Page 1 | Search Results | Blood | American Society of Hematology

1-17 of 17

Sort by

Sort Order Select

Journal Articles

Preliminary Results of a Phase 1/2 Clinical Study of Zinc Finger Nuclease-Mediated Editing of BCL11A in Autologous Hematopoietic Stem Cells for Transfusion-Dependent Beta Thalassemia

Angela R. Smith, MD MS, Gary J. Schiller, MD, Gregory M Vercellotti, MD, Janet L. Kwiatkowski, MD MSCE, Lakshmanan Krishnamurti, MD, Erica B. Esrick, MD, David A. Williams, MD, Weston P. Miller, MD, Adrian Woolfson, MD PhD, Mark C. Walters, MD

Blood (2019) 134 (Supplement_1): 3544.

https://doi.org/10.1182/blood-2019-125743

Published: 2019

Journal Articles

Successful donor engraftment and repair of the blood-brain barrier in cerebral adrenoleukodystrophy

Paul J. Orchard, David R. Nascene, Weston P. Miller, Ashish Gupta, Dan Kenney-Jung, Troy C. Lund

Blood (2019) 133 (12): 1378–1381.

https://doi.org/10.1182/blood-2018-11-887240

Published: 2019

Includes: Supplemental data

Journal Articles

Immune Mediated Cytopenias Following Allogeneic Hematopoietic Cell Transplantation for Non-Malignant Disease: Risk Factors and Treatment Response in the Pediatric Population

Robert T. Galvin, MD, Qing Cao, MS, Weston P. Miller, MD, Angela R. Smith, MD MS, Christen L. Ebens, MD MPH

Blood (2018) 132 (Supplement 1): 3377.

https://doi.org/10.1182/blood-2018-99-117718

Published: 2018

Journal Articles

Reduced Toxicity Conditioning Is Better Tolerated but Has Higher Graft Failure Compared to Myeloablative Conditioning in Children with Inherited Metabolic Disorders

Michael Downey, BA, Ashish O. Gupta, MBBS, MPH, Ryan Shanley, M.S, Weston P. Miller, MD, Paul Orchard, MD, Angela R. Smith, MD MS

Blood (2018) 132 (Supplement 1): 3352.

https://doi.org/10.1182/blood-2018-99-117573

Published: 2018

Journal Articles

Repair of the Blood Brain Barrier and Neutrophil Recovery Following HSCT in Cerebral Adrenoleukodystrophy

Troy C Lund, MDMS, PhD, Weston P. Miller, MD, Dave Nascene, MD, Paul Orchard, MD, Ashish O. Gupta, MBBS, MPH

Blood (2018) 132 (Supplement 1): 4628.

https://doi.org/10.1182/blood-2018-99-109801

Published: 2018

Journal Articles

The Changing Patterns of Graft Failure in MPS1H, Hurler Syndrome: A Review of 30-Years Experience

Su Han Lum, Weston P Miller, Simon Jones, Jean Mercer, Troy Lund, Denise Bonney, Paul J Orchard, Robert Wynn

Blood (2016) 128 (22): 4700.

https://doi.org/10.1182/blood.V128.22.4700.4700

Published: 2016

Journal Articles

Neurocognitive Trajectory of Patients with Childhood Cerebral Adrenoleukodystrophy Who Received Allogeneic Hematopoietic Cell Transplantation at an Early Stage of Cerebral Disease

Elizabeth Pierpont, PhD, Julie Eisengart, PhD, Richard Ziegler, PhD, Gerald Raymond, Paul J Orchard, Troy Lund, Weston P Miller

Blood (2016) 128 (22): 4682.

https://doi.org/10.1182/blood.V128.22.4682.4682

Published: 2016

Journal Articles

High-Exposure, Targeted Daily Busulfan and Fludarabine-Based Conditioning for Children Undergoing Hematopoietic Stem Cell Transplantation for Inherited Metabolic Disorders: Outcomes at a Single Center

Weston P Miller, Melisa Kay Stricherz, PharmD, Cathryn Jennissen, PharmD, Nicole Sando, Jennifer Danielson, Troy Lund, Paul J Orchard

Blood (2016) 128 (22): 2191.

https://doi.org/10.1182/blood.V128.22.2191.2191

Published: 2016

Journal Articles

Patient and Parental Perspectives on Long-Term Adaptive, Behavioral and Functional Outcomes Following Allogeneic Hematopoietic Cell Transplantation for Inherited Metabolic Disorders

Rachel Phelan, MD MPH, Paul J Orchard, MD, Margaret Semrud-Clikeman, PhD, Nicholas Smiley, Weston P Miller, IV, MD

Blood (2015) 126 (23): 4351.

https://doi.org/10.1182/blood.V126.23.4351.4351

Published: 2015

Journal Articles

The Impact of Graft/Recipient ABO Compatibility on Outcomes after Umbilical Cord Blood Transplant for Non-Malignant Disease

Matthew R Kudek, MD, Ryan Shanley, MS, Nicole D. Zantek, MD, PhD, Angela R. Smith, MD MS, Weston P Miller, IV, MD

Blood (2015) 126 (23): 4369.

https://doi.org/10.1182/blood.V126.23.4369.4369

Published: 2015

Journal Articles

Outcomes after Donor Lymphocyte Infusion for Insufficient Donor Chimerism Following Hematopoietic Cell Transplantation for Non-Malignant Disorders

Carter Biewen, BA, Angela R Smith, MD MS, Jakub Tolar, MD, PhD, Weston P Miller, IV, MD

Blood (2015) 126 (23): 1969.

https://doi.org/10.1182/blood.V126.23.1969.1969

Published: 2015

Journal Articles

Outcomes Following Allogeneic Hematopoietic Stem Cell Transplantation For Metachromatic Leukodystrophy

Alexander A Boucher, MD, Gerald V Raymond, MD, Ryan Shanley, Paul J Orchard, MD, Weston P Miller, IV, MD

Blood (2013) 122 (21): 714.

https://doi.org/10.1182/blood.V122.21.714.714

Published: 2013

Journal Articles

Cardiac QTc Interval Characteristics and Behavior in 995 Consecutive Hematopoietic Cell Transplantation Patients At a Single Institution

Weston P Miller IV, MD, Ryan Shanley, MS, Parvin Dorostkar, MD

Blood (2011) 118 (21): 1967.

https://doi.org/10.1182/blood.V118.21.1967.1967

Published: 2011

Journal Articles

Outcomes after allogeneic hematopoietic cell transplantation for childhood cerebral adrenoleukodystrophy: the largest single-institution cohort report

Weston P. Miller, Steven M. Rothman, David Nascene, Teresa Kivisto, Todd E. DeFor, Richard S. Ziegler, Julie Eisengart, Kara Leiser, Gerald Raymond, Troy C. Lund, Jakub Tolar, Paul J. Orchard

Blood (2011) 118 (7): 1971–1978.

https://doi.org/10.1182/blood-2011-01-329235

Published: 2011

Journal Articles

GVHD after haploidentical transplantation: a novel, MHC-defined rhesus macaque model identifies CD28 − CD8 + T cells as a reservoir of breakthrough T-cell proliferation during costimulation blockade and sirolimus-based immunosuppression

Blood (2010) 116 (24): 5403–5418.

https://doi.org/10.1182/blood-2010-06-289272

Published: 2010

Includes: Supplemental data

Journal Articles

Outcomes Following Allogeneic Hematopoietic Stem Cell Transplantation for Childhood Cerebral Variant Adrenoleukodystrophy: A Modern, Single-Institution Experience

Weston P Miller, IV, MD, Steven Rothman, MD, David Nascene, MD, Teresa Kivisto, RN, Todd Defor, Troy Lund, MD, PhD, Jakub Tolar, MD, PhD, Paul Orchard, MD

Blood (2010) 116 (21): 3543.

https://doi.org/10.1182/blood.V116.21.3543.3543

Published: 2010

Journal Articles

GvHD After Haploidentical Transplant: A Novel, MHC-Defined Rhesus Macaque Model Identifies CD28-Negative CD8+ T Cells as a Reservoir of Breakthrough T Cell Proliferation During Costimulation Blockade and Sirolimus-Based Immunosuppression

Swetha Srinivasan, Weston P. Miller IV, MD, Angela Panoskalltsis-Mortari, Sharon Sen, Kelly Hamby, Taylor Deane, Linda Stempora, Karnail Singh, Jonathan Beus, Bruce R. Blazar, MD, Leslie Kean, MD, PhD

Blood (2010) 116 (21): 2550.

https://doi.org/10.1182/blood.V116.21.2550.2550

Published: 2010

NARROW

Preliminary Results of a Phase 1/2 Clinical Study of Zinc Finger Nuclease-Mediated Editing of BCL11A in Autologous Hematopoietic Stem Cells for Transfusion-Dependent Beta Thalassemia

Successful donor engraftment and repair of the blood-brain barrier in cerebral adrenoleukodystrophy

Immune Mediated Cytopenias Following Allogeneic Hematopoietic Cell Transplantation for Non-Malignant Disease: Risk Factors and Treatment Response in the Pediatric Population

Reduced Toxicity Conditioning Is Better Tolerated but Has Higher Graft Failure Compared to Myeloablative Conditioning in Children with Inherited Metabolic Disorders

Repair of the Blood Brain Barrier and Neutrophil Recovery Following HSCT in Cerebral Adrenoleukodystrophy

The Changing Patterns of Graft Failure in MPS1H, Hurler Syndrome: A Review of 30-Years Experience

Neurocognitive Trajectory of Patients with Childhood Cerebral Adrenoleukodystrophy Who Received Allogeneic Hematopoietic Cell Transplantation at an Early Stage of Cerebral Disease

High-Exposure, Targeted Daily Busulfan and Fludarabine-Based Conditioning for Children Undergoing Hematopoietic Stem Cell Transplantation for Inherited Metabolic Disorders: Outcomes at a Single Center

Patient and Parental Perspectives on Long-Term Adaptive, Behavioral and Functional Outcomes Following Allogeneic Hematopoietic Cell Transplantation for Inherited Metabolic Disorders

The Impact of Graft/Recipient ABO Compatibility on Outcomes after Umbilical Cord Blood Transplant for Non-Malignant Disease

Outcomes after Donor Lymphocyte Infusion for Insufficient Donor Chimerism Following Hematopoietic Cell Transplantation for Non-Malignant Disorders

Outcomes Following Allogeneic Hematopoietic Stem Cell Transplantation For Metachromatic Leukodystrophy

Cardiac QTc Interval Characteristics and Behavior in 995 Consecutive Hematopoietic Cell Transplantation Patients At a Single Institution

Outcomes after allogeneic hematopoietic cell transplantation for childhood cerebral adrenoleukodystrophy: the largest single-institution cohort report

GVHD after haploidentical transplantation: a novel, MHC-defined rhesus macaque model identifies CD28 − CD8 + T cells as a reservoir of breakthrough T-cell proliferation during costimulation blockade and sirolimus-based immunosuppression

Outcomes Following Allogeneic Hematopoietic Stem Cell Transplantation for Childhood Cerebral Variant Adrenoleukodystrophy: A Modern, Single-Institution Experience

GvHD After Haploidentical Transplant: A Novel, MHC-Defined Rhesus Macaque Model Identifies CD28-Negative CD8+ T Cells as a Reservoir of Breakthrough T Cell Proliferation During Costimulation Blockade and Sirolimus-Based Immunosuppression

Email alerts

ASH Publications

American Society of Hematology

Email alerts

ASH Publications

American Society of Hematology

This Feature Is Available To Subscribers Only