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Denise A. Carbonaro
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Journal Articles

Long-term outcomes after gene therapy for adenosine deaminase severe combined immune deficiency

Clinical Trials & Observations
Bryanna Reinhardt, Omar Habib, Kit L. Shaw, Elizabeth Garabedian, Denise A. Carbonaro-Sarracino, Dayna Terrazas, Beatriz Campo Fernandez, Satiro De Oliveira, Theodore B. Moore, Alan K. Ikeda, Barbara C. Engel, Gregory M. Podsakoff, Roger P. Hollis, Augustine Fernandes, Connie Jackson, Sally Shupien, Suparna Mishra, Alejandra Davila, Jack Mottahedeh, Andrej Vitomirov, Wenzhao Meng, Aaron M. Rosenfeld, Aoife M. Roche, Pascha Hokama, Shantan Reddy, John Everett, Xiaoyan Wang, Eline T. Luning Prak, Kenneth Cornetta, Michael S. Hershfield, Robert Sokolic, Suk See De Ravin, Harry L. Malech, Frederic D. Bushman, Fabio Candotti, Donald B. Kohn
Journal: Blood
Blood (2021) 138 (15): 1304–1316.
https://doi.org/10.1182/blood.2020010260
Published: 2021
Includes: Supplemental data
Journal Articles

Cytoreductive conditioning intensity predicts clonal diversity in ADA-SCID retroviral gene therapy patients

Aaron R. Cooper, Georgia R. Lill, Kit Shaw, Denise A. Carbonaro-Sarracino, Alejandra Davila, Robert Sokolic, Fabio Candotti, Matteo Pellegrini, Donald B. Kohn
Journal: Blood
Blood (2017) 129 (19): 2624–2635.
https://doi.org/10.1182/blood-2016-12-756734
Published: 2017
Includes: Supplemental data
Journal Articles

Gene therapy/bone marrow transplantation in ADA-deficient mice: roles of enzyme-replacement therapy and cytoreduction

Denise A. Carbonaro, Xiangyang Jin, Xingchao Wang, Xiao-Jin Yu, Nora Rozengurt, Michael L. Kaufman, Xiaoyan Wang, David Gjertson, Yang Zhou, Michael R. Blackburn, Donald B. Kohn
Journal: Blood
Blood (2012) 120 (18): 3677–3687.
https://doi.org/10.1182/blood-2012-02-408591
Published: 2012
Includes: Supplemental data
Journal Articles

Neonatal bone marrow transplantation of ADA-deficient SCID mice results in immunologic reconstitution despite low levels of engraftment and an absence of selective donor T lymphoid expansion

Denise A. Carbonaro, Xiangyang Jin, Daniel Cotoi, Tiejuan Mi, Xiao-Jin Yu, Dianne C. Skelton, Frederick Dorey, Rodney E. Kellems, Michael R. Blackburn, Donald B. Kohn
Journal: Blood
Blood (2008) 111 (12): 5745–5754.
https://doi.org/10.1182/blood-2007-08-103663
Published: 2008
Journal Articles

Prolonged pancytopenia in a gene therapy patient with ADA-deficient SCID and trisomy 8 mosaicism: a case report

Brief Report
Barbara C. Engel, Greg M. Podsakoff, Joanna L. Ireland, E. Monika Smogorzewska, Denise A. Carbonaro, Kathy Wilson, Ami Shah, Neena Kapoor, Mirna Sweeney, Mark Borchert, Gay M. Crooks, Kenneth I. Weinberg, Robertson Parkman, Howard M. Rosenblatt, Shi-Qi Wu, Michael S. Hershfield, Fabio Candotti, Donald B. Kohn
Journal: Blood
Blood (2006) 109 (2): 503–506.
https://doi.org/10.1182/blood-2006-06-031476
Published: 2006
Journal Articles

A Clinical Trial of Retroviral-Mediated Transfer of a rev -Responsive Element Decoy Gene Into CD34 + Cells From the Bone Marrow of Human Immunodeficiency Virus-1–Infected Children

Donald B. Kohn, Gerhard Bauer, C. Robert Rice, J.C. Rothschild, Denise A. Carbonaro, Penelope Valdez, Qian-lin Hao, Chen Zhou, Ingrid Bahner, Karen Kearns, Kate Brody, Sarah Fox, Elizabeth Haden, Kathy Wilson, Cathy Salata, Cathy Dolan, Charles Wetter, Estuardo Aguilar-Cordova, Joseph Church
Journal: Blood
Blood (1999) 94 (1): 368–371.
https://doi.org/10.1182/blood.V94.1.368.413a47_368_371
Published: 1999