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Research Article October 30 2025
Derivation and External Validation of a Venous Thromboembolism Risk Prediction Model in Asparaginase-Treated ALL
Daniela R. Anderson,Radhika Gangaraju,Wafik G. Sedhom,Eva N. Hamulyák,Tzu-Fei Wang,Kristen M O'Dwyer,Brian J. Carney,Chandrasekar Muthiah,Michaela Liedtke,Talha Badar,Shai Shimony,Renana Robinson,Kristen Sanfilippo,Andriy Derkach,Shira Naomi Dinner,Bart J. Biemond,David Nemirovsky,Leah A. Goldberg,Anjani D. Kapadia,Hannah Levavi,Michal Bar-Natan,Grace Van Hyfte,Karan Bansal,Marc Carrier,Jill Fulcher,Anke M. Gerrits,Mark R. Litzow,Selina M Luger,Guru Subramanian Guru Murthy,Marlise R. Luskin,Ofir Wolach,William Shomali,Jeffrey I. Zwicker,Wendy A Stock,Avi Leader
Research Article October 29 2025
Long term Follow-up of Zevor-cel in Patients with Relapsed/Refractory Multiple Myeloma
Research Article October 28 2025
Comparative Analysis of CRISPR-Cas9, lentiviral transduction, and base editing for sickle cell disease in a murine model
Research Article October 28 2025
OPTICAL GENOME MAPPING IN MYELOFIBROSIS: ENHANCING PROGNOSTIC ACCURACY THROUGH HIGH-RESOLUTION GENOMIC PROFILING.
Álvaro Díaz González,Elvira Mora,Marta Garrote,Gonzalo Carreño-Tarragona,Marta Salido Galeote,Irene Pastor-Galán,Ruth Stuckey,Adela Cisneros Sala,Jose Antonio Domingo-Monfort,Nerea Uresandi,Nagore Argoitia-Ituarte,Gayane Avetisyan,Cristian Garcia-Ruiz,Neus Torres Hernandez,Santiago Furió,Eduardo Arellano-Rodrigo,Noemí Álvarez,Patricia Velez,Eva Villamon,Adrián Segura-Díaz,Rosa Ayala,Blanca Espinet,Alberto Álvarez-Larrán,Juan Carlos Hernandez-Boluda,Esperanza Such
Research Article October 24 2025
Intranasal Fentanyl and Impact of an Emergency Department Pain Protocol for Sickle Cell Disease on Hospitalization Rates
Research Article October 24 2025
Central Nervous System Involvement in CLL: An International Retrospective Study by ERIC, the European Research Initiative on CLL
Thomas Chatzikonstantinou,Mariia Mikhaleva,Christian Brieghel,Christina Papangelou,Evangelia Minga,Celso Arrais-Rodrigues,Sotiria Dimou-Besikli, Dr,Amalia Cerutti,Michael Doubek,Lisbeth Enggaard,Blanca Espinet,Blanca Ferrer-Lores,Jose Antonio Garcia Vela,Massimo Gentile,Eva Gimeno Vazquez,Odit Gutwein,Yair Herishanu,Paula Jabłonowska-Babij,Ozren Jaksic,Pär Josefsson,Elżbieta Kalicińska,Maria Kislova,Enrico Lista,Ioannis Kotsianidis,Juan Marquet,Enrica Antonia Antonia Martino,Ciaran P McAuley,Maria J Mela-Osorio,Riccardo Moia,Claudia Mosquera Rubal,Eugene A. Nikitin,Miguel Arturo Pavlovsky,Verena Pfister,Emine Merve Savaş,Lydia Scarfò,Matjaz Sever,Lev Shvidel,Martin Simkovic,Niki Stavroyianni,Persefoni Talimtzi,Antigoni Tranidou,Andrea Visentin,George Vrachiolias,Ewa Wasik-Szczepanek,Tomasz Wróbel,Münci Yağcı,Alessandro Cellini,Anastasia Chatzidimitriou,Gianluca Gaidano,Mary Ann Anderson,Matthew S. Davids,Jennifer R. Brown,Carsten Utoft Niemann,Kostas Stamatopoulos,Paolo Ghia,Inhye E. Ahn,Maya Koren-Michowitz
Research Article October 22 2025
Late failure of aggressive B-cell lymphoma following CAR T-cell therapy: a LYSA study from the DESCAR-T registry
Federico Erbella,Emmannuel Bachy,Guillaume Cartron,Elodie Gat,Guillaume Manson,Franck Morschhauser,Francois-Xavier Gros,Louise Roulin,Benoit Tessoulin,Pierre Bories,Olivier Tournilhac,Laure Ricard,Stephanie Guidez,Sylvain Choquet,René-Olivier Casasnovas,Gabriel Brisou,Arnaud Campidelli,Cristina Castilla-Llorente,Fabrice Jardin,Emmanuel Gyan,Blandine Guffroy,Julie Abraham,Justine Decroocq,Adrien Chauchet,Magalie Joris,Fabien Claves,Sylvain Carras,Gaelle Guillerm,Michael Loschi,Olivier Hermine,Aline Schmidt,Steven Le Gouill,Roch Houot,Roberta Di Blasi
Letter October 22 2025
Outcomes of Bispecific Antibodies After CAR T-Cell Failure for Large B-cell Lymphoma- Results from the ABC Consortium
Megan Melody,Natalie S. Grover,Stephanie Franco,Jason T. Romancik,Matthew J. Cortese,Tamara K Moyo,Rahul S Bhansali,Thomas A Ollila,Vaishalee P Kenkre,Lindsey A. Fitzgerald,Brian T Hess,Matthew J. Matasar,Geoffrey Shouse,Kaitlin Annunzio,Megan M. Herr,James A Davis,Christy Jesme,Ari Pelcovits,Jonathan Moreira,Shuo Ma,Jane N Winter,Adam Yuh Lin,Alexey V Danilov,Ishan Roy,Stefan K. Barta,Leo I. Gordon,Deborah M Stephens,Jonathon B Cohen,Narendranath Epperla,Reem Karmali
Research Article October 22 2025
Efficacy and Safety of Vemircopan as Monotherapy in Patients With Paroxysmal Nocturnal Hemoglobinuria
Research Article October 22 2025
Prognostic Value of Inflammation-Based Scores in R/R LBCL Patients Treated with CD3xCD20 Bispecific T-Cell Engagers
Giulia Magno,Kai Rejeski,Giulia Rappa,Sophia Stock,Alessandra Holzem,Maria Landwehr,Maximilian Seib,Nadine Kutsch,Jamila Mammadova,Stephanie Mayer,Shlomzion Aumann,Jonas Van Ham,Shimrit Ringelstein-Harlev,Giuliano Filippini Velazquez,Rebecca Wurm-Kuczera,Julia Katharina Scholz,Uri Greenbaum,Sandeep S Raj,Roni Shouval,Fabian Müller,Bjoern Chapuy,Christoph Schmid,Ofrat Beyar-Katz,Vibeke KJ Vergote,Hendrik Poeck,Ning Dong,Udo Holtick,Ron Ram,Thomas Pabst,Evgenii Shumilov,Georg Lenz,Gloria Iacoboni,Pere Barba,Veit L. Bücklein,Marion Subklewe
Research Article October 22 2025
Molecular Risk Markers Define Risk of Relapse in Myeloid Leukemia of Down syndrome Beyond Measurable Residual Disease
Jason N Berman,Anupam Verma,Shelton A. Viola,Todd Alonzo,Yi-Cheng Wang,Lisa Eidenschink Brodersen,Michael R Loken,Amy K. Beckman,Betsy A Hirsch,Susana Raimondi,Karen M. Chisholm,Xiaotu Ma,Rhonda E. Ries,Soheil Meshinchi,Alan S Gamis,Reuven J Schore,Jeffrey W. Taub,E Anders Kolb,Todd M Cooper,Johann K. Hitzler
Research Article October 21 2025
Pyruvate kinase M2 promotes venous thrombosis by enhancing SNAP23-mediated platelet exocytosis and consequent NETosis
Research Article October 21 2025
The Na/K-ATPase Alpha-1 Subunit Fine-Tunes Platelet P2Y12 Function and Mediates Sex-Dimorphism-Associated Thrombosis
Research Article October 21 2025
Childhood isolated C3d-positive AIHA: favorable prognosis but rare relapse or associated immunodeficiency
Marion Blachez,Nathalie Aladjidi,Thomas Modot,Helder Fernandes,Nathalie Garnier,Pascal Chastagner,Sophie Bayart,Corinne Armari-Alla,Christophe Piguet,Marlène Pasquet,Catherine Paillard,Claire Pluchart,Corinne Guitton,Caroline Thomas,Vincent Barlogis,Isabelle Pellier,Jean-Louis Louis Stephan,Joy Benadiba,Eric Jeziorski,Marianna Deparis,Liana Carausu,Nathalie Cheikh,Valérie Li Thiao Te,Julien Lejeune,Aude Marie-Cardine,Frédéric Millot,Wadih Abou Chahla,Sophie Gay,Aurélia Alimi,Arnaud Petit,Martin Castelle,Despina Moshous,Capucine Picard,Frédéric Rieux-Laucat,Thierry M Leblanc,Stéphane Ducassou,Guy Leverger,Mony Fahd,Sebastien Heritier
Research Article October 21 2025
Modeling Response to High-Purity Von Willebrand Factor: Toward Tailored Dosing During Surgery in von Willebrand Disease
Research Article October 20 2025
Heme and hemozoin induce platelet cell death through UPR-induced apoptosis and ferroptosis in vivax malaria
Milena Tavares Gomes,Isabel Matos Medeiros-de-Moraes,Adriana Vieira-de-Abreu,Isaclaudia G. Azevedo-Quintanilha, Dr.,Thayane Modesto Fontes,Alan De Brito Carneiro,Pedro Azambuja,Neal D. Tolley,Jesse W Rowley,Barbara Albuquerque Carpinter,Marcelo U Ferreira,Raquel Muller Gonçalves-Lopes,Vinicius Novaes Rocha,Ana Lucia Rosa Nascimento,Wanessa Araújo Carvalho,Kézia K. G. Scopel,Robert A Campbell,Patricia Torres Bozza,Andrew S. Weyrich,Guy A. Zimmerman,Marcus V.G. Lacerda,Hugo C. Castro Faria Neto,Eugenio Damaceno Hottz
Research Article October 20 2025
Short- and long-term effects of transfusion in beta-thalassemia: a longitudinal study of transfusion efficiency factors
Konstantina Theocharaki,Ioanna Barla,Sophia Delicou,Alkmini T Anastasiadi, Dr.,Vassilis L Tzounakas,Stella Rouvela,Georgia Tzafa,Elli-Anna Stylianaki,Efthymia-Ioanna Koufogeorgou,Theodore Gousdovas,Efthymia Pavlou,Ioannis V Kostopoulos,Nikolaos Simantiris,Niki Vassilaki,Maria Moraki,Konstantinos Stamoulis,Ersi Voskaridou,Efrosyni Nomikou,Ourania Tsitsilonis,Nikolaos Thomaidis,Evagelos Gikas,Marianna Politou,Veroniki Komninaka,Marianna H Antonelou
Letter October 20 2025
Danazol treatment for telomere biology disorders: long-term results of a phase I/II study
Research Article October 15 2025
Diagnostic sequencing identifies high-risk markers and mechanisms of resistance to guide immunotherapy selection.
Letter October 15 2025
AL Amyloidosis: A Real-World Experience with CAR-T Cell Therapy
Melinda SY Tan,Rahma Warsame,Ricardo D Parrondo,Eli Muchtar,Taxiarchis V. Kourelis,Francis K Buadi,Wilson I Gonsalves,Joselle Cook,Prashant Kapoor,Suzanne R Hayman,David Dingli,Moritz Binder,Nelson Leung,Vivek Roy,Taimur Sher,Erin Erin Wiedmeier-Nutor,Saurabh Chhabra,Rafael Fonseca,Nadine Abdallah,S. Vincent Rajkumar,Shaji K Kumar,Morie A Gertz,Yi Lin,Angela Dispenzieri
Research Article October 15 2025
Azathioprine or mycophenolate mofetil for pediatric autoimmune cytopenia: A propensity score-matched study
Thomas Pincez,Helder Fernandes,Guy Leverger,Vincent Barlogis,Mony Fahd,Nathalie Garnier,Catherine Paillard,Corinne Guitton,Wadih Abou Chahla,Marlène Pasquet,Eric Jeziorski,Martin Castelle,Sophie Bayart,Isabelle Pellier,Caroline Thomas,Anne Pagnier,Joy Benadiba,Valérie Li Thiao Te,Nathalie Cheikh,Julien Lejeune,Marianna Deparis,Aude Marie-Cardine,Pascal Chastagner,Claire Desplantes,Frédéric Millot,Philippe Vic,Sandrine Thouvenin Doulet,Christophe Piguet,Claire Pluchart,Thierry M Leblanc,Sebastien Heritier,Nathalie Aladjidi
Review Article October 10 2025
Primary and Secondary Stroke Prophylaxis in Children with Sickle Cell Anemia: A Meta-Analysis
Research Article October 10 2025
Population-Wide Introduction of Dose-Adjusted EPOCH-R In High-grade B-cell Lymphoma with MYC/BCL2 Rearrangements, DLBCL Morphology
Waleed Alduaij,Laurie H. Sehn,Jean-Nicolas Champagne,Brett Collinge,Susana Ben-Neriah,Aixiang Jiang,Laura K Hilton,Merrill Boyle,Barbara Meissner,Graham W. Slack,Pedro Farinha,Jeffrey W. Craig,Kerry J. Savage,Diego Villa,Alina S. Gerrie,Ciara L Freeman,Andrew J Mungall,Christian Steidl,David W. Scott
Research Article October 10 2025
Targeting macrophages prevents alloantibody-mediated platelet clearance in a murine model of transfusion refractoriness
Research Article October 10 2025
Survival in Adults with High Risk TA-TMA - A Comparative Analysis of Narsoplimab Versus Supportive Care
Research Article October 8 2025
Myeloid landscape profiling identifies DLBCL-specific suppressive macrophages colocalized with blood endothelial cells
Juliette Ferrant,Simon Le Gallou,Francine Padonou,Charlotte Dubec-Fleury,Simon Léonard,Ilenia Papa,Charles Brottier,Celine Pangault,Anne Barthel,Vincent Launay,Guillaume Manson,Benedicte Hoareau,Laurent Deleurme,Celine Monvoisin,Benoit Alaud,Margaret A. Shipp,Nathalie Van Acker,Camille Laurent,Francisco Llamas Gutierrez,Henri-Alexandre Michaud,Nathalie Bonnefoy,Thierry Pécot,Karin Tarte,Mikael Roussel
Research Article October 8 2025
Polatuzumab vedotin in CNS lymphoma: proof-of-concept study for blood-brain barrier penetration
Lei Gao,Avyakta Kallam,Geoffrey Shouse,John H. Baird,Stacy Pak,Yue Qin,Joo Y. Song,Guido Marcucci,Lucy Y. Ghoda,Claire Guillen,Suk-Joon Hyung,Ola M. Saad,Helen Davis,Randall Dere,Connie Lee Lee Batlevi,Joshua Meinert,L. Elizabeth E Budde,Alexey V Danilov,Alex F. F. Herrera,Larry W Kwak,Stephen J Forman,James K. Godfrey
Review Article October 8 2025
Predictive markers for the efficacy of CAR T-cell therapy: the interplay of CAR-T fitness and systemic immunity
Research Article October 8 2025
Transplantation in lower risk MDS patients: a prospective phase 2 trial based on donor availability
Marie Sebert,Sylvain Thepot,Thomas Cluzeau,Nicolas Duployez,Thibaud Lefebvre,Cendrine Chaffaut,Corentin Orvain,Michael Loschi,Pierre Peterlin,Patrice Chevallier,Maud D'Aveni,Marie-Thérèse Rubio,Odile Rauzy,Anne Huynh,Amandine Charbonnier,Rosa Sapena,Fatiha Chermat,Patrice Ceballos,Gaelle Fossard,Stephanie Nguyen,Sophie Park,Lionel Adès,Régis Peffault De Latour,Claude Preudhomme,Pierre Fenaux,Sylvie Chevret,Marie Robin
Research Article October 7 2025
Germline LCP1 mutations cause immunodeficiency with neutropenia, monocytopenia, lymphopenia and defective cytokinesis
Thijs van Bergen,Dennis Bosch,Christine Bellanné-Chantelot,Roger Mulet-Lazaro,Jacob R. Bledsoe,Lanpeng Chen,Hans W.J. de Looper,Claire van Dijk,Mariëtte ter Borg,Eric Bindels,Remco Hoogenboezem,Onno Roovers,Patricia A Olofsen,Marije Bartels,Joris M. van Montfrans,Puck Breed,Elisabeth Salzer,Marloes G. Holierhoek,Brigittie Nelken,Blandine Beaupain,Mark Daniel Fleming,Akiko Shimamura,Marc H.G.P. Raaijmakers,Jean Donadieu,Peter E. Newburger,Ivo P. Touw,Anna M Aalbers
Research Article October 7 2025
Risk stratification of diffuse large B-cell lymphoma patients using plasma NMR-based metabolomics at diagnostic
Aurélie Montagne,Gildas Bertho,Thomas Papastergiou,Loïc Chartier,Romain Ricci,Fabrice Jardin,Herve Ghesquieres,Cédric Rossi,Franck Morschhauser,Corinne Haioun,Vincent Ribrag,Pierre Feugier,Gabriel Brisou,Lucie Obéric,Philippe Gaulard,Nicolas Giraud,Younès Bennani,Catherine Thieblemont,Véronique I Baud
Research Article October 7 2025