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Letter February 4 2025
ICE polychemotherapy is an efficient salvage treatment in relapsed/refractory primary central nervous system lymphoma.
Research Article February 4 2025
CD19.CAR-T cell-derived extracellular vesicles express CAR and kill leukemic cells, contributing to antineoplastic therapy
Paola Lanuti, PhD,Francesco Guardalupi,Giulia Corradi, PhD,Rosalba Florio, PhD,Davide Brocco, MD, PhD,Serena Veschi, PhD,Elsa Pennese, MD,Domenico De Bellis, PhD student,Francesca D'Ascanio, PhD Student,Anna Piro, PhD Student,Laura De Lellis, PhD,Pasquale Simeone,Maria Concetta Cufaro,Serena Pilato, PhD,Isabella D'Amario, PhD student,Ida Villanova, PhD,Barbara Di Francesco, PhD,Lucia Di Re, PhD Student,Fabio Verginelli, PhD,Damiana Pieragostino,Pressede Salutari, MD,Fabrizia Colasante, MD,Annalisa Natale, MD,Maria Vittoria Mattoli, MD,Simone Vespa,Antonella Fontana, PhD,Raffaella Giancola, MD, PhD,Bianca Fabi, MD,Stefano Baldoni,Stella Santarone,Francesco Restuccia,Nicola Tinari, MD, PhD,Piero Del Boccio,Alessandro Cama, PhD, MD,Mauro Di Ianni
Letter February 4 2025
Estimating rare genetic disease prevalence: a challenging task
Letter February 4 2025
Distress and Symptom Burden in Patients with Monoclonal Gammopathy of Undetermined Significance and Smoldering Myeloma
Research Article January 30 2025
Impact of Vein-to-vein Time in Patients With R/R LBCL Treated With Axicabtagene Ciloleucel
Frederick L Locke,Tanya Siddiqi,Caron A. Jacobson,Sarah Nikiforow,Sairah Ahmed,David B Miklos,Yi Lin,Matthew A Lunning,Brian T. Hill,Armin Ghobadi,Zhen-Huan Hu,Michael T. Hemmer,Michael J Zoratti,Suresh Vunnum,Jonathan Tsang,Clare Spooner,Harry Smith,Christine Fu,Anik R Patel,Harry Miao,Shilpa A. Shahani,Debbie L. Mirjah,Hairong Xu,Marcelo C. Pasquini
Research Article January 30 2025
Six-month Rituximab-Lenalidomide regimen in advanced untreated Follicular Lymphoma: SAKK 35/10 Trial 10-year Update
Eva K Kimby, Professor Emerita,Sämi Schär,Maria Cristina Pirosa,Anna Vanazzi,Ulrich J.M. Mey,Daniel Rauch,Björn E. Wahlin,Felicitas Hitz,Micaela Hernberg,Ann-Sofie Johansson,Peter de Nully Brown,Hans Hagberg,Andrés José María JM Ferreri,Fatime Krasniqi,Michele Voegeli,Urban Novak,Thilo Zander,Hanne Bersvendsen,Christoph Mamot,Walter Mingrone,Anastasios Stathis,Stefan Dirnhofer,Stefanie Hayoz,Bjørn Østenstad,Emanuele Zucca
Research Article January 28 2025
Deciphering the complex clonal heterogeneity of polycythemia vera and the response to interferon alpha
Milena Kalmer,Martin Grasshoff,Tiago Maié,Kristina Pannen,Marcelo A.S. Toledo,Margherita Vieri,Kathrin Olschok,Rebecca Lemanzyk,Jelena Lazarevic,Baerbel Junge,Julian Baumeister,Angela Galauner,Noa Chapal-Ilani,Dror Bar,Elia Colin,Mingobo Cheng,Joelle Schifflers,Kim Kricheldorf,Mirle Schemionek,Tim Henrik Brümmendorf,Ralf Weiskirchen,Liran Shlush,Martin Zenke,Nicolas Chatain,Ivan G Costa,Steffen Koschmieder
Research Article January 28 2025
Outcome of high-grade B-cell lymphoma compared to other large B-cell lymphoma after CAR-T rescue. A DESCAR-T LYSA study
Xavier Phina-Ziebin,Emmanuel Bachy,Francois-Xavier Gros,Roberta Di Blasi,Charles Herbaux,Jacques Olivier Bay,Sylvain Carras,Pierre Bories,Olivier Casasnovas,Fabrice Jardin,Franck Morschhauser,Blandine Guffroy,Mohamad Mohty,Elodie Gat,Julien Calvani,Marie-Cécile Parrens,Elsa Poullot,Alexandra Traverse-Glehen,Louise Roulin
Research Article January 28 2025
Efficacy and safety of dapsone in adult primary immune thrombocytopenia
Marion Larue,Guillaume Moulis,Manuela Rueter,Sylvain Audia,Louis Terriou,Jean-François Viallard,Brigitte Pan-Petesch,Bruno Royer,Bernard Bonnotte,Lionel Galicier,Olivier Lambotte,Francois Y Lefrere,Stéphane Cheze,Mikael Ebbo,Tu-Anh Duong,Emmanuelle Boutin,Laetitia Languille,Matthieu Mahevas,Bertrand Godeau,Florence Canoui-Poitrine,Marc Michel
Review Article January 28 2025
Hepatosplenic T-cell lymphoma in children and adolescents
Research Article January 24 2025
Cutaneous dysbiosis characterizes the post-allogeneic hematopoietic stem cell transplantation period
Review Article January 24 2025
Audit of B-cell Cancer Genes
Research Article January 24 2025
ACQUIRED MUTATIONS IN PATIENTS WITH RELAPSED/REFRACTORY CLL WHO PROGRESSED IN THE ALPINE STUDY
Research Article January 24 2025
TP53 Mutant Variant Allele Frequency and Cytogenetics Determine Prognostic Groups in MDS/AML for Transplantation
Review Article January 24 2025
Systemic Mastocytosis: Current Status and Challenges in 2024
Research Article January 18 2025
Molecular clustering on ctDNA improves the prognostic stratification of DLBCL patients compared to ctDNA levels
Riccardo Moia,Donatella Talotta,Lodovico Terzi di Bergamo,Mohammad Almasri,Riccardo Dondolin,Matin Salehi,Chiara Cosentino,Roberta Soscia,Irene Della Starza,Alessio Bruscaggin,Annalisa Giovanna Andorno,Francesca Mercalli,Stefania Cresta,Riccardo Bomben,Tamara Bittolo,Filippo Vit,Pietro Bulian,Antonella Zucchetto,Riccardo Bruna,Giulia Maria Rivolta,Mattia Schipani,Eleonora Secomandi,Sreekar Kogila,Matteo Bellia,Samir Mouhssine,Jana Nabki,Bashar Al Deeban,Joseph Ghanej,Luca Cividini,Nawar Maher,Federica Melle,Giovanna Motta,Monica Leutner,Angela Lorenzi,Abdurraouf Mokhtar Mahmoud,Wael Al Essa,Clara Deambrog,Silvia Rasi,Luigi Petrucci,Renzo Boldorini,Alice Di Rocco,Ilaria Del Giudice,Michele Spina,Stefano Palazzolo,Fabio Canal,Vincenzo Canzonieri,Maurizio Martelli,Stefano A Pileri, Professor,Valter Gattei,Robin Foà,Davide Rossi,Gianluca Gaidano
Letter January 18 2025
PRIMARY CUTANEOUS CD8+ AGGRESSIVE EPIDERMOTROPIC CYTOTOXIC T-CELL LYMPHOMA WITH NOVEL FGFR1 FUSION TREATED WITH PEMIGATINIB
Research Article January 18 2025
PRMT5 Inhibition Reduces Hyperinflammation in a Murine Model of Secondary Hemophagocytic Lymphohistiocytosis (HLH)
Fiona Brown-Burke,Rachel Saadey,Hsiao-Yin Charlene Charlene Mao,Paola Marra,Eric Brooks,Alexa Wandtke,Ian Hout,Sydney Leon,Archisha Sharma,Aneeq Yasin,Taylor Cash,Elshafa Hassan Ahmed,Ethan James Baiocchi,Stephanie Scarlett Finoti,Xiaoli Zhang,Neha Bhagwat,Kris Vaddi,Peggy Scherle,Anna Mozhenkova,Ikbale El-Ayachi,Austin D. Schenk,Shelby L. Sloan,Kaylee Whitman,JoBeth Helmig-Mason,Sheldon Steyn,Haley L. Klimaszewski,Jessica Weist,Christoph Weigel,Shirsha Koirala,Lapo Alinari,Katiri Snyder,Parvathi Ranganathan,Chia-Jo Chen,Michael B. Jordan,Robert A. Baiocchi,Polina Shindiapina
Research Article January 18 2025
Final Analysis of the Phase 1b Chemotherapy And Venetoclax in Elderly Acute Myeloid Leukaemia Trial (CAVEAT)
Research Article January 18 2025
Definitions and use of tumour bulk in phase 3 lymphoma trials: a comprehensive literature review
Research Article January 16 2025
Stroke Prevention in Hispanic Children with Sickle Cell Anemia: the SACRED trial
Rosa Nieves,Teresa Latham,Nicolle Marie Marte,Melissa Berges Morales,Luisanna M. Sanchez,Gabriela Urcuyo,Carla Florencio,Carla González Guaschino,Paola DelVillar,Sheena Chen Lin,Daniel Alejandro Pierre Ramirez,Paula Reyes,Manuel Marinez J,Euladys Matos,Neelum Dilip Jeste,Susan E Stuber,William H Schultz,Adam Lane,Rafael Mena,Russell E. Ware
Research Article January 16 2025
TP53 Mutations are Associated with CD19 Negative Relapse and Inferior Outcomes after Blinatumomab in Adults with ALL
Ibrahim Aldoss,Shanpeng Li,Jianying Zhang,Mary C Clark,Vaibhav Agrawal,Hoda Pourhassan,Paul B Koller,Ahmed Aribi,Haris Ali,Amanda Blackmon,Salman Otoukesh,Karamjeet S. Sandhu,Brian J. Ball,Shukaib Arslan,Andrew S. Artz,Idoroenyi Amanam,Monzr M. Al Malki,Amandeep Salhotra,Tibor J Kovacsovics,Lindsey A Murphy,Michelle Afkhami,Dat Ngo,Jose Tinajero,Zhaohui Gu,Pamela S. Becker,Ryotaro Nakamura,Anthony S. Stein,Guido Marcucci,Stephen J. Forman,Vinod A. Pullarkat
Research Article January 16 2025
Phase 1 Study of Quercetin, a Natural Antioxidant in Children and Young Adults with Fanconi Anemia (FA)
Parinda A Mehta,Adam S Nelson,Sara Katharine Loveless,Adam Lane,Tsuyoshi Fukuda,Ashley Teusink-Cross,Deborah Elder,Denise Lagory,Erica Miller,Jose A. Cancelas,Jonathan Howell,Junfang Zhao,Kana Mizuno,Kasiani C. Myers,Kelly Lake,Kelly McIntosh,Kenneth D. R. Setchell,Nathan Luebbering,Stephanie Edwards,Tafadzwa Chihanga,Susanne I Wells,Stella M Davies
Research Article January 16 2025
Phase I study of CD19 CAR T-cell therapy harboring a fully human scFv in CAR-naïve adult B-ALL patients
Jordan Gauthier,Emily C. Liang,Jennifer J. Huang,Erik Lesley Kimble,Alexandre V. Hirayama,Salvatore Fiorenza,Jenna M Voutsinas,Qian (Vicky) Wu,Carla A Jaeger-Ruckstuhl,Barbara S. Pender,Delaney R. Kirchmeier,Aiko Torkelson,Kristina Braathen,Ryan Basom,Mazyar Shadman,Noam E. Kopmar,Ryan D. Cassaday,Stanley R. Riddell,David G Maloney,Cameron J Turtle
Research Article January 15 2025
N-glycan shielded CUB domains of ADAMTS13 prevent binding of C-terminal antibodies in patients with immune-mediated TTP
Research Article January 14 2025
Impacts of donor age and HLA mismatch on HCT outcomes differ according to the donor CMV serostatus in unrelated allo-HCT
Research Article January 14 2025
Large clones of Clonal Hematopoiesis affect outcome in Mantle Cell Lymphoma: Results from The FIL MCL0208 Clinical Trial
Simone Ragaini,Anna Galli,Elisa Genuardi,Martina Gandossini,Beatrice Alessandria,Aurora Maria Civita,Andrea Evangelista,Enrico Amaducci,Vittorio Stefoni, Dr,Federica Cavallo,Filippo Ballerini,Benedetta Puccini,Daniele Vallisa,Mariagrazia Michieli,Anna Pascarella,Angelo D. Palmas,Caterina Patti,Elisa Lucchini,Maria Grazia Careddu,Michele Merli,Massimiliano Postorino,Carola Boccomini,Monica Balzarotti, MD,Vittorio Ruggero Ruggero Zilioli,Maria Gomes da Silva,Benedetto Bruno,Ettore Rizzo,Marco Ladetto,Luca Malcovati,Simone Ferrero
Research Article January 7 2025
Extended clinical phenotypes and treatment modalities in 32 JAGN1-deficient patients. A multicenter study by EBMT IEWP
Julia Fekadu-Siebald,Emilia Salzmann-Manrique,Jan Robert Heusel,Andre Willasch,Fabian Hauck,Luis Ignacio Gonzalez-Granado,Zahra Chavoshzadeh,Samin Sharafian,Franziska Cuntz,Safa Baris,Andrea Finocchi,Mattia Algeri,Roya Sherkat,Maja Klaudel-Dreszler,Cornelia Zeidler,Christine Bellanné-Chantelot,Gerhard Kindle,Blandine Beaupain,Catherine Paillard,Markus G Seidel,Peter Bader,Michael H Albert,Bénédicte Neven,Jean Donadieu,Shahrzad Bakhtiar
Research Article January 7 2025
Pre-treatment Pulmonary Function Testing Has Limited Utility In B-cell Lymphoma Treated with CD19 CAR T-cells
Research Article January 7 2025
Patient-Reported Improvements in Patients with PNH Treated with Iptacopan from Two Phase 3 Studies
Research Article January 7 2025
Maximum Tumor Diameter is Associated with Relapse Risk in Limited-Stage Hodgkin Lymphoma: An International Study
Research Article December 20 2024
Platelet spleen tyrosine kinase is a key regulator of anti-PF4 antibody-induced immunothrombosis
Research Article December 11 2024
Safety and Efficacy of Glofitamab for Relapsed/Refractory Large B-Cell Lymphoma in a Multinational Real-World Study
Evgenii Shumilov,Rebecca Wurm-Kuczera,Andrea Kerkhoff,Meng Wang,Thomas Melchardt,Udo Holtick,Ulrike Bacher,Philipp B. Staber,Paolo Mazzeo,Corinna Leng,David Böckle,Alexander Sebastian Hölscher,Joseph Kauer,Natalia Rotter,Vladan Vucinic,Jakob D. Rudzki,David Nachbaur,Veit L. Bücklein,Ulf Schnetzke,Isabelle Krämer,Kai Wille,Alexander Hasse,Bastian von Tresckow,Mathias Hänel,Christian Koenecke,Giuliano Filippini Velazquez,Andreas Viardot,Christoph Schmid,Lorenz Thurner,Dominik Wolf,Marion Subklewe,Martin Dreyling,Peter Dreger,Sascha Dietrich,Ulrich Keller,Ulrich Jaeger,Richard Greil,Thomas Pabst,Georg Lenz,Björn Chapuy
Research Article November 15 2024
ATP citrate lyase is an essential player in the metabolic rewiring induced by PTEN loss during T-ALL development.
Research Article August 12 2024