Page 1 | Search Results | Blood | American Society of Hematology

1-20 of 26

Sort by

Sort Order Select

Journal Articles

Iron Unloading By Therapeutic Phlebotomy in Previously Transfused Children with Sickle Cell Anemia: The Twitch Experience

Banu Aygun, MD, Nicole Mortier, PA-C, Zora R. Rogers, MD, William Owen, MD, Beng Fuh, MD, Alex George, MD, PhD, Theodosia A. Kalfa, MD PhD, Janet Kwiatkowski, MD, Margaret Lee, MD, Hamayun Imran, MD, Scott T. Miller, MD, John C Wood, MD PhD, Alan R. Cohen, MD, Sara L Pressel, MS, Russell E. Ware, MD PhD

Blood (2016) 128 (22): 1018.

https://doi.org/10.1182/blood.V128.22.1018.1018

Published: 2016

Journal Articles

Lentiglobin Gene Therapy for Transfusion-Dependent β-Thalassemia: Update from the Northstar Hgb-204 Phase 1/2 Clinical Study

Alexis A. Thompson, MD MPH, Janet Kwiatkowski, MD, John Rasko, MBBS, PhD, Suradej Hongeng, MD, Gary J. Schiller, MD, Usanarat Anurathapan, MD, Marina Cavazzana, MD PhD, P. Joy Ho, Christof von Kalle, MD, Morris Kletzel, MD FAAP, MBA, Philippe Leboulch, MD, Elliott Vichinsky, MD, Alexandria Petrusich, Mohammed Asmal, MD PhD, Mark C. Walters, MD

Blood (2016) 128 (22): 1175.

https://doi.org/10.1182/blood.V128.22.1175.1175

Published: 2016

Journal Articles

Interim Results from a Phase 1/2 Clinical Study of Lentiglobin Gene Therapy for Severe Sickle Cell Disease

Julie Kanter, MD, Mark C. Walters, MD, Matthew M. Hsieh, MD, Lakshmanan Krishnamurti, MD, Janet Kwiatkowski, MD, Rammurti T Kamble, MD, Christof von Kalle, MD, Frans A. Kuypers, PhD, Marina Cavazzana, MD PhD, Philippe Leboulch, MD, Marcelyne Joseney-Antoine, Mohammed Asmal, MD PhD, Alexis A. Thompson, MD MPH, John F. Tisdale, MD

Blood (2016) 128 (22): 1176.

https://doi.org/10.1182/blood.V128.22.1176.1176

Published: 2016

Journal Articles

Impact of TCD Screening Protocol on the Incidence of Hemorrhagic Stroke in Children and Young Adults with Sickle Cell Disease

Julie Kanter, MD, Janet Kwiatkowski, MD, Heather J. Fullerton, MD, Jenifer Voeks, Ellen Debenham, RN, Lynette J Brown, Robert J. Adams, MD MS

Blood (2015) 126 (23): 3402.

https://doi.org/10.1182/blood.V126.23.3402.3402

Published: 2015

Journal Articles

Initial Results from Study Hgb-206: A Phase 1 Study Evaluating Gene Therapy By Transplantation of Autologous CD34+ Stem Cells Transduced Ex Vivo with the Lentiglobin BB305 Lentiviral Vector in Subjects with Severe Sickle Cell Disease

Julie Kanter, MD, Mark C. Walters, MD, Matthew Hsieh, MD, Alexis A. Thompson, MD, Lakshmanan Krishnamurti, MD, Janet Kwiatkowski, MD, Rammurti T Kamble, MD, Christof von Kalle, MD, Frans A. Kuypers, PhD, Marina Cavazzana, MD PhD, Philippe Leboulch, MD, Laura Sandler, MPH, Sandeep Soni, MD, John F. Tisdale, MD

Blood (2015) 126 (23): 3233.

https://doi.org/10.1182/blood.V126.23.3233.3233

Published: 2015

Journal Articles

Epidemiologic and Clinical Characteristics of Thalassemia (Thal) Intermedia (TI) in the United States

Elliott P. Vichinsky, MD, Janet Kwiatkowski, MD, Patricia J. Giardina, MD, Carole Paley, MD, Francis Vekeman, MA, Wendy Y. Cheng, MPH, MPhil, Joseph Damron, BA, Nora McCormick, MSc, Medha Sasane, PhDBPharm,MS, Ying Qiu, PhD, Mei Sheng Duh, MPH, ScD, Alexis A. Thompson, MD

Blood (2015) 126 (23): 3279.

https://doi.org/10.1182/blood.V126.23.3279.3279

Published: 2015

Journal Articles

TCD with Transfusions Changing to Hydroxyurea (TWiTCH): Hydroxyurea Therapy As an Alternative to Transfusions for Primary Stroke Prevention in Children with Sickle Cell Anemia

Russell E. Ware, MD PhD, Barry R Davis, MD PhD, William H Schultz, MHS PA, Clark Brown, MD PhD, Banu Aygun, MD, Sharada A. Sarnaik, MD, Isaac Odame, MD, Beng Fuh, MD, Alex George, MD, PhD, William Owen, MD, Lori Luchtman-Jones, MD, Zora R. Rogers, MD, Lee Hilliard, MD, Cynthia Gauger, MD, Connie M. Piccone, MD, Margaret T. Lee, MD, Janet Kwiatkowski, MD, Sherron Jackson, MD, Scott T. Miller, MD, Carla W Roberts, MD, Matthew M. Heeney, MD FRCP(C), Theodosia A. Kalfa, MD PhD, Stephen C Nelson, MD, Hamayun Imran, MD, Kerri A Nottage, MD MPH, Ofelia A. Alvarez, MD, Melissa Rhodes, MD, Alexis A. Thompson, MD, Jennifer Rothman, MD, Kathleen J. Helton, MD, Donna Roberts, MD, Jamie Coleman, MD, Melanie J Bonner, PhD, Abdullah Kutlar, MD, Niren Patel, MD, John C Wood, MD PhD, Linda Piller, MD, Peng Wei, PhD, Judy Luden, CCRP, Nicole A. Mortier, MHS, PA-C, Susan Stuber, MA, Naomi L.C. Luban, MD, Alan R. Cohen, MD, Sara L Pressel, MS, Robert J. Adams, MD MS

Blood (2015) 126 (23): 3.

https://doi.org/10.1182/blood.V126.23.3.3

Published: 2015

Journal Articles

Update of Results from the Northstar Study (HGB-204): A Phase 1/2 Study of Gene Therapy for Beta-Thalassemia Major Via Transplantation of Autologous Hematopoietic Stem Cells Transduced Ex-Vivo with a Lentiviral Beta AT87Q-Globin Vector (LentiGlobin BB305 Drug Product)

Mark C. Walters, MD, John Rasko, MBBS, PhD, Suradej Hongeng, MD, Janet Kwiatkowski, MD, Gary J Schiller, MD, Morris Kletzel, MD, P. Joy Ho, MBBS, DPhil, Elliott Vichinsky, MD, Christof von Kalle, MD, Marina Cavazzana, MD PhD, Philippe Leboulch, MD, Alexandria Petrusich, Sandeep Soni, MD, Alexis A. Thompson, MD

Blood (2015) 126 (23): 201.

https://doi.org/10.1182/blood.V126.23.201.201

Published: 2015

Journal Articles

Multicenter Investigation Of Unrelated Donor Hematopoietic Cell Transplantation (HCT) For Thalassemia Major After a Reduced Intensity Conditioning Regimen (URTH Trial)

Blood (2013) 122 (21): 543.

https://doi.org/10.1182/blood.V122.21.543.543

Published: 2013

Journal Articles

Liver Iron Concentration By MRI In Chronically Transfused Children With Sickle Cell Anemia In The Twitch Trial

John C. Wood, MD, PhD, Zora R. Rogers, MD, Isaac Odame, MD, Janet Kwiatkowski, MD, Margaret Lee, MD, William C. Owen, MD, Alan Cohen, MD, Timothy St. Pierre, PhD, Barry R Davis, MD, PhD, Crystal Parker, MS, William Herbert Schultz, PA-C, Russell E. Ware, MD, PhD

Blood (2013) 122 (21): 780.

https://doi.org/10.1182/blood.V122.21.780.780

Published: 2013

Journal Articles

A pilot study of subcutaneous decitabine in β-thalassemia intermedia

Nancy F. Olivieri, Yogen Saunthararajah, Vivek Thayalasuthan, Janet Kwiatkowski, Russell E. Ware, Frans A. Kuypers, Hae-Young Kim, Felicia L. Trachtenberg, Elliott P. Vichinsky, for the Thalassemia Clinical Research Network

Blood (2011) 118 (10): 2708–2711.

https://doi.org/10.1182/blood-2011-03-341909

Published: 2011

Includes: Supplemental data

Journal Articles

A Pilot Study of Epigenetic-Differentiation Therapy with Decitabine to Treat β-Thalassemia Intermedia

Nancy F Olivieri, MD, Yogenthiran Saunthararajah, MD, Vivekanandan Thayalasuthan, MD, Janet Kwiatkowski, MD, Russell E. Ware, MD, PhD, Franz Kuypers, PhD, Hae-Young Kim, DrPH, Elliott P Vichinsky, MD

Blood (2010) 116 (21): 2078.

https://doi.org/10.1182/blood.V116.21.2078.2078

Published: 2010

Journal Articles

A Phase 1B Dose-Escalation Study to Assess the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of FBS0701, a Novel Oral Iron Chelator for the Treatment of Chronic Iron Overload

Hugh Y. Rienhoff, Jr, MD, ip Viprakasit, MD, D, Phil, Lay H. Tay, MBBS, FRCPA, Paul Harmatz, MD, Elliott Vichinsky, MD, Deborah Chirnomas, MD, MPH, Janet Kwiatkowski, MD, Amy E Tapper, PhD, John B Porter, MD, Ellis J. Neufeld, MD, PhD

Blood (2010) 116 (21): 2057.

https://doi.org/10.1182/blood.V116.21.2057.2057

Published: 2010

Journal Articles

Phenomenon of Pain In Thalassemia: A Prospective Analysis by the Thalassemia Clinical Research Network (TCRN)

Blood (2010) 116 (21): 256.

https://doi.org/10.1182/blood.V116.21.256.256

Published: 2010

Journal Articles

Increased Nucleosomal DNA Fragmentation in Leukocytes of Thalassemia Patients.

Patrick B Walter, PhD, John B Porter, MD, Patricia Evans, PhD, Janet Kwiatkowski, MD, Ellis J. Neufeld, MD, PhD, Thomas D. Coates, MD, Patricia Giardina, MD, Robert jW Grady, PhD, Elliott Vichinsky, MD, Nancy F. Olivieri, MD, Felicia Trachtenberg, PhD, Daniele Alberti, MD, Ellen Fung, PhD, Bruce Ames, PhD, Annie Lui, BS, Paul Harmatz, MD

Blood (2008) 112 (11): 1868.

https://doi.org/10.1182/blood.V112.11.1868.1868

Published: 2008

Journal Articles

Hemoglobin H-Constant Spring in North America: A Common Alpha Thalassemia with Frequent Complications.

Titi Singer, Hae-Young Kim, Nancy F Olivieri, Janet Kwiatkowski, Ashutosh Lal, Thomas D. Coates, Susan Carson, Melody J. Cunningham, Patricia J Giardina, Brigitta U Mueller, Charles Quinn, Elliott Vichinsky, Thalassemia Clinical Research Network

Blood (2008) 112 (11): 1880.

https://doi.org/10.1182/blood.V112.11.1880.1880

Published: 2008

Journal Articles

Body Composition and Its Relationship to Growth and Bone Mass in Patients with Thalassemia

Ellen Fung, PhD, Yan Xu, PhD, Janet Kwiatkowski, MD, Sylvia Titi Singer, MD, Ashutosh Lal, Maria G Vogiatzi, Nancy F. Olivieri, MD, Ellis J. Neufeld, Elliott Vichinsky, MD, Patricia Giardina, MD

Blood (2008) 112 (11): 3890.

https://doi.org/10.1182/blood.V112.11.3890.3890

Published: 2008

Journal Articles

Safety and Efficacy of Peginterferon Alfa-2a and Ribavirin for Hepatitis C in Thalassemia.

Paul Harmatz, MD, Nancy F. Olivieri, MD, Janet Kwiatkowski, MD, Elliott Vichinsky, MD, Patricia Giardina, MD, Farrukh Shah, MD, Elizabeth C. Wright, PhD, Roland Fischer, PhD, Maureen M. Jonas, MD

Blood (2006) 108 (11): 558.

https://doi.org/10.1182/blood.V108.11.558.558

Published: 2006

Journal Articles

Vertebral Abnormalities by Spine Morphometry in Thalassemia.

Maria Vogiatzi, Eric Macklin, Robert Schneider, Joseph Lane, Irina Chaikodinov, Nancy Olivieri, Melanie Kirby, Elliott Vichinky, Ellen Fung, Janet Kwiatkowski, Melody Cunningham, Patricia Giardina

Blood (2006) 108 (11): 3829.

https://doi.org/10.1182/blood.V108.11.3829.3829

Published: 2006

Journal Articles

Academic Community Standards for Chronic Transfusion Therapy in Children with Sickle Cell Anemia and Stroke.

Blood (2006) 108 (11): 1213.

https://doi.org/10.1182/blood.V108.11.1213.1213

Published: 2006

NARROW

Iron Unloading By Therapeutic Phlebotomy in Previously Transfused Children with Sickle Cell Anemia: The Twitch Experience

Lentiglobin Gene Therapy for Transfusion-Dependent β-Thalassemia: Update from the Northstar Hgb-204 Phase 1/2 Clinical Study

Interim Results from a Phase 1/2 Clinical Study of Lentiglobin Gene Therapy for Severe Sickle Cell Disease

Impact of TCD Screening Protocol on the Incidence of Hemorrhagic Stroke in Children and Young Adults with Sickle Cell Disease

Initial Results from Study Hgb-206: A Phase 1 Study Evaluating Gene Therapy By Transplantation of Autologous CD34+ Stem Cells Transduced Ex Vivo with the Lentiglobin BB305 Lentiviral Vector in Subjects with Severe Sickle Cell Disease

Epidemiologic and Clinical Characteristics of Thalassemia (Thal) Intermedia (TI) in the United States

TCD with Transfusions Changing to Hydroxyurea (TWiTCH): Hydroxyurea Therapy As an Alternative to Transfusions for Primary Stroke Prevention in Children with Sickle Cell Anemia

Update of Results from the Northstar Study (HGB-204): A Phase 1/2 Study of Gene Therapy for Beta-Thalassemia Major Via Transplantation of Autologous Hematopoietic Stem Cells Transduced Ex-Vivo with a Lentiviral Beta AT87Q-Globin Vector (LentiGlobin BB305 Drug Product)

Multicenter Investigation Of Unrelated Donor Hematopoietic Cell Transplantation (HCT) For Thalassemia Major After a Reduced Intensity Conditioning Regimen (URTH Trial)

Liver Iron Concentration By MRI In Chronically Transfused Children With Sickle Cell Anemia In The Twitch Trial

A pilot study of subcutaneous decitabine in β-thalassemia intermedia

A Pilot Study of Epigenetic-Differentiation Therapy with Decitabine to Treat β-Thalassemia Intermedia

A Phase 1B Dose-Escalation Study to Assess the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of FBS0701, a Novel Oral Iron Chelator for the Treatment of Chronic Iron Overload

Phenomenon of Pain In Thalassemia: A Prospective Analysis by the Thalassemia Clinical Research Network (TCRN)

Increased Nucleosomal DNA Fragmentation in Leukocytes of Thalassemia Patients.

Hemoglobin H-Constant Spring in North America: A Common Alpha Thalassemia with Frequent Complications.

Body Composition and Its Relationship to Growth and Bone Mass in Patients with Thalassemia

Safety and Efficacy of Peginterferon Alfa-2a and Ribavirin for Hepatitis C in Thalassemia.

Vertebral Abnormalities by Spine Morphometry in Thalassemia.

Academic Community Standards for Chronic Transfusion Therapy in Children with Sickle Cell Anemia and Stroke.

Email alerts

ASH Publications

American Society of Hematology

Email alerts

ASH Publications

American Society of Hematology

This Feature Is Available To Subscribers Only