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Susan C Stevenson
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Journal Articles

Targeted Degradation of the Wiz Transcription Factor for Gamma Globin De-Repression

Free
Pamela Y Ting, Sneha Borikar, John Ryan Kerrigan, Noel M Thomsen, Eamon Aghania, Amelia E Hinman, Nicolas Pizzato, Alejandro Reyes, Barna D Fodor, Fabian Wu, Muluken S Belew, Xiaohong Mao, Jian Wang, Shripad Chitnis, Peter Ashcroft, Wei Niu, Amanda Hachey, Jennifer S Cobb, Nikolas A Savage, Ashley Burke, Joshiawa Paulk, Dustin Dovala, James Lin, Matthew C Clifton, Elizabeth Ornelas, Xiaolei Ma, Nathaniel F Ware, Carina C Sanchez, Remi Terranova, Judith Knehr, Marc Altorfer, S. Whitney Barnes, John Taraszka, Danuta Lubicka, James R Manning, Sonia R Miranda, Rohan EJ Beckwith, Jonathan M Solomon, William Forrester, Gregory Hollingworth, Natalie A Dales, Andrew W Patterson, Tewis Bouwmeester, Juergen Wagner, Glenn Dranoff, Susan C Stevenson, James E Bradner
Journal: Blood
Blood (2023) 142 (Supplement 1): 2.
https://doi.org/10.1182/blood-2023-179331
Published: 2023
Journal Articles

Treatment of Individuals with Severe Sickle Cell Disease with OTQ923, an Autologous, Ex Vivo , CRISPR/Cas9-Edited, CD34+ Hematopoietic Stem and Progenitor Cell Product, Leads to Durable Engraftment and Fetal Hemoglobin Induction

Free
Akshay Sharma, Jaap Jan Boelens, Maria I. Cancio, Jane Hankins, Prafulla A Bhad, Andrew Lewandowski, Xiaojun Zhao, Shripad Chitnis, Radhika Peddinti, Yan Zheng, Neena Kapoor, Fabio Ciceri, Jianping Yuan, Vionnie W. Yu, Susan C. Stevenson, Serena De Vita, James LaBelle
Journal: Blood
Blood (2022) 140 (Supplement 1): 1906–1908.
https://doi.org/10.1182/blood-2022-166254
Published: 2022
Journal Articles

CRISPR/Cas9 Genome-Edited Autologous Hematopoietic Stem Cell Transplantation Therapies for Sickle Cell Disease

Free
Yi Liu, Vionnie W. Yu, Qi Zhang, Madhura Panditrao, Yi Yang, Alberto Del Rio-Espinola, Daher Ibrahim Aibo, Azeddine Elhajouji, Konrad Mueller, Karin Abitorabi, Daniel O'Connell, Bo Han, Nishit Patel, Carsten Russ, Craig Mickanin, Timothy K. MacLachlan, Susan C. Stevenson
Journal: Blood
Blood (2022) 140 (Supplement 1): 12982–12983.
https://doi.org/10.1182/blood-2022-159892
Published: 2022