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Susana Navarro
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Journal Articles

Lentiviral-mediated Gene Therapy for Patients with Fanconi Anemia [Group A]: Updated Results from Global RP-L102 Clinical Trials

Agnieszka Czechowicz, Julián Sevilla, Claire Booth, Rajni Agarwal, Josune Zubicaray, Paula Río, Susana Navarro, Kritika Chetty, Grainne O'Toole, Jinhua Xu-Bayford, Philip Ancliff, Elena Sebastián, Grace Choi, Miriam Zeini, Eileen Nicoletti, John E Wagner, Gayatri R. Rao, Adrian J. Thrasher, Jonathan D. Schwartz, Maria Grazia Roncarolo, Juan A. Bueren
Journal: Blood
Blood (2022) 140 (Supplement 1): 10646–10647.
https://doi.org/10.1182/blood-2022-168342
Published: 2022
Journal Articles

Lentiviral-mediated Gene Therapy for Adults and Children with Severe Pyruvate Kinase Deficiency: Results from an Ongoing Global Phase 1 Study

Ami J. Shah, José Luis López Lorenzo, Julián Sevilla, Susana Navarro, Lucía Llanos, Begoña Pérez de Camino Gaisse, Sol Sanchez, Josune Zubicaray, Bert Glader, May Chien, Oscar Quintana Bustamante, Miriam Zeini, Grace Choi, Eileen Nicoletti, Gayatri R. Rao, Maria Grazia Roncarolo, Juan A. Bueren, Jonathan D. Schwartz, José C. Segovia
Journal: Blood
Blood (2022) 140 (Supplement 1): 4902–4903.
https://doi.org/10.1182/blood-2022-170948
Published: 2022
Journal Articles

Lentiviral Mediated Gene Therapy for Pyruvate Kinase Deficiency: Interim Results of a Global Phase 1 Study for Adult and Pediatric Patients

Ami J Shah, José Luis López Lorenzo, Susana Navarro, Julián Sevilla, Lucía Llanos, Begoña Pérez de Camino Gaisse, Sol Sanchez, Bert Glader, May Chien, Oscar Quintana Bustamante, Brian C Beard, Kenneth M Law, Miriam Zeini, Grace Choi, Eileen Nicoletti, Gayatri R Rao, Maria Grazia Roncarolo, Juan A Bueren, Jonathan D Schwartz, José C Segovia
Journal: Blood
Blood (2021) 138 (Supplement 1): 563.
https://doi.org/10.1182/blood-2021-148161
Published: 2021
Journal Articles

Gene Therapy for Fanconi Anemia [Group A]: Interim Results of RP-L102 Clinical Trials

Agnieszka Czechowicz, Julián Sevilla, Rajni Agarwal, Claire Booth, Josune Zubicaray, Paula Río, Susana Navarro, Philip Ancliff, Elena Sebastian, Brian C Beard, Kenneth M Law, Grace Choi, Miriam Zeini, Camilla Duran-Persson, Eileen Nicoletti, John E Wagner, Gayatri R Rao, Adrian J. Thrasher, Jonathan D Schwartz, Juan A Bueren, Maria Grazia Roncarolo
Journal: Blood
Blood (2021) 138 (Supplement 1): 3968.
https://doi.org/10.1182/blood-2021-147071
Published: 2021
Journal Articles

Lentiviral Mediated Gene Therapy for Pyruvate Kinase Deficiency: A Global Phase 1 Study for Adult and Pediatric Patients

José Luis López Lorenzo, MD, Susana Navarro, PhD, Ami J Shah, MD, Maria Grazia Roncarolo, MD, Julián Sevilla, MD PhD, Lucía Llanos, MD PhD, Begoña Pérez Camino de Gaisse, MD, Sol Sanchez, MD, Bertil Glader, MD PhD, May Chien, MD, Oscar Quintana Bustamante, PhD, Brian C Beard, PhD, Kenneth M Law, PhD, Miriam Zeini, PhD, Grace Choi, BS, Eileen Nicoletti, MD, Juan A Bueren, PhD, Gayatri R Rao, MD JD, Jonathan D Schwartz, MD, José C Segovia, PhD
Journal: Blood
Blood (2020) 136 (Supplement 1): 47.
https://doi.org/10.1182/blood-2020-137246
Published: 2020
Journal Articles

Gene Therapy for Fanconi Anemia, Complementation Group a: Updated Results from Ongoing Global Clinical Studies of RP-L102

Agnieszka Czechowicz, MDPhD, Rajni Agarwal, MD, Julián Sevilla, MD PhD, Paula Río, PhD, Susana Navarro, PhD, Brian C Beard, PhD, Kenneth M Law, PhD, Grace Choi, BS, Miriam Zeini, PhD, Eileen Nicoletti, MD, John E Wagner, MD, Claire Booth, MBBS, PhD MSc, Jonathan D Schwartz, MD, Juan A Bueren, PhD, Maria Grazia Roncarolo, MD
Journal: Blood
Blood (2020) 136 (Supplement 1): 14.
https://doi.org/10.1182/blood-2020-137106
Published: 2020
Journal Articles

Hematopoietic Engraftment of Fanconi Anemia Patients through 3 Years after Gene Therapy

Paula Rio, PhD, Susana Navarro, PhD, Rebeca Sanchez-Dominguez, PhD, Jose C Segovia, PhD, Wei Wang, PhD, Eva Merino, Rosa M Yañez, PhD, Jose Antonio Casado, PhD, Yari A. Gimenez, Francisco J Roman-Rodriguez, PhD, Omaira Alberquilla, Eva Galvez, MD, Raquel Hladun, MD, Jordi Barquinero, PhD, Anne Galy, PharmD, PhD, Nagore García de Andoín, MD, Ricardo López, MD PhD, Albert Catalá, MD PhD, Marina Cavazzana, Francois Lefrere, MD, Thierry Leblanc, MD, Jonathan D Schwartz, MD, Roser Pujol, PhD, Jordi Surrallés, PhD, Jean Soulier, MD PhD, Manfred Schmidt, PhD, Cristina Díaz de Heredia, MD PhD, Julian Sevilla, MD PhD, Juan A. Bueren, PhD
Journal: Blood
Blood (2019) 134 (Supplement_1): 4627.
https://doi.org/10.1182/blood-2019-129686
Published: 2019
Journal Articles

Advances in the Gene Therapy of Patients with Fanconi Anemia

Juan A. Bueren, PhD, Susana Navarro, PhD, Wei Wang, PhD, Rebeca Sanchez-Dominguez, PhD, Eva Merino, Jose C Segovia, PhD, Anne Galy, PharmD, PhD, María L. Lamana, MD PhD, Rosa M Yañez, PhD, Jose A Casado, PhD, Yari A. Gimenez, Francisco J Roman-Rodriguez, Lara A. Alvarez, Roser Pujol, PhD, Jordi Surralles, PhD, Ricardo López, MD PhD, Nagore García de Andoín, MD, Albert Catala, MD PhD, Eva Galvez, MD, Raquel Hladun, MD, Jonathan D Schwartz, MD, Manfred Schmidt, PhD, Cristina Díaz de Heredia, MD PhD, Paula Rio, PhD, Julian Sevilla, MD PhD
Journal: Blood
Blood (2018) 132 (Supplement 1): 1022.
https://doi.org/10.1182/blood-2018-99-111160
Published: 2018
Journal Articles

Engraftment and in vivo proliferation advantage of gene-corrected mobilized CD34 + cells from Fanconi anemia patients

Paula Río, Susana Navarro, Guillermo Guenechea, Rebeca Sánchez-Domínguez, Maria Luisa Lamana, Rosa Yañez, Jose A. Casado, Parinda A. Mehta, Maria Roser Pujol, Jordi Surrallés, Sabine Charrier, Anne Galy, José C. Segovia, Cristina Díaz de Heredia, Julián Sevilla, Juan A. Bueren
Journal: Blood
Blood (2017) 130 (13): 1535–1542.
https://doi.org/10.1182/blood-2017-03-774174
Published: 2017
Includes: Supplemental data
Journal Articles

In vivo proliferation advantage of genetically corrected hematopoietic stem cells in a mouse model of Fanconi anemia FA-D1

Paula Río, Néstor W. Meza, África González-Murillo, Susana Navarro, Lara Álvarez, Jordi Surrallés, Maria Castella, Guillermo Guenechea, José C. Segovia, Helmut Hanenberg, Juan A. Bueren
Journal: Blood
Blood (2008) 112 (13): 4853–4861.
https://doi.org/10.1182/blood-2008-05-156356
Published: 2008
Journal Articles

Non-Random Lentiviral Vector Insertions in Bone Marrow Progenitors from Fanconi Anemia Patients

Ali Nowrouzi, Africa Gonzales-Murillo, Anna Paruzynski, Ariana Jacome, Paula Rio, Susana Navarro, José Carlos Segovia, Nadine Krenzer, Christof von Kalle, Guillermo Guenechea, Juan A. Bueren, Manfred Schmidt
Journal: Blood
Blood (2008) 112 (11): 2358.
https://doi.org/10.1182/blood.V112.11.2358.2358
Published: 2008
Journal Articles

Relationship between the Hematopoietic Phenotype and the Subtype of Fanconi Anemia Mice.

Susana Navarro, PhD, Paula Rio, Ph.D, Nestor W. Meza, Ph.D, Raquel Chinchon, Bsc, Jose C. Segovia, Ph.D, Juan A. Bueren, Ph.D
Journal: Blood
Blood (2007) 110 (11): 2447.
https://doi.org/10.1182/blood.V110.11.2447.2447
Published: 2007
Journal Articles

Development of Efficent Gene Therapy for the Treatment of Erythrocyte Pyruvate Kinase Deficiency.

Nestor W. Meza, Ph.D., Maria Eugenia Alonso, Susana Navarro, Ph.D, Guillermo Guenechea, Ph.D, Oscar Quintana-Bustamante, Ph.D, Maria Garcia-Gomez, Juan A. Bueren, Ph.D, Jose M. Bautista, Ph.D, Jose C. Segovia, PhD
Journal: Blood
Blood (2007) 110 (11): 2584.
https://doi.org/10.1182/blood.V110.11.2584.2584
Published: 2007