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Research Article July 11 2025
Landscape and clinicopathologic features of RAS pathway mutations in chronic myelomonocytic leukemia
Guillermo Montalban-Bravo,Sanam Loghavi,Ziyi Li,Kelly Sharon Chien,Rashmi Kanagal-Shamanna,Alex Bataller,Anuya Natu,Mark Gurney,Alexandre Bazinet,Danielle Hammond,Koji Sasaki,Gautam Borthakur,Mahesh Swaminathan,Courtney D. DiNardo,Tapan M. Kadia,Farhad Ravandi,Naval G Daver,Nicholas J. Short,Naveen Pemmaraju,Ghayas C. Issa,Terra L Lasho,Christy M. Finke,Aref Al-Kali,Clifford M Csizmar,Hassan B Alkhateeb,Naseema Gangat,Abhishek A. Mangaonkar,Carlos E. Bueso-Ramos,Ayalew Tefferi,Hagop M Kantarjian,Guillermo Garcia-Manero,Mrinal M Patnaik
Research Article July 11 2025
Outcomes and survival prediction in adults with sickle cell disease treated with extracorporeal membrane oxygenation
Letter July 3 2025
PROM1/CD133 MARKS A PROLIFERATIVE STEM CELL LIKE POPULATION OF BLASTS IN KMT2A REARRANGED INFANT ALL
Joe Wilson Cross,Lucy May Field,Alastair Smith,Emily Neil,Lucy Hamer,Thomas Jackson,Natalina Elliott,Siobhan Rice,Nicholas Crump,Joe Harman,Rebecca E Ling,Qingqing Wu,Nouhad El Ouazzani,Rebecca Thomas,Sarah Inglott,Jack Bartram,Owen Smith, Professor,Jonathan Bond,Irene Roberts,Thomas A. Milne,Anindita Roy
Research Article July 3 2025
Sex and genotype specificities of microvasculature and muscle remodeling in sub-Saharan sickle cell trait and disease
Research Article July 3 2025
Deleting ACC1 in platelets alters phospholipidome and reduces platelet activation and thrombosis in mice
Marie Octave,Laurence Pirotton,Emma de Cartier d'Yves,Alice Marino,Jérôme Ambroise,Martin Giera,Bruno Guigas,Audrey Ginion,Valentine Robaux,Marijke J.E. Kuijpers,Constance C.F.M.J. Baaten,Johan W.M. Heemskerk,Zoltan Nagy,Yotis A Senis,Davide Brusa,Caroline Bouzin,Luc Bertrand,Christophe Beauloye,Sandrine Horman
Research Article July 3 2025
Age-Adjusted Dosing of Fludarabine for Lymphodepletion in CAR T-cell Therapy: A Clinical Trial Simulation Study
Research Article July 2 2025
Symptoms, unmet needs, and quality of life in Erdheim-Chester disease: A longitudinal registry-based analysis
Letter July 2 2025
Long term outcomes of genome edited 'universal' CAR19 T-cells for relapsed/refractory B-ALL at a single pediatric centre
Letter July 2 2025
Asciminib for relapsed or refractory Philadelphia chromosome-positive acute lymphoblastic leukemia.
Mathilde Chanut,Aurélie Cabannes-Hamy,Marie Balsat,Nassim Sahki,Emmanuel Raffoux,Yosr Hicheri,Bruno Lioure,Lucie Laemmel,Thibaut TL Leguay,Victoria Cacheux,Maria Pilar Gallego-Hernanz,Andrea Pieragostini,Gabrielle Roth-Guepin,Ludovic Gabellier,Nathalie Denizon,Lise Willems,Quentin Cabrera,Sylvain P Chantepie,Valérie Coiteux,Claudie Capdupuy,Martin Carre,Antoine Machet,Juliette Lambert,Sandrine Roux,Franck-Emmanuel Emmanuel Nicolini,Nicolas Boissel,Emmanuelle Clappier,Rathana Kim,Philippe Rousselot
Research Article July 2 2025
BH3 mimetic drugs overcome the microenvironment-induced resistance to crizotinib in ALK+ anaplastic large cell lymphoma
Claudia Pignataro,Pietro Zoppoli,Luca Vincenzo Cappelli,Liron Yoffe,Marta Moretti,Mariapaola Izzo,Selene Mallia,Clarisse Kayembe,Abigail Taylor,Gianluca Petrillo,Alessandra Affinito,Cristina Quintavalle,Giada De Luca,Martina Mascolo,Sara Verde,Aurelia Fraticelli,Alessia Ciarrocchi,Paolo Salerno,Enrico De Smaele,Antonio Francesco Campese,Valentina Fragliasso,Robin Foà,Giuseppe Merla,Giorgio GA Inghirami,Gerolama Condorelli,Danilo Fiore
Research Article July 1 2025
Prospective Cohort Study of eDiary Acute Pain Assessments in Sickle Cell Disease During Third Trimester and Postpartum
Research Article July 1 2025
Impact of transplant conditioning, NPM1 mutations, and measurable residual disease in FLT3-ITD acute myeloid leukemia
Mark J. Levis,Mehdi Hamadani,Brent R. Logan,Richard J. Jones,Anurag K Singh,Mark R Litzow,John R. Wingard,Esperanza B. Papadopoulos,Alexander E. Perl,Robert J. Soiffer,Celalettin Ustun,Masumi Ueda Oshima,Geoffrey L. Uy,Edmund K Waller,Sumithira Vasu,Melhem M. Solh,Asmita Mishra,Lori S. Muffly,Hee-Je Kim,Matthias Stelljes,Yuho Najima,Masahiro Onozawa,Kirsty J Thomson,Caroline Chen,Nahla Hasabou,Matt Rosales,Jason E. Hill,Stanley C. Gill,Rishita Nuthethi,Denise King,Adam M Mendizabal,Steven M. Devine,Mary M Horowitz,Yi-Bin Chen
Research Article July 1 2025
Refinement of Day 28 Treatment Response Criteria for Acute GVHD: A Collaboration Study of the JSTCT and MAGIC
Yu Akahoshi,Yoshihiro Inamoto,Nikolaos Spyrou,Hideki Nakasone,Marcio Diniz,Noboru Asada,Francis Ayuketang Ayuk,Hannah K Choe,Noriko Doki,Tetsuya Eto,Aaron M. Etra,Elizabeth O. Hexner,Nobuhiro Hiramoto,William J Hogan,Ernst Holler, Prof. Dr. med,Keisuke Kataoka,Toshiro Kawakita,Masatsugu Tanaka,Takashi Tanaka,Naoyuki Uchida,Ingrid Vasova,Satoshi Yoshihara,Fumihiko Ishimaru,Takahiro Fukuda,Yi-Bin Chen,Junya Kanda,Ryotaro Nakamura,Yoshiko Atsuta,James L.M. Ferrara,Yoshinobu Kanda,John E Levine,Takanori Teshima
Research Article July 1 2025
Effect of age on ISTH-BAT scores and Low VWF diagnosis in the Zimmerman Program
Research Article June 26 2025
Prognostic Impact of Focal Lesion Location and Persistence in Multiple Myeloma: Insights from Serial PET/DWI Imaging
Research Article June 26 2025
From CyBorD to Dara-CyBorD: ASCT Utilization Trends in AL Amyloidosis, A 15-Year Analysis
Eli Muchtar,Angela Dispenzieri,Francis K Buadi,Prashant Kapoor,David Dingli,Taxiarchis V. Kourelis,Wilson I Gonsalves,Nelson Leung,Suzanne R Hayman,Martha Q Lacy,Mustaqeem Siddiqui,Joselle Cook,Nadine Abdallah,Moritz Binder,Saurabh Zanwar,William J Hogan,Rahma Warsame,S. Vincent Rajkumar,Shaji K Kumar,Morie A Gertz
Letter June 25 2025
Blood-derived Cell-Free DNA is a Superior Biomarker for Non-Invasive DNA Methylation Profiling in Multiple Myeloma
Letter June 25 2025
Invasive fungal disease is rare in patients with relapsed/refractory multiple myeloma treated with BCMA CAR T-cell therapy
Review Article June 25 2025
Efficacy and Safety of Thrombolysis for Pediatric Venous Thromboembolism: A Systematic Review and Meta-analysis
Hassan Kawtharany,Muayad Azzam,Aseel Alkhader,Marisol Betensky,Qais Hamarsha,Hadi K. Abou Zeid,Razan Mansour,Carine Tabak,Payal Patel,Sarah L. Baghdadi,Rachel Sara Bercovitz,Rukhmi Bhat,Tina T Biss,Brian R Branchford,Leonardo R. Brandão,Anthony KC Chan,E. Vincent S. Faustino,Julie Jaffray,Sophie E Jones,Bryce A Kerlin,Nicole Kucine,Riten Kumar,Christoph Male,Marie-Claude Pelland-Marcotte,Leslie Raffini,Chittalsinh M Raulji,Sarah E Sartain,Clifford M. Takemoto,Cristina Tarango,C. Heleen van Ommen,Maria C Velez,Sara K Vesely,John T Wiernikowski,Suzan Williams,Hope P Wilson,Gary Woods,Ayesha Zia,Paul Monagle,Reem A. Mustafa
Research Article June 24 2025
Evaluation of In vivo CAR Transgene Levels in Tisagenlecleucel-Treated Patients with Relapsed/Refractory B-ALL and DLBCL
Rakesh Awasthi,Stephan A. Grupp,Edward Waldron,Gregory A Yanik,Constantine S Tam,Susana Rives,Joseph P. McGuirk,Michael A. Pulsipher,Ulrich Jaeger,Gary Douglas Myers,Peter Borchmann,Stephen J. Schuster,Heather E Stefanski,Michael R Bishop,Abhijit Chakraborty,Aisha Masood,André Baruchel,Edmund K Waller
Research Article June 24 2025
A prospective clinical trial of GVHD prophylaxis with Post-Transplant Cyclophosphamide and Abatacept
Review Article June 24 2025
Upfront Alternative Donor HCT in Severe Aplastic Anemia: Gaps and Opportunities to Translate Evidence into Practice
Research Article June 24 2025
Multi-population GWAS for venous thromboembolism identifies novel loci followed by experimental validation in zebrafish
Brooke N Wolford,Queena Yakun Zhao,Kuan-Han H. Wu,Xinge Yu,Catherine E. Richter,Laxmi Bhatta,Ben M. Brumpton,Karl C. Desch,Florian Thibord,Derek Klarin,Andrew D Johnson,David-Alexandre Tregouet,Scott M. Damrauer,Nicholas L. Smith,Valeria Lo Faro,Kristin Tsuo,Mark Daly,Ben Neale,Wei Zhou,Cristen J. Willer,Jordan A Shavit,Ida Surakka
Research Article June 24 2025
Real-world data for tisagenlecleucel in patients with R/R B-ALL: subgroup analyses from the CIBMTR registry
Samuel John,Kevin J. Curran,Erin M. Hall,Amy Keating,Susanne H.C. Baumeister,Sarah Nikiforow,Timothy Driscoll,Amy Moskop,Kevin O. McNerney,Christine L. Phillips,Michael A. Pulsipher,Emily M. Hsieh,Rayne H Rouce,Marcelo C. Pasquini,Ranjan Tiwari,Jennifer Willert,Roberto Javier Ramos,Joerg Krueger,Erin Guest,Stephan A. Grupp
Research Article June 24 2025
Pirfenidone for the treatment of bronchiolitis obliterans syndrome related to chronic graft-versus-host disease
Research Article June 24 2025
Long-term outcomes of patients with refractory cytopenia of childhood under observation only
Beatrice Drexler,Stephan Schwarz-Furlan,Irith Baumann,Martina Rudelius,Peter Nöllke,Dirk Lebrecht,Senthilkumar Ramamoorthy,Natalia Rotari,Axel Karow,Shinsuke Hirabayashi,Fabian Beier,Yvonne Lisa Behrens,Gudrun Göhring,Reinhard Kalb,Marcin W Wlodarski,Brigitte Strahm,Miriam Erlacher,Charlotte M Niemeyer,Ayami Yoshimi
Research Article June 24 2025
Point-of-care fresh CAR T cells for pediatric or young adult BCP-ALL that is relapsed/refractory or in very-high-risk first relapse
Francesca Del Bufalo,Marco Becilli,Chiara Rosignoli,Pietro Merli,Mattia Algeri,Daria Pagliara,Federica Galaverna,Michele Massa,Valeria Paganelli,Maria Giuseppina Cefalo,Linda Hanssens,Valentina Bertaina,Giuseppina Li Pira,Giovanna Leone, Dr,Matilde Sinibaldi,Stefano Di Cecca,Laura Iaffaldano,Valentina Fustaino,Biagio De Angelis,Concetta Quintarelli,Franco Locatelli
Research Article June 20 2025
Allogeneic haematopoietic stem cell transplantation for STAT3 hyper-IgE syndrome: a worldwide study
Christo Tsilifis,Johannes Raedler,Joanna Renke,Michael Medinger,Alexandra Laberko,Ásgeir Haraldsson,Niraj Patel,Peter Ciznar,Melanie Wong,Steven John Keogh, MBBS, FRACP,Paul E Gray,Richard Mitchell,Venetia Bigley,Suzanne Elizabeth Elcombe,Fabian Hauck,Michael H Albert,Eleni Tholouli,Archana Herwadkar,Shuayb Elkhalifa,Chris Kosmidis,Giorgio Callisti,Lauri M. Burroughs,Karin Chen,Ben Carpenter,Thomas A Fox,Emma C. Morris,Ramya Uppuluri,Revathi Raj,Masakatsu Yanagimachi,Emilie Pauline Buddingh,Christina Oikonomopoulou,Corina E Gonzalez,Dimana Dimitrova,Jennifer A. Kanakry,Danielle E Arnold,Sung-Yun Pai,Mary A Slatter,Mark S. Pearce,Austen J Worth,Alexandra F Freeman,Andrew R Gennery
Research Article June 20 2025