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Maria Pia Cicalese
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Journal Articles

Interleukin-1 blockade in patients with Wiskott-Aldrich syndrome: a retrospective multinational case series

Clinical Trials & Observations Brief Report
Samuele Naviglio, Maria Pia Cicalese, Elizabeth Rivers, Francesca Ferrua, Carmem Bonfim, Sabina Cenciarelli, Kai-Ning Cheong, Maura Faraci, Stefano Giardino, Sujal Ghosh, Pamela P. Lee, Paula Teixeira Lyra, Roland Meisel, Valentina Sofia, Antimo Tessitore, Alberto Tommasini, Erica Valencic, Tanja Christine Vallée, Stefano Volpi, Austen J. Worth, Marco Rabusin, Michael H. Albert, Adrian J. Thrasher, Alessandro Aiuti
Journal: Blood
Blood (2024) 144 (16): 1699–1704.
https://doi.org/10.1182/blood.2024024524
Published: 2024
Includes: Supplemental data
Journal Articles

Circulating hematopoietic stem/progenitor cell subsets contribute to human hematopoietic homeostasis

Pamela Quaranta, Luca Basso-Ricci, Raisa Jofra Hernandez, Guido Pacini, Matteo Maria Naldini, Matteo Barcella, Luca Seffin, Giulia Pais, Giulio Spinozzi, Fabrizio Benedicenti, Carlo Pietrasanta, Jin Gyu Cheong, Andrea Ronchi, Lorenza Pugni, Francesca Dionisio, Ilaria Monti, Stefania Giannelli, Silvia Darin, Federico Fraschetta, Graziano Barera, Francesca Ferrua, Valeria Calbi, Marco Ometti, Raffaella Di Micco, Fabio Mosca, Steven Zvi Josefowicz, Eugenio Montini, Andrea Calabria, Maria Ester Bernardo, Maria Pia Cicalese, Bernhard Gentner, Ivan Merelli, Alessandro Aiuti, Serena Scala
Journal: Blood
Blood (2024) 143 (19): 1937–1952.
https://doi.org/10.1182/blood.2023022666
Published: 2024
Includes: Supplemental data
Journal Articles

Unveiling the Biological Role of Peripheral Blood Human Circulating Hematopoietic Stem and Progenitor Cells

Pamela Quaranta, Luca Basso-Ricci, Raisa Jofra Hernández, Matteo Maria Naldini, Matteo Barcella, Guido Pacini, Carlo Pietrasanta, Lorenza Pugni, Giulia Pais, Fabrizio Benedicenti, Francesca Dionisio, Stefania Giannelli, Ilaria Monti, Silvia Darin, Graziano Barera, Francesca Tucci, Francesca Ferrua, Valeria Calbi, Marco Ometti, Bernhard Gentner, Raffaella Di Micco, Eugenio Montini, Andrea Calabria, Ivan Merelli, Fabio Mosca, Maria Ester Bernardo, Maria Pia Cicalese, Alessandro Aiuti, Serena Scala
Journal: Blood
Blood (2022) 140 (Supplement 1): 1977–1978.
https://doi.org/10.1182/blood-2022-163251
Published: 2022
Journal Articles

Lentiviral-Mediated Gene Therapy for the Treatment of Adenosine Deaminase 2 Deficiency

Alessandra Mortellaro, Matteo Zoccolillo, Cristina Mesa Nuñez, Alessia Brix, Immacolata Brigida, Federica Barzaghi, Serena Scala, Raisa Jofra Hernández, Luca Basso-Ricci, Mariasilvia Colantuoni, Simone Cesaro, Francesca Conti, Andrea Pession, Fabio Benedetti, Marco Gattorno, Luigi Naldini, Maria Pia Cicalese, Anna Pistocchi, Alessandro Aiuti
Journal: Blood
Blood (2021) 138 (Supplement 1): 2937.
https://doi.org/10.1182/blood-2021-152127
Published: 2021
Journal Articles

Lentiviral Hematopoietic Stem and Progenitor Cell Gene Therapy for Wiskott-Aldrich Syndrome (WAS): Up to 8 Years of Follow up in 17 Subjects Treated Since 2010

Francesca Ferrua, MD PhD, Maria Pia Cicalese, MD PhD, Stefania Galimberti, PhD, Stefania Giannelli, PhD, Francesca Dionisio, MSc, Federica Barzaghi, MD PhD, Maddalena Migliavacca, MD PhD, Maria Ester Bernardo, MD PhD, Valeria Calbi, MD, Francesca Tucci, MD, Andrea A. Assanelli, MD, Jacopo Peccatori, MD, Elena Albertazzi, PhD, Alessandra G. Clerici, Federica A. Salerio, MSc, Serena Scala, PhD, Luca Basso-Ricci, MSc, Sabina Cenciarelli, MD, Daniele Canarutto, MD, Federico Fraschetta, RN, Antonella Bartoli, MScPharm, Hermann M. Wolf, MD, Paolo Silvani, MD, Salvatore Gattillo, MD, Milena Coppola, MD, Luca Santoleri, MD, Anna Villa, MD, Russell Jones, Chris Dott, PhD, Maria Grazia Valsecchi, PhD, Fabio Ciceri, MD, Luigi Naldini, MD PhD, Alessandro Aiuti, MD PhD
Journal: Blood
Blood (2019) 134 (Supplement_1): 3346.
https://doi.org/10.1182/blood-2019-124665
Published: 2019
Journal Articles

T-cell defects in patients with ARPC1B germline mutations account for combined immunodeficiency

Immacolata Brigida, Matteo Zoccolillo, Maria Pia Cicalese, Laurène Pfajfer, Federica Barzaghi, Serena Scala, Carmen Oleaga-Quintas, Jesus A. Álvarez-Álvarez, Lucia Sereni, Stefania Giannelli, Claudia Sartirana, Francesca Dionisio, Luca Pavesi, Marta Benavides-Nieto, Luca Basso-Ricci, Paola Capasso, Benedetta Mazzi, Jeremie Rosain, Nufar Marcus, Yu Nee Lee, Raz Somech, Massimo Degano, Giuseppe Raiola, Roberta Caorsi, Paolo Picco, Marcela Moncada Velez, Joelle Khourieh, Andrés Augusto Arias, Aziz Bousfiha, Thomas Issekutz, Andrew Issekutz, Bertrand Boisson, Kerry Dobbs, Anna Villa, Angelo Lombardo, Benedicte Neven, Despina Moshous, Jean-Laurent Casanova, José Luis Franco, Luigi D. Notarangelo, Cristina Scielzo, Stefano Volpi, Loïc Dupré, Jacinta Bustamante, Marco Gattorno, Alessandro Aiuti
Journal: Blood
Blood (2018) 132 (22): 2362–2374.
https://doi.org/10.1182/blood-2018-07-863431
Published: 2018
Includes: Supplemental data
Journal Articles

Gene Therapy for Beta Thalassemia: Preliminary Results from the PHASE I/II Tiget-Bthal Trial of Autologous Hematopoietic Stem Cells Genetically Modified with GLOBE Lentiviral Vector

Sarah Marktel, MD, Maria Pia Cicalese, Fabio Giglio, MD, Samantha Scaramuzza, Valeria Calbi, Miriam Casiraghi, Francesca Ciotti, Maria Rosa Lidonnici, Claudia Rossi, Nicoletta Masera, Emanuela D'Angelo, Nadia Mirra, Raffaella Origa, MD, Immacolata Tartaglione, Giacomo Mandelli, Raffaella Milani, Salvatore Gattillo, Milena Coppola, Gianluca Viarengo, Luca Santoleri, Andrea Calabria, Silverio Perrotta, Eugenio Montini, Giovanna Graziadei, MD, Luigi Naldini, MD PhD, Maria Domenica Cappellini, MD, Fabio Ciceri, MD, Alessandro Aiuti, Giuliana Ferrari
Journal: Blood
Blood (2017) 130 (Supplement 1): 355.
https://doi.org/10.1182/blood.V130.Suppl_1.355.355
Published: 2017
Journal Articles

Update on the safety and efficacy of retroviral gene therapy for immunodeficiency due to adenosine deaminase deficiency

Maria Pia Cicalese, Francesca Ferrua, Laura Castagnaro, Roberta Pajno, Federica Barzaghi, Stefania Giannelli, Francesca Dionisio, Immacolata Brigida, Marco Bonopane, Miriam Casiraghi, Antonella Tabucchi, Filippo Carlucci, Eyal Grunebaum, Mehdi Adeli, Robbert G. Bredius, Jennifer M. Puck, Polina Stepensky, Ilhan Tezcan, Katie Rolfe, Erika De Boever, Rickey R. Reinhardt, Jonathan Appleby, Fabio Ciceri, Maria Grazia Roncarolo, Alessandro Aiuti
Journal: Blood
Blood (2016) 128 (1): 45–54.
https://doi.org/10.1182/blood-2016-01-688226
Published: 2016
Includes: Supplemental data
Journal Articles

Safety and Clinical Benefit of Lentiviral Hematopoietic Stem Cell Gene Therapy for Wiskott-Aldrich Syndrome

Francesca Ferrua, MD, Maria Pia Cicalese, MD PhD, Stefania Galimberti, PhD, Samantha Scaramuzza, PhD, Stefania Giannelli, PhD, Roberta Pajno, MD, Francesca Dionisio, PhD, Luca Biasco, PhD, Maria Carmina Castiello, PhD, Miriam Casiraghi, RN, Marcella Facchini, PhD, Andrea Finocchi, MD, Ayse Metin, MD PhD, Jordan S. Orange, MD PhD, Michael H. Albert, MD, Carmen Petrescu, MD, Marita Bosticardo, PhD, Anna Villa, MD, Chris Dott, PhD, Koen van Rossem, MD MSc, PhD, Maria Grazia Valsecchi, PhD, Fabio Ciceri, MD, Maria Grazia Roncarolo, MD, Luigi Naldini, MD PhD, Alessandro Aiuti, MD PhD
Journal: Blood
Blood (2015) 126 (23): 259.
https://doi.org/10.1182/blood.V126.23.259.259
Published: 2015