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Journal Articles

Use of HSC-targeted LNP to generate a mouse model of lethal α-thalassemia and treatment via lentiviral gene therapy

Blood (2024) 144 (15): 1633–1645.

https://doi.org/10.1182/blood.2023023349

Published: 2024

Includes: Supplemental data

Journal Articles

Differential Effect of Transferrin Lobe Iron Occupancy on a Murine Model of Inflammation

Nermi L. Parrow, Nisha Ajit George, Faris Ali, Nadia Wattad, Amaliris Guerra, Yelena Ginzburg, Stefano Rivella, Robert E. Fleming

Blood (2023) 142 (Supplement 1): 1095.

https://doi.org/10.1182/blood-2023-190984

Published: 2023

Journal Articles

Phenotypic HSPC Rescue By RNA Lipid Nanoparticles in a Murine Model of Fanconi Anemia

Linah Omer, Omar Banda, Sarah Adams, Seul K Jung, Stefano Rivella, Mohamad-Gabriel Alameh, Drew Weissman, Peter Kurre

Blood (2023) 142 (Supplement 1): 3625.

https://doi.org/10.1182/blood-2023-188193

Published: 2023

Journal Articles

Differential Effects of Monoferric Transferrin Forms on Erythropoiesis Are Mediated By TFR2

Amaliris Guerra, Ariel Rivera, Nolan Hamilton, Xiuli An, Nermi L. Parrow, Yelena Ginzburg, Robert E. Fleming, Stefano Rivella

Blood (2023) 142 (Supplement 1): 3846.

https://doi.org/10.1182/blood-2023-189107

Published: 2023

Journal Articles

Establishment of High Titer Baboon Endogenous Retrovirus Envelope Pseudotyped Lentiviral Vector Production Protocol Focusing on Syncytium Formation and Exfoliation

Kazuhiro Noguchi, Yasuhiro Ikawa, Mika Takenaka, Yuta Sakai, Toshihiro Fujiki, Rie Kuroda, Maxwell Chappell, Valentina Ghiaccio, Stefano Rivella, Taizo Wada

Blood (2022) 140 (Supplement 1): 12987–12989.

https://doi.org/10.1182/blood-2022-163144

Published: 2022

Journal Articles

Combination of a TGF-β Ligand Trap (RAP-GRL) and TMPRSS6 -ASO Is Superior for Correcting β-Thalassemia

Amaliris Guerra, Perry Demsko, Ariel Rivera, Carlo Castruccio Castracani, Laura Breda, Naoto Tanaka, Shuling Guo, Stefano Rivella

Blood (2022) 140 (Supplement 1): 1944–1945.

https://doi.org/10.1182/blood-2022-166801

Published: 2022

Journal Articles

In Vivo Modification of Hematopoietic Stem Cells By Targeted Lipid Nanoparticles Encapsulating mRNA

Laura Breda, Tyler E Papp, Michael Triebwasser, Amir Yadegari, Megan T Fedorky, Naoto Tanaka, Houping Ni, Drew Weissman, Stefano Rivella, Hamideh Parhiz

Blood (2022) 140 (Supplement 1): 305–306.

https://doi.org/10.1182/blood-2022-165089

Published: 2022

Journal Articles

Direct Delivery of mRNA-Loaded Lipid Nanoparticles to the Hematopoietic Stem Cell Niche

Omar Banda, Mohamad-Gabriel Alameh, Seul Jung, Drew Weissman, Stefano Rivella, Peter Kurre

Blood (2022) 140 (Supplement 1): 4923–4924.

https://doi.org/10.1182/blood-2022-159085

Published: 2022

Journal Articles

The Effect of Monoferric Transferrins on Hypoferremia in a Murine Model of Inflammation

Nermi Parrow, Nisha George, Faris Ali, Nadia Wattad, Amaliris Guerra, Yelena Ginzburg, Stefano Rivella, Robert E Fleming

Blood (2022) 140 (Supplement 1): 2463–2464.

https://doi.org/10.1182/blood-2022-171130

Published: 2022

Journal Articles

Lnp-Targeting Hematopoietic Stem Cells and Lentiviral Gene Transfer to Generate and Rescue a Novel Mouse Model of Lethal Alpha-Thalassemia

Maxwell Chappell, Laura Breda, Danuta Jadwiga Jarocha, Michael Triebwasser, Tyler E Papp, Valentina Ghiaccio, Megan T Fedorky, Amaliris Guerra, Kandace Gollomp, Osheiza Y. Abdulmalik, Nattiya Teawtrakul, Stavros Glentis, Antonis Kattamis, Hamideh Parhiz, Stefano Rivella

Blood (2022) 140 (Supplement 1): 300–302.

https://doi.org/10.1182/blood-2022-166621

Published: 2022

Journal Articles

TNFα and Anti-IFNγ Rescues Chronic Anemia of Inflammation Phenotype in Tnfαko Mice Treated with Heat-Killed Brucella Abortus

Amaliris Guerra, Vania Lo Presti, Ding-Wen Chen, Ana Catarina Martins, Carlo Castruccio Castracani, Ritama Gupta, Laura Bennett, Raffaella Gozzelino, Robert Paulson, Peter Kurre, Stefano Rivella, Carla Casu

Blood (2022) 140 (Supplement 1): 5302–5303.

https://doi.org/10.1182/blood-2022-166643

Published: 2022

Journal Articles

Differential Effects of Monoferric Forms of Transferrin on Mouse Models of Anemia of Inflammation and Congenital Anemia

Amaliris Guerra, Ana Catarina Martins, Ariel Rivera, Nermi Parrow, Raffaella Gozzelino, Yelena Ginzburg, Robert E Fleming, Stefano Rivella

Blood (2022) 140 (Supplement 1): 8179–8180.

https://doi.org/10.1182/blood-2022-166391

Published: 2022

Journal Articles

Lack of IL6 Improves Recovery from Anemia of Inflammation Which Gets Hampered in Presence of Excess Iron

Sayantani Sinha, Ritama Gupta, Amaliris Guerra, Paige Mc Veigh, Sara Gardenghi, Carla Casu, Francesca Vinchi, Stefano Rivella

Blood (2021) 138 (Supplement 1): 3072.

https://doi.org/10.1182/blood-2021-153126

Published: 2021

Journal Articles

Improved Gene Therapy for Metachromatic Leukodystrophy

Lucas Tricoli, Adeline Vanderver, Laura Adang, Maxwell Chappell, Laura Breda, Naoto Tanaka, Michael Triebwasser, David Wenger, Danuta Jadwiga Jarocha, Amaliris Guerra, Lars Schlotawa, Karthikeyan Radhakrishnan, Rebecca Ahrens-Nicklas, Peter Kurre, Stephanie Hurwitz, Stefano Rivella

Blood (2021) 138 (Supplement 1): 3979.

https://doi.org/10.1182/blood-2021-150986

Published: 2021

Journal Articles

A Severe Mouse Model of Alpha-Thalassemia to Study Abnormal Iron Metabolism and Erythropoiesis, Hematopoietic Stem Cell Behavior and Development of a Gene Therapy Approach for Its Treatment

Maxwell Chappell, Danuta Jadwiga Jarocha, Laura Breda, Valentina Ghiaccio, Michael Triebwasser, Megan Fedorky, Amaliris Guerra, Kandace Gollomp, Nattiya Teawtrakul, Stavros Glentis, Antonis Kattamis, Osheiza Abdulmalik, Stefano Rivella

Blood (2021) 138 (Supplement 1): 2012.

https://doi.org/10.1182/blood-2021-151217

Published: 2021

Journal Articles

Combination of a Luspatercept-like Drug (RAP-GRL) and Tmprss6 -ASO Is Superior to Either Drug Alone for Correcting β-Thalassemia

Amaliris Guerra, Perry Demsko, Paige McVeigh, Sayantani Sinha, Carlo Castruccio Castracani, Laura Breda, Carla Casu, Shuling Guo, Stefano Rivella

Blood (2021) 138 (Supplement 1): 2013.

https://doi.org/10.1182/blood-2021-151181

Published: 2021

Journal Articles

Obligate N-Terminal but Not C-Terminal Monoferric Transferrin Ameliorates Anemia in β-Thalassemic Mice

Amaliris Guerra, Nermi Parrow, Paige McVeigh, Robert E Fleming, Yelena Ginzburg, Stefano Rivella

Blood (2021) 138 (Supplement 1): 937.

https://doi.org/10.1182/blood-2021-152709

Published: 2021

Journal Articles

Rescue of Murine IL-7 Receptor Deficiency with Human IL-7 Receptor Gene Therapy

Michael Triebwasser, Danuta Jadwiga Jarocha, Laura Breda, Megan Fedorky, Stefano Rivella

Blood (2021) 138 (Supplement 1): 3131.

https://doi.org/10.1182/blood-2021-151040

Published: 2021

Journal Articles

Dietary Iron Increases Expression of Liver Hepcidin Relative to BMP6 By a Mechanism Involving Transferrin Receptor 2 and Specificity of Transferrin Lobe Iron Occupancy

Nermi Parrow, Faris Ali, Nisha George, Yelena Ginzburg, Stefano Rivella, Robert E Fleming

Blood (2021) 138 (Supplement 1): 3067.

https://doi.org/10.1182/blood-2021-153973

Published: 2021

Journal Articles

Tfr2 Genetic Deletion Makes Transfusion-Independent a Murine Model of Transfusion-Dependent β-Thalassemia

Simona Maria Di Modica, Violante Olivari, Emanuele Tanzi, Mariateresa Pettinato, Maria Rosa Lidonnici, Alessia Pagani, Francesca Tiboni, Giuliana Ferrari, Laura Silvestri, Stefano Rivella, Antonella Nai

Blood (2021) 138 (Supplement 1): 575.

https://doi.org/10.1182/blood-2021-148419

Published: 2021

NARROW

Use of HSC-targeted LNP to generate a mouse model of lethal α-thalassemia and treatment via lentiviral gene therapy

Differential Effect of Transferrin Lobe Iron Occupancy on a Murine Model of Inflammation

Phenotypic HSPC Rescue By RNA Lipid Nanoparticles in a Murine Model of Fanconi Anemia

Differential Effects of Monoferric Transferrin Forms on Erythropoiesis Are Mediated By TFR2

Establishment of High Titer Baboon Endogenous Retrovirus Envelope Pseudotyped Lentiviral Vector Production Protocol Focusing on Syncytium Formation and Exfoliation

Combination of a TGF-β Ligand Trap (RAP-GRL) and TMPRSS6 -ASO Is Superior for Correcting β-Thalassemia

In Vivo Modification of Hematopoietic Stem Cells By Targeted Lipid Nanoparticles Encapsulating mRNA

Direct Delivery of mRNA-Loaded Lipid Nanoparticles to the Hematopoietic Stem Cell Niche

The Effect of Monoferric Transferrins on Hypoferremia in a Murine Model of Inflammation

Lnp-Targeting Hematopoietic Stem Cells and Lentiviral Gene Transfer to Generate and Rescue a Novel Mouse Model of Lethal Alpha-Thalassemia

TNFα and Anti-IFNγ Rescues Chronic Anemia of Inflammation Phenotype in Tnfαko Mice Treated with Heat-Killed Brucella Abortus

Differential Effects of Monoferric Forms of Transferrin on Mouse Models of Anemia of Inflammation and Congenital Anemia

Lack of IL6 Improves Recovery from Anemia of Inflammation Which Gets Hampered in Presence of Excess Iron

Improved Gene Therapy for Metachromatic Leukodystrophy

A Severe Mouse Model of Alpha-Thalassemia to Study Abnormal Iron Metabolism and Erythropoiesis, Hematopoietic Stem Cell Behavior and Development of a Gene Therapy Approach for Its Treatment

Combination of a Luspatercept-like Drug (RAP-GRL) and Tmprss6 -ASO Is Superior to Either Drug Alone for Correcting β-Thalassemia

Obligate N-Terminal but Not C-Terminal Monoferric Transferrin Ameliorates Anemia in β-Thalassemic Mice

Rescue of Murine IL-7 Receptor Deficiency with Human IL-7 Receptor Gene Therapy

Dietary Iron Increases Expression of Liver Hepcidin Relative to BMP6 By a Mechanism Involving Transferrin Receptor 2 and Specificity of Transferrin Lobe Iron Occupancy

Tfr2 Genetic Deletion Makes Transfusion-Independent a Murine Model of Transfusion-Dependent β-Thalassemia

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American Society of Hematology

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ASH Publications

American Society of Hematology

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