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    Corrine Pondarre
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    Journal Articles

    Study Hgb-205: Outcomes of Gene Therapy for Hemoglobinopathies Via Transplantation of Autologous Hematopoietic Stem Cells Transduced Ex Vivo with a Lentiviral β Α-T87Q -Globin Vector (LentiGlobin ® BB305 Drug Product)

    Marina Cavazzana, MD PhD, Jean-Antoine Ribeil, MD PhD, Emmanuel Payen, Felipe Suarez, MD PhD, Yves Beuzard, MD, Fabien Touzot, MDPhD, Resy Cavallesco, PhD, Francois Lefrère, MD, Stany Chretien, Phillipe Bourget, Fabrice Monpoux, Corrine Pondarre, Benedicte Neven, MD, Manfred Schmidt, PhD, Christof von Kalle, MD, Laura Sandler, MPH, Sandeep Soni, MD, Olivier Hermine, Stephanie Blanche, Mariane De Montalembert, MD, Salima Hacein-Bey-Abina, Pharm.D., PhD, Philippe Leboulch, MD
    Journal: Blood
    Blood (2014) 124 (21): 4797.
    https://doi.org/10.1182/blood.V124.21.4797.4797
    Published: 2014

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