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Research Article October 21 2025
Modeling Response to High-Purity Von Willebrand Factor: Toward Tailored Dosing During Surgery in von Willebrand Disease
Research Article October 20 2025
Heme and hemozoin induce platelet cell death through UPR-induced apoptosis and ferroptosis in vivax malaria
Milena Tavares Gomes,Isabel Matos Medeiros-de-Moraes,Adriana Vieira-de-Abreu,Isaclaudia G. Azevedo-Quintanilha, Dr.,Thayane Modesto Fontes,Alan De Brito Carneiro,Pedro Azambuja,Neal D. Tolley,Jesse W Rowley,Barbara Albuquerque Carpinter,Marcelo U Ferreira,Raquel Muller Gonçalves-Lopes,Vinicius Novaes Rocha,Ana Lucia Rosa Nascimento,Wanessa Araújo Carvalho,Kézia K. G. Scopel,Robert A Campbell,Patricia Torres Bozza,Andrew S. Weyrich,Guy A. Zimmerman,Marcus V.G. Lacerda,Hugo C. Castro Faria Neto,Eugenio Damaceno Hottz
Research Article October 20 2025
Short- and long-term effects of transfusion in beta-thalassemia: a longitudinal study of transfusion efficiency factors
Konstantina Theocharaki,Ioanna Barla,Sophia Delicou,Alkmini T Anastasiadi, Dr.,Vassilis L Tzounakas,Stella Rouvela,Georgia Tzafa,Elli-Anna Stylianaki,Efthymia-Ioanna Koufogeorgou,Theodore Gousdovas,Efthymia Pavlou,Ioannis V Kostopoulos,Nikolaos Simantiris,Niki Vassilaki,Maria Moraki,Konstantinos Stamoulis,Ersi Voskaridou,Efrosyni Nomikou,Ourania Tsitsilonis,Nikolaos Thomaidis,Evagelos Gikas,Marianna Politou,Veroniki Komninaka,Marianna H Antonelou
Letter October 20 2025
Danazol treatment for telomere biology disorders: long-term results of a phase I/II study
Research Article October 15 2025
Diagnostic sequencing identifies high-risk markers and mechanisms of resistance to guide immunotherapy selection.
Letter October 15 2025
AL Amyloidosis: A Real-World Experience with CAR-T Cell Therapy
Melinda SY Tan,Rahma Warsame,Ricardo D Parrondo,Eli Muchtar,Taxiarchis V. Kourelis,Francis K Buadi,Wilson I Gonsalves,Joselle Cook,Prashant Kapoor,Suzanne R Hayman,David Dingli,Moritz Binder,Nelson Leung,Vivek Roy,Taimur Sher,Erin Erin Wiedmeier-Nutor,Saurabh Chhabra,Rafael Fonseca,Nadine Abdallah,S. Vincent Rajkumar,Shaji K Kumar,Morie A Gertz,Yi Lin,Angela Dispenzieri
Research Article October 15 2025
Azathioprine or mycophenolate mofetil for pediatric autoimmune cytopenia: A propensity score-matched study
Thomas Pincez,Helder Fernandes,Guy Leverger,Vincent Barlogis,Mony Fahd,Nathalie Garnier,Catherine Paillard,Corinne Guitton,Wadih Abou Chahla,Marlène Pasquet,Eric Jeziorski,Martin Castelle,Sophie Bayart,Isabelle Pellier,Caroline Thomas,Anne Pagnier,Joy Benadiba,Valérie Li Thiao Te,Nathalie Cheikh,Julien Lejeune,Marianna Deparis,Aude Marie-Cardine,Pascal Chastagner,Claire Desplantes,Frédéric Millot,Philippe Vic,Sandrine Thouvenin Doulet,Christophe Piguet,Claire Pluchart,Thierry M Leblanc,Sebastien Heritier,Nathalie Aladjidi
Review Article October 10 2025
Primary and Secondary Stroke Prophylaxis in Children with Sickle Cell Anemia: A Meta-Analysis
Research Article October 10 2025
Population-Wide Introduction of Dose-Adjusted EPOCH-R In High-grade B-cell Lymphoma with MYC/BCL2 Rearrangements, DLBCL Morphology
Waleed Alduaij,Laurie H. Sehn,Jean-Nicolas Champagne,Brett Collinge,Susana Ben-Neriah,Aixiang Jiang,Laura K Hilton,Merrill Boyle,Barbara Meissner,Graham W. Slack,Pedro Farinha,Jeffrey W. Craig,Kerry J. Savage,Diego Villa,Alina S. Gerrie,Ciara L Freeman,Andrew J Mungall,Christian Steidl,David W. Scott
Research Article October 10 2025
Targeting macrophages prevents alloantibody-mediated platelet clearance in a murine model of transfusion refractoriness
Research Article October 10 2025
Survival in Adults with High Risk TA-TMA - A Comparative Analysis of Narsoplimab Versus Supportive Care
Research Article October 8 2025
Myeloid landscape profiling identifies DLBCL-specific suppressive macrophages colocalized with blood endothelial cells
Juliette Ferrant,Simon Le Gallou,Francine Padonou,Charlotte Dubec-Fleury,Simon Léonard,Ilenia Papa,Charles Brottier,Celine Pangault,Anne Barthel,Vincent Launay,Guillaume Manson,Benedicte Hoareau,Laurent Deleurme,Celine Monvoisin,Benoit Alaud,Margaret A. Shipp,Nathalie Van Acker,Camille Laurent,Francisco Llamas Gutierrez,Henri-Alexandre Michaud,Nathalie Bonnefoy,Thierry Pécot,Karin Tarte,Mikael Roussel
Research Article October 8 2025
Polatuzumab vedotin in CNS lymphoma: proof-of-concept study for blood-brain barrier penetration
Lei Gao,Avyakta Kallam,Geoffrey Shouse,John H. Baird,Stacy Pak,Yue Qin,Joo Y. Song,Guido Marcucci,Lucy Y. Ghoda,Claire Guillen,Suk-Joon Hyung,Ola M. Saad,Helen Davis,Randall Dere,Connie Lee Lee Batlevi,Joshua Meinert,L. Elizabeth E Budde,Alexey V Danilov,Alex F. F. Herrera,Larry W Kwak,Stephen J Forman,James K. Godfrey
Review Article October 8 2025
Predictive markers for the efficacy of CAR T-cell therapy: the interplay of CAR-T fitness and systemic immunity
Research Article October 8 2025
Transplantation in lower risk MDS patients: a prospective phase 2 trial based on donor availability
Marie Sebert,Sylvain Thepot,Thomas Cluzeau,Nicolas Duployez,Thibaud Lefebvre,Cendrine Chaffaut,Corentin Orvain,Michael Loschi,Pierre Peterlin,Patrice Chevallier,Maud D'Aveni,Marie-Thérèse Rubio,Odile Rauzy,Anne Huynh,Amandine Charbonnier,Rosa Sapena,Fatiha Chermat,Patrice Ceballos,Gaelle Fossard,Stephanie Nguyen,Sophie Park,Lionel Adès,Régis Peffault De Latour,Claude Preudhomme,Pierre Fenaux,Sylvie Chevret,Marie Robin
Research Article October 7 2025
Germline LCP1 mutations cause immunodeficiency with neutropenia, monocytopenia, lymphopenia and defective cytokinesis
Thijs van Bergen,Dennis Bosch,Christine Bellanné-Chantelot,Roger Mulet-Lazaro,Jacob R. Bledsoe,Lanpeng Chen,Hans W.J. de Looper,Claire van Dijk,Mariëtte ter Borg,Eric Bindels,Remco Hoogenboezem,Onno Roovers,Patricia A Olofsen,Marije Bartels,Joris M. van Montfrans,Puck Breed,Elisabeth Salzer,Marloes G. Holierhoek,Brigittie Nelken,Blandine Beaupain,Mark Daniel Fleming,Akiko Shimamura,Marc H.G.P. Raaijmakers,Jean Donadieu,Peter E. Newburger,Ivo P. Touw,Anna M Aalbers
Research Article October 7 2025
Risk stratification of diffuse large B-cell lymphoma patients using plasma NMR-based metabolomics at diagnostic
Aurélie Montagne,Gildas Bertho,Thomas Papastergiou,Loïc Chartier,Romain Ricci,Fabrice Jardin,Herve Ghesquieres,Cédric Rossi,Franck Morschhauser,Corinne Haioun,Vincent Ribrag,Pierre Feugier,Gabriel Brisou,Lucie Obéric,Philippe Gaulard,Nicolas Giraud,Younès Bennani,Catherine Thieblemont,Véronique I Baud
Research Article October 7 2025
Ablation of CD38 in Multiple Myeloma Cells Leads to an Aggressive Phenotype in a Mouse Xenograft Model
Research Article October 7 2025
Phase I Study of Rogocekib in Patients with Relapsed or Refractory Hematologic Malignancies
Research Article October 6 2025
FLT3-ITD measurable residual disease from the QuANTUM-First trial
Mark J. Levis,Harry P. Erba,Pau Montesinos,Hee-Je Kim,Radovan Vrhovac,Elzbieta Patkowska,Pavel Zak,Po-Nan Wang,Jaime E. Connolly Rohrbach, PhD,Ken Chang,Li Liu,Yasser Mostafa Kamel,Karima Imadalou,Arnaud Lesegretain,Jorge E. Cortes,Mikkael A Sekeres,Hervé Dombret,Sergio Amadori,Jianxiang Wang,Richard F. Schlenk,Alexander E. Perl
Research Article October 6 2025
Matched Unrelated vs Haploidentical Donor Hematopoietic Cell Transplantation Using Post-Transplant Cyclophosphamide
Dipenkumar Modi,Yosra M. Aljawai,Todd E DeFor,Caitrin Bupp,Monzr M. Al Malki,Javier Bolaños-Meade,Mahasweta Gooptu,Antonio M Jimenez Jimenez,Hongtao Liu,Felix Mensah,Marco Mielcarek,Brian C. Shaffer,Bronwen E. Shaw,Stephen R. Spellman,Heather E Stefanski,Jeffery J. Auletta,Steven M. Devine,Farhad Khimani,Ramzi Abboud
Research Article October 6 2025
CAR HEMATOTOX independently predicts outcomes after CD19 CAR-T therapy for acute lymphoblastic leukemia
Yannis K. Valtis,Chenyu Lin,David Nemirovsky,Sean M. Devlin,Kai Rejeski,Kevin J. Curran,Xiuyan Wang,Nirali N. Shah,Nikeshan Jeyakumar,Katharine Miller,Amy Zhang,Vamsi K. Kota,Ali Al Darobi,Ibrahim N. Muhsen,Joshua P Sasine,Ibrahim Aldoss,Anjali S Advani,Ran Reshef,Evan C. Chen,Noam E. Kopmar,Stephanie B. Tsai,Talal Hilal,Bijal D Shah,Rawan G. Faramand,Melhem M. Solh,Virginia Tan,Evandro D Bezerra,Minoo Battiwalla,Aravind Ramakrishnan,John Mathews,Paul J Shaughnessy,Luke Mountjoy,Rasmus T. Hoeg,Kaitlyn C. Dykes,Aaron C Logan,Muthu Kumaran,Marc S. Schwartz,Sean I Tracy,Jozal Moore,Silvina Odstrcil Bobillo,Noelle V Frey,Matthew P Connor,Abdullah Ladha,Bhagirathbhai Dholaria,Katherine C. Sutherland,Gregory W. Roloff,Lori S. Muffly,Jae H Park
Letter September 30 2025
Liberalizing Hospital Proximity Requirements for Children/Young Adults with Low Burden B-ALL Receiving Tisagenlecleucel
Lauren Elizabeth Appell,Christina Baggott,Khanh Nguyen,Snehit Prabhu,Holly L Pacenta,Samuel John,Vanessa A. Fabrizio,Christine L. Phillips,Jenna Rossoff,Julie-An M. Talano,Amy Moskop,Rachel Phelan,Susanne H.C. Baumeister,Michael R Verneris,Erin M. Hall,Gary Douglas Myers,Nicole A. Karras,Stacy Cooper,Muna Qayed,Sunil Sudhir Raikar,Lena E. Winestone,Michelle L. Hermiston,Prakash Satwani,Christa Krupski,Amy Keating,Danielle Novetsky Friedman,Kevin J. Curran,Alex Hoover,Margaret L. MacMillan,Christen L Ebens,Archana Ramgopal,April L Rahrig,Crystal L. Mackall,Theodore W. Laetsch,Liora M. Schultz
Review Article September 30 2025
Antibody-DNA nanostructure conjugates integrate doxorubicin and rituximab to enhance therapeutic efficacy for DLBCL
Research Article September 30 2025
Population-scale Analysis Reveals Germline Loss of SERPING1 (C1-Inhibitor) is a Polyphenotypic Thrombotic Disorder
Research Article September 30 2025
Outcome of Patients with Mantle Cell Lymphoma after Failure of Anti-CD19 CAR-T Cell Therapy: A Descar-T Study By Lysa Group
Research Article September 30 2025
Safety and Efficacy of Combining Midostaurin and Gemtuzumab Ozogamicin with Induction Chemotherapy in FLT3 mutated AML
Nigel H. Russell,Jad Othman,Oliver Sebastian Cumming,Abin Thomas,Aditya Tedjaseputra,Nicola Potter,Jelena Jovanovic,Amanda Frances Gilkes,Leona Batten,Joanna Canham,Emily L Hinson,Manohursingh Runglall,Phoebe Aucken,Panagiotis Kottaridis,James Durrell Cavenagh,Claire Arnold,Sylvie D Freeman,Mike Dennis,Steven Knapper,Richard James Dillon
Research Article September 30 2025
Hydroxyurea pharmacokinetics in children with sickle cell anemia across different global populations
Alexandra Power-Hays,Kathryn E. McElhinney,Thomas N Williams,George Mochamah,Peter Olupot-Olupot,George Paasi,Marvin E. Reid,Angela E Rankine-Mullings,Robert O Opoka,Chandy C. John,Patrick T. McGann,Charles T. Quinn,Nieko C Punt,Luke R. Smart,Susan E. Stuber,Teresa S. Latham,Alexander A. Vinks,Russell E. Ware
Letter September 30 2025
Dual Anti-CD19/22 and Anti-BCMA CAR-T cell therapy in a patient with multiple myeloma and secondary B-ALL
Research Article September 24 2025
Tumor-Specific Immune Responses and Biomarkers in pediatric High-Risk Hodgkin Lymphoma Patients
Letter September 24 2025
Age-Based Pegaspargase Dosing is Safe and Achieves Therapeutic Levels in Infants with ALL: Report from COG AALL15P1
Research Article September 24 2025
Patient-reported outcomes in patients with hematologic malignancies treated with CAR T-cell therapy in Europe
Elise RA Pennings,Anne Mea Spanjaart,Frederick W. Thielen,Simone Oerlemans,Anna Fleischer,Carmen Sanges,Maria Gomes Da Silva,Yolanda Cabrerizo,Pacôme Lecot,Lutgart Roux-Opstaele,Caroline Dreuillet,Eglys Gonzalez-Marcano,Olga Millán,Ulrich Jaeger,Julio Delgado,Maik Luu,Barbara Huber,Margot Lorrain,Mariana Galhardas Pina,Andreas Kremer,Natacha Bolanos,Solène Clavreul,Samantha Nier,Roberto D.K. Liu,Birgit I. Lissenberg-Witte,Sébastien Anguille,Marie Robin,Emma C. Morris,Anna Sureda,Marie Préau,Myriam Pannard,Geertruida H. De Bock,Scott S. Wagers,Hélène Trebeden-Negre,Delphine Maucort-Boulch,Michael Hudecek,Carin A. Uyl-de Groot,Marie José Kersten
Research Article September 24 2025