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Raechel Peralta
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Journal Articles

2'-O-Methoxyethyl Splice-Switching Oligos to Reverse Splicing from IVS2-745 β-Thalassemia Patient Cells: A Foundation for Potential Therapies

Valentina Ghiaccio, PhD, Alisa Dong, PhD, Irene Motta, MD, Shuling Guo, PhD, Raechel Peralta, MS, Susan M Freier, Andy Watt, Yasuhiro Ikawa, MD PhD, Maxwell Chappell, MS, Coralea Stephanou, PhD, Paola Delbini, PhD, Connie Chen, Soteroula Christou, MD, Marina Kleanthous, PhD, Kim Smith-Whitley, MD, Deepa Manwani, MD, Carla Casu, PhD, Maria Domenica Cappellini, MD, Osheiza Abdulmalik, DVM, Stefano Rivella, PhD, Laura Breda, PhD
Journal: Blood
Blood (2019) 134 (Supplement_1): 2244.
https://doi.org/10.1182/blood-2019-127017
Published: 2019
Journal Articles

Adult Hemoglobin Production, Chain Rebalance, and Splice Correction in IVS2-745 Beta-Thalassemia Patient Cells Using 2'-O-Methoxyethyl Splice-Switching Oligos

Alisa Cheung Dong, Valentina Ghiaccio, Irene Motta, MD, Shuling Guo, PhD, Raechel Peralta, MS, Coralea Stephanou, PhD, Paola Delbini, PhD, Connie Chen, Soteroula Christou, Marina Kleanthous, PhD, Maria Domenica Cappellini, MD, Osheiza Abdulmalik, DVM, MS, Laura Breda, PhD, Stefano Rivella, PhD
Journal: Blood
Blood (2016) 128 (22): 1014.
https://doi.org/10.1182/blood.V128.22.1014.1014
Published: 2016
Journal Articles

Targeting KLF1 for the Treatment of Sickle Cell Disease Using Antisense Oligonucleotides

Raechel Peralta, MS, Audrey Low, Sheri Booten, Dewang Zhou, Aneeza Kim, Sue Freier, Shuling Guo, PhD, Sue Murray, Tim M. Townes, PhD, Gene Hung
Journal: Blood
Blood (2014) 124 (21): 4038.
https://doi.org/10.1182/blood.V124.21.4038.4038
Published: 2014
Journal Articles

Targeting BCL11A and KLF1 For The Treatment Of Sickle Cell Disease and β-Thalassemia In Vitro using Antisense Oligonucleotides

Raechel Peralta, Audrey Low, Aneeza Kim, Sue Murray, Shuling Guo, PhD, Sue Freier, Tim M. Townes, PhD, Gene Hung
Journal: Blood
Blood (2013) 122 (21): 1022.
https://doi.org/10.1182/blood.V122.21.1022.1022
Published: 2013