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Wolfgang Miesbach, MD PhD
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Journal Articles

Stable FIX Expression and Durable Reductions in Bleeding and Factor IX Consumption for up to 4 Years Following AMT-060 Gene Therapy in Adults with Severe or Moderate-Severe Hemophilia B

Wolfgang Miesbach, MD PhD, Karina Meijer, Michiel Coppens, MD, Peter Kampmann, MD, Dr. Klamroth, Roger Schutgens, MD PhD MSc, Giancarlo Castaman, MD, Erhard Seifried, MD PhD, Joachim Schwaeble, Halvard Bönig, Eileen K Sawyer, PhD, Frank W.G. Leebeek, MD PhD
Journal: Blood
Blood (2019) 134 (Supplement_1): 2059.
https://doi.org/10.1182/blood-2019-122535
Published: 2019
Journal Articles

Development of a Human in Vitro Cell Model for Haemophilia a

Rosa Toenges, MD, Nadin Hodroj, Nina Kurrle, PhD, Wolfgang Miesbach, MD PhD, Frank Schnuetgen, PhD, Hubert Serve, MD
Journal: Blood
Blood (2019) 134 (Supplement_1): 3634.
https://doi.org/10.1182/blood-2019-121908
Published: 2019
Journal Articles

One Year Data from a Phase 2b Trial of AMT-061 (AAV5-Padua hFIX variant), an Enhanced Vector for Gene Transfer in Adults with Severe or Moderate-Severe Hemophilia B

Steven Pipe, MD, Adam Giermasz, MD PhD, Giancarlo Castaman, MD, Nigel S. Key, MBChB, FRCP, Susan U Lattimore, Frank Leebeek, MD PhD, Wolfgang Miesbach, MD PhD, Michael Recht, MD PhD, Esteban Gomez, MD, Alison Long, Robert Gut, Annette von Drygalski, MD PharmD
Journal: Blood
Blood (2019) 134 (Supplement_1): 3348.
https://doi.org/10.1182/blood-2019-128765
Published: 2019