weijian Liu, PhD, Richard A. Colvin, MD PhD, Mark C. Walters, MD, Franco Locatelli, MD PhD

Blood (2020) 136 (Supplement 1): 52–54.

https://doi.org/10.1182/blood-2020-135857

Published: 2020

Journal Articles

Longitudinal Effect of Luspatercept Treatment on Iron Overload and Iron Chelation Therapy (ICT) in Adult Patients (Pts) with β-Thalassemia in the Believe Trial

Olivier Hermine, Maria Domenica Cappellini, Ali T. Taher, Thomas D. Coates, MD, Vip Viprakasit, Ersi Voskaridou, Ashutosh Lal, MD, Hong Keng Liew, Silverio Perrotta, Abderrahim Khelif, Antonis Kattamis, Jeevan K. Shetty, George Zhang, Yu (Olivia) Tian, Dimana Miteva, Tatiana Zinger, Derek Tang, Jay T. Backstrom, John B. Porter, MA, MD, FRCP, FRCPath

Blood (2020) 136 (Supplement 1): 47–48.

https://doi.org/10.1182/blood-2020-136517

Published: 2020

Journal Articles

Response of Patients with Transfusion-Dependent β-Thalassemia (TDT) to Betibeglogene Autotemcel (beti-cel; LentiGlobin for β-Thalassemia) Gene Therapy Based on HBB Genotype and Disease Genetic Modifiers

Mark C. Walters, MD, David H.K. Chui, MD FRCPC, John J Farrell, PhD, Ashutosh Lal, MD, Franco Locatelli, MD PhD, Janet L. Kwiatkowski, MD MSCE, John B. Porter, MA, MD, FRCP, FRCPath, Martin G. Sauer, MD, Isabelle Thuret, MD, Suradej Hongeng, MD, Andreas E. Kulozik, MD PhD, Adrian J. Thrasher, MBBS, PhD FMedSci, Evangelia Yannaki, MD, Julia Yang, Dustin Whitney, PhD, Alexandria Petrusich, Richard A. Colvin, MD PhD, Alexis A. Thompson, MD

Blood (2020) 136 (Supplement 1): 1–3.

https://doi.org/10.1182/blood-2020-137642

Published: 2020

Journal Articles

Northstar-3: Interim Results from a Phase 3 Study Evaluating Lentiglobin Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia and Either a β0 or IVS-I-110 Mutation at Both Alleles of the HBB Gene

Ashutosh Lal, MD, Franco Locatelli, MD PhD, Janet L. Kwiatkowski, MD MSCE, Andreas E. Kulozik, MD PhD, Evangelia Yannaki, MD, John B. Porter, MA MDFRCP FRCPath, Isabelle Thuret, MD, Martin G. Sauer, MD, Heidi Elliot, Ying Chen, PhD, Richard A. Colvin, MD PhD, Alexis A. Thompson, MD MPH

Blood (2019) 134 (Supplement_1): 815.

https://doi.org/10.1182/blood-2019-128482

Published: 2019

Journal Articles

Trends in Iron Overload over Past Two Decades: Results from the Natural History of Iron Burden Study with the SQUID Biosusceptometer

Ashutosh Lal, MD, Roland Fischer, PhD, Elliott Vichinsky, MD UCSF, Marcela Weyhmiller, PhD

Blood (2019) 134 (Supplement_1): 961.

https://doi.org/10.1182/blood-2019-129701

Published: 2019

Journal Articles

The Believe Trial: Results of a Phase 3, Randomized, Double-Blind, Placebo-Controlled Study of Luspatercept in Adult Beta-Thalassemia Patients Who Require Regular Red Blood Cell (RBC) Transfusions

Blood (2018) 132 (Supplement 1): 163.

https://doi.org/10.1182/blood-2018-163

Published: 2018

Journal Articles

Lentiglobin Gene Therapy for Patients with Transfusion-Dependent β-Thalassemia (TDT): Results from the Phase 3 Northstar-2 and Northstar-3 Studies

Franco Locatelli, Mark C. Walters, MD, Janet L. Kwiatkowski, MD, John Porter, MA MDFRCP FRCPath, Martin G. Sauer, MD, Isabelle Thuret, MD, Suradej Hongeng, MD, Andreas E. Kulozik, MD PhD, Ashutosh Lal, MD, Adrian J. Thrasher, MD PhD FMedSci, Evangelia Yannaki, MD, Heidi Elliot, Ge Tao, PhD, Mohammed Asmal, MD PhD, Alexis A. Thompson, MD MPH

Blood (2018) 132 (Supplement 1): 1025.

https://doi.org/10.1182/blood-2018-99-112667

Published: 2018

Journal Articles

Advances in Biomagnetic Liver Susceptometry Allow the Measurement of Liver Iron Concentration with a Room Temperature Sensor

Ashutosh Lal, MD, William Avrin, PhD, Viktoriia Kolotovska, MS, Lisa Calvelli, MS, Marcela Weyhmiller, PhD

Blood (2018) 132 (Supplement 1): 4890.

https://doi.org/10.1182/blood-2018-99-117355

Published: 2018

Journal Articles

Thalassemia Management Checklists: Quick Reference Guides to Reduce Disparities in the Care of Patients with Transfusion-Dependent Thalassemia

Ashutosh Lal, MD, Sujit Sheth, MD, Sandra Gilbert, PhD, Janet L. Kwiatkowski, MD

Blood (2018) 132 (Supplement 1): 2233.

https://doi.org/10.1182/blood-2018-99-109945

Published: 2018

Journal Articles

Pituitary Iron: Effect on Pituitary Volume and Function in Transfusion Dependent Thalassemia

Sylvia Titi Titi Singer, MD, Roland Fischer, PhD, Qing Yuan, PhD, Ashutosh Lal, MD, Isabel E Allen, PhD, Elliott Vichinsky, MD, Zhiyue J Wang, PhD

Blood (2017) 130 (Supplement 1): 3502.

https://doi.org/10.1182/blood.V130.Suppl_1.3502.3502

Published: 2017

Journal Articles

Community Survey of Knowledge of Thalassemia

Jin Mei, BA, Robert Yamashita, PhD, Ashutosh Lal, MD, Nancy F. Olivieri, MD, Elliott Vichinsky, MD

Blood (2017) 130 (Supplement 1): 5580.

https://doi.org/10.1182/blood.V130.Suppl_1.5580.5580

Published: 2017

Journal Articles

Factors Related to Iron Chelation Therapy Adherence in Young Adults with Thalassemia: A Framework from the Patient Perspective

Meghan Foe, Marsha J. Treadwell, PhD, Robert Yamashita, PhD, Ashutosh Lal, MD

Blood (2017) 130 (Supplement 1): 2080.

https://doi.org/10.1182/blood.V130.Suppl_1.2080.2080

Published: 2017

Journal Articles

Implications of Low Zinc and Copper Levels As Well As Altered Iron Trafficking Proteins on Oxidant Stress in Patients with Transfusion Dependant Thalassemia

Patrick B Walter, PhD, Michael Minkley, BS, Caitlin Curtis, BS, Hodge Maeve, BS, Razavi Morty, PhD, Sarah Ewing, BS, Ashutosh Lal, MD, Anne Higa, BS, David Killilea, PhD, Terry Pearson, PhD, Ellen B. Fung, PhD RD, CCD

Blood (2016) 128 (22): 1289.

https://doi.org/10.1182/blood.V128.22.1289.1289

Published: 2016

Journal Articles

Towards the Development of a Noninvasive Prenatal Test for Beta-Thalassemia: Utilization of Probe Capture Enrichment and Next Generation Sequencing

Katie Carlberg, MD, Nikhil Bose, Jingyi Deng, Ashutosh Lal, MD, Henry Erlich, PhD, Cassandra Calloway, PhD

Blood (2016) 128 (22): 3622.

https://doi.org/10.1182/blood.V128.22.3622.3622

Published: 2016

Journal Articles

Assessing Bone Quality Using Trabecular Bone Score in Patients with Hemoglobinopathies

Melissa Cervantes, Ashutosh Lal, MD, Anne M Marsh, MD, Ellen B. Fung, PhD RD, CCD

Blood (2016) 128 (22): 3629.

https://doi.org/10.1182/blood.V128.22.3629.3629

Published: 2016

Journal Articles

Threshold Ferritin Values to Predict Control of Liver Iron Burden in Thalassemia

Ashutosh Lal, MD, Marcela G Weyhmiller, PhD, Elliott Vichinsky, MD

Blood (2016) 128 (22): 4824.

https://doi.org/10.1182/blood.V128.22.4824.4824

Published: 2016

Journal Articles

Iron Level and Monocyte Morphology Predict TLR4 Expression and Reactive Oxygen Species Production Which Influences Chronic Inflammation in β-Thalassemia

Patrick B. Walter, PhD, Nick Slater, BS, Paul Harmatz, MD, Annie Higa, BS, Vivian Ng, BS, Marcels Weyhmiller, Patricia Evans, PhD, John B Porter, Nancy Sweeters, Jackson Price, BS, David Killilea, PhD, Lynne Neumayr, MD, Ashutosh Lal, MD, Elliott Vichinsky, MD

Blood (2015) 126 (23): 950.

https://doi.org/10.1182/blood.V126.23.950.950

Published: 2015

Journal Articles

Elevated End-Tidal Carbon Monoxide Concentration in Children with Sickle Cell Anemia

Ashutosh Lal, MD, Kristen Yen, MS, Lasandra Patterson, BS, Alisa Goldrich, BA, Anne M Marsh, MD, Anish Bhatnagar, MD

Blood (2014) 124 (21): 1390.

https://doi.org/10.1182/blood.V124.21.1390.1390

Published: 2014

Journal Articles

Dietary Intake Insufficient to Support Nutritional Adequacy in Patients with Thalassemia

Ellen B. Fung, PhD RD, CCD, Neogi Sushrita, BA, Drucilla Haines, PNP, Connie Schroepfer, MS, RD, CSR, Ashutosh Lal, MD

Blood (2014) 124 (21): 1361.

https://doi.org/10.1182/blood.V124.21.1361.1361

Published: 2014

Journal Articles

Association Of Cardiac Iron By T2* With Innate Immune Markers In Transfusion-Dependent Thalassemia Patients Undergoing Combined Chelation Therapy

Patrick B Walter, PhD, Annie Higa, BS, Vivian Ng, B.S., Marcela G Weyhmiller, PhD, Nick R Slater, Patricia Evans, PhD, John B Porter, MD, Nancy Sweeters, RN, PNP, Jackson Price, B.S., Alisha Manji, B.S., David Killilea, PhD, Ashutosh Lal, MD, Elliott Vichinsky, MD

Blood (2013) 122 (21): 3450.

https://doi.org/10.1182/blood.V122.21.3450.3450

Published: 2013

NARROW

Favorable Outcomes in Pediatric Patients in the Phase 3 Hgb-207 (Northstar-2) and Hgb-212 (Northstar-3) Studies of Betibeglogene Autotemcel Gene Therapy for the Treatment of Transfusion-Dependent β-Thalassemia

Longitudinal Effect of Luspatercept Treatment on Iron Overload and Iron Chelation Therapy (ICT) in Adult Patients (Pts) with β-Thalassemia in the Believe Trial

Response of Patients with Transfusion-Dependent β-Thalassemia (TDT) to Betibeglogene Autotemcel (beti-cel; LentiGlobin for β-Thalassemia) Gene Therapy Based on HBB Genotype and Disease Genetic Modifiers

Northstar-3: Interim Results from a Phase 3 Study Evaluating Lentiglobin Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia and Either a β0 or IVS-I-110 Mutation at Both Alleles of the HBB Gene

Trends in Iron Overload over Past Two Decades: Results from the Natural History of Iron Burden Study with the SQUID Biosusceptometer

The Believe Trial: Results of a Phase 3, Randomized, Double-Blind, Placebo-Controlled Study of Luspatercept in Adult Beta-Thalassemia Patients Who Require Regular Red Blood Cell (RBC) Transfusions

Lentiglobin Gene Therapy for Patients with Transfusion-Dependent β-Thalassemia (TDT): Results from the Phase 3 Northstar-2 and Northstar-3 Studies

Advances in Biomagnetic Liver Susceptometry Allow the Measurement of Liver Iron Concentration with a Room Temperature Sensor

Thalassemia Management Checklists: Quick Reference Guides to Reduce Disparities in the Care of Patients with Transfusion-Dependent Thalassemia

Pituitary Iron: Effect on Pituitary Volume and Function in Transfusion Dependent Thalassemia

Community Survey of Knowledge of Thalassemia

Factors Related to Iron Chelation Therapy Adherence in Young Adults with Thalassemia: A Framework from the Patient Perspective

Implications of Low Zinc and Copper Levels As Well As Altered Iron Trafficking Proteins on Oxidant Stress in Patients with Transfusion Dependant Thalassemia

Towards the Development of a Noninvasive Prenatal Test for Beta-Thalassemia: Utilization of Probe Capture Enrichment and Next Generation Sequencing

Assessing Bone Quality Using Trabecular Bone Score in Patients with Hemoglobinopathies

Threshold Ferritin Values to Predict Control of Liver Iron Burden in Thalassemia

Iron Level and Monocyte Morphology Predict TLR4 Expression and Reactive Oxygen Species Production Which Influences Chronic Inflammation in β-Thalassemia

Elevated End-Tidal Carbon Monoxide Concentration in Children with Sickle Cell Anemia

Dietary Intake Insufficient to Support Nutritional Adequacy in Patients with Thalassemia

Association Of Cardiac Iron By T2* With Innate Immune Markers In Transfusion-Dependent Thalassemia Patients Undergoing Combined Chelation Therapy

Email alerts

ASH Publications

American Society of Hematology

Email alerts

ASH Publications

American Society of Hematology

This Feature Is Available To Subscribers Only