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Research Article May 7 2025
Augmented CD47 expression impairs alloreactive T-cell clearance after allo-HCT
Cindy Sheree Flamann,Haroon Shaikh,Carina Matos,Marina Kreutz,Hla Ali,Michael AG Kern,Maike Büttner-Herold,Benedikt Jacobs,Simon Völkl,Christopher Lischer,Christian Kellner,Johannes Berges,Katrin Bitterer,Domenica Saul,Manisha Goel,Cornelia Link-Rachner,Alma Zernecke,Daniela Andrea Weber,Dimitrios Mougiakakos,Andreas Mackensen,Andreas Beilhack,Heiko Bruns
Research Article May 7 2025
BLAST: A Globally Applicable and Molecularly Versatile Survival Model for Chronic Myelomonocytic Leukemia
Ayalew Tefferi,Saubia Fathima,Maymona Abdelmagid,Ali Alsugair,Fnu Aperna,Mahsa Rezasoltani,Muhammad Yousuf,Anuya Natu,Clifford M Csizmar,Mark Gurney,Terra L Lasho,Christy M. Finke,Rashmi Kanagal-Shamanna,Danielle Hammond,Kelly Sharon Chien,Alexandre Bazinet,Courtney D. DiNardo,Tapan M. Kadia,Abhishek A. Mangaonkar,Naval G. Daver,Animesh D Pardanani,Gautam Borthakur,Cinthya J Zepeda-Mendoza,Kaaren K Reichard,Rong He,Sanam Loghavi,Francesco Passamonti,Farhad Ravandi,Koji Sasaki,Dirk Larson,Guillermo Garcia-Manero,Francesco Onida,Naseema Gangat,Guillermo Montalban-Bravo,Mrinal M. Patnaik
Research Article May 7 2025
A multiomic analysis of Waldenström macroglobulinemia defines distinct disease subtypes
Dylan C Gagler,Hussein Ghamlouch,Di Zhang,Patrick Blaney,Avital Tenenbaum,James Blake Langton,Marine Armand,Alexandre Eeckhoutte,Amina Joudat,Michaël Degaud,Michela Esposito,Gaurav Varma,Yubao Wang,Sanghoon Lee,Sanxiong Liu,Oscar B Lahoud,David Kaminetzky,Marc J. Braunstein,Louis Williams,Florence Nguyen-Khac,Brian A Walker,Damien Roos-Weil,Faith E Davies,Olivier A Bernard,Gareth J Morgan
Research Article April 29 2025
The mitochondrial protease ClpP is a metabolic vulnerability and an immunogenic trigger against multiple myeloma.
Tommaso Perini,Paola Zordan,Rossella Del Pizzo,Massimo Resnati,Lisa Viviani,Davide Stefanoni,Laura Cassina,Ugo Paolo Orfanelli,Matteo Trudu,laura oliva,Daniel Lacidogna,Mehmet K. Samur,Maria Materozzi,Denise Drago,Annapaola Andolfo,Marco Patrone,Massimo Degano,Alessandra Boletta,Enrico Milan,Fabio Ciceri,Nikhil C. Munshi,Matteo Bellone,Simone Cenci, MD
Research Article April 29 2025
High Incidence of Severe TA-TMA Increases Mortality in adult Allogeneic Transplant recipients: A prospective MIDAS Consortium study
Research Article April 25 2025
Expansions of circulating plasmablasts producing commensal-reactive IgA antibodies are predictors for chronic GVHD
Katharina Marie Habenicht,Jana Wanzek,Anna Bootz,Simon Schäfer,Lara Vollmer,Andreas Hiergeist,Matthias Alexander Fante,Jakob Thomas Hasenbank,Andrea Schneider,Ingrid Vasova,Silvia Spoerl,Anna Brandt,Michael Rehli,Petra Hoffmann,Stefan Wirtz,Jesika Kotorri,Roman G Gerlach,André Gessner,Andreas Mackensen,Julia Winkler,Daniel Wolff,Thomas H Winkler
Research Article April 25 2025
Genome-wide Meta-Analysis of Heavy Menstrual Bleeding Reveals 36 Risk Loci
Research Article April 25 2025
A Novel Mouse Model of Hemoglobin SC Disease Reveals Mechanisms Underlying Beneficial Effects of Hydroxyurea
Research Article April 25 2025
A phase 2 randomized study of modakafusp alfa as a single agent in patients with relapsed/refractory multiple myeloma
Sarah A Holstein,Shebli Atrash,Hira Mian,Meletios Athanasios Dimopoulos,Fredrik Schjesvold,Rakesh Popat,Nishi Shah,Moshe E Gatt,Christian B. Gocke,Laurent Frenzel,Cyrille Touzeau,Meral Beksac,Salomon Manier,Hila Magen,Patrick Travis,Omar Nadeem,Kaveri Suryanarayan,Cheryl Li,Shuli Li,Allison Nelson,Dasha Cherepanov,Xavier Parot,Dan T Vogl
Research Article April 25 2025
Clinical phenotype and pathophysiological mechanisms underlying qualitative Low VWF
Ferdows Atiq,Robin Blok,Calvin van Kwawegen,Anne-Marije Hulshof,Dearbhla Doherty,Michelle Lavin,Johanna G van der Bom,Niamh M O'Connell,Joke de Meris,Kevin Ryan,Saskia E.M. Schols,Waander L. van Heerde,Mairead M Doyle,Mary B Byrne,Floor C.J.I. Heubel-Moenen,Karin P.M. van Galen,Roger J.S. Preston,Marjon H. Cnossen,Karin Fijnvandraat, Prof,Ross Ian Baker,Karina Meijer,Paula D. James,Jorge Di Paola,Jeroen C.J. Eikenboom,Frank W.G. Leebeek,James S. O'Donnell
Research Article April 21 2025
Heterogeneity of high-potency multilineage hematopoietic stem cells and identification of 'Super' transplantability
Research Article April 21 2025
T-ICAHT: Grading and Prognostic Impact of Thrombocytopenia After CAR T-cell Therapy
Kai Rejeski,Jaime Sanz,Teng Fei,Monica S Nair,Hamza Hashmi,Abraham Avigdor,Ofrat Beyar-Katz,Veit L. Bücklein,Kevin J. Curran,Sigrun Einarsdottir,Jonathan H Esensten,Netta Glaubach, Dr,Noa Golan-Accav,Marina Gomez-Llobell,Iris Halamis,Orit Itzhaki,Frederick L. Locke,Sham Mailankody,Ronit Marcus,Marcela V. Maus,M. Lia Palomba,Jae H Park,Marcelo C. Pasquini,Sandeep S Raj,Sridevi Rajeeve,Gilles A. Salles,Michael Scordo,Gunjan L Shah,Avichai Shimoni,Marion Subklewe,Tobias Tix,Saad Z Usmani,Ori Ben Valid,Yannis K. Valtis,Tsila Zuckerman,Nirali N Shah,Miguel-Angel Perales,Roni Shouval
Research Article April 16 2025
Genotype-specific immune responses at the intestinal barrier predispose to colitis in chronic granulomatous disease in mice
Review Article April 16 2025
International Consensus Statement on Diagnosis, Evaluation, and Research of Richter Transformation: the ERIC Recommendations
Adam S Kittai,Monia Marchetti,Othman Al-Sawaf,Ohad Benjamini,Alexey V Danilov,Matthew S. Davids,Barbara F. Eichhorst,Toby A. Eyre,Anna Maria Frustaci,Michael J Hallek,Paul Joseph Hampel,Yair Herishanu,Rodney John Hicks,Arnon P. Kater,Rebecca L. King,José-Ignacio Ignacio Martín-Subero,Carolyn Owen,Erin M. Parry,Maurilio Ponzoni,Davide Rossi,Tanya Siddiqi,Stephan Stilgenbauer,Constantine S. Tam,Elisa ten Hacken,Philip A Thompson,William G. Wierda,Gianluca Gaidano,Jennifer A. Woyach,Paolo Ghia
Research Article April 15 2025
Outcomes of PLAT-02 and PLAT-03: Evaluating CD19 CAR T-Cell Therapy and CD19-expressing T-APC Support in Pediatric B-ALL
Research Article April 15 2025
The ENHANCE-3 study: venetoclax and azacitidine plus magrolimab or placebo for untreated AML unfit for intensive therapy
Naval G. Daver,Paresh Vyas,Gerwin A Huls,Hartmut Döhner,Sebastien Maury,Jan Novak,Cristina Papayannidis,Carmen Martinez Chamorro,Pau Montesinos,Rabin Niroula,Pierre Fenaux,Jordi Esteve,Shang-Ju Wu,Adrien De Voeght,Jiri Mayer,Peter J.M. Valk,Lisa Johnson,Mei Dong,Ke Liu,Sowmya Banda Kuwahara,Kenneth Caldwell,Guru Subramanian Guru Murthy
Research Article April 15 2025
HNRNPC and m6A RNA methylation control oncogenic transcription and metabolism in T-cell leukemia
Jonas De Kesel,Igor Fijalkowski,Tim Pieters,Cristina Borin,Kasper Thorhauge Christensen,Manou Wittouck,Jolien Van Laere,Laura Guerrero,Lindy Reunes,Marino Caruso,Bijal Thakkar,Wouter Sleeckx,Luyao Kevin Xu,Filip Van Nieuwerburgh,Dieter Deforce,Kim De Keersmaecker,Tim Lammens,Steven Goossens,Tom Taghon,Cuijuan Han,Giulia Veltri,Valentina Serafin,Bruno Palhais,Nitesh D. Sharma,Hao Huang,Hudan Liu,Ksenia Matlawska-Wasowska,Ana Milovanovic,Eva Maria Novoa,Eric Wang,Panagiotis Ntziachristos
Brief Report April 10 2025
ZUMA-8: A Phase 1 Study of Brexucabtagene Autoleucel in Patients With Relapsed/Refractory Chronic Lymphocytic Leukemia
Research Article April 10 2025
An unbiased genomewide screen uncovers 7 genes that drive hematopoietic stem cell fate from mouse embryonic stem cells
Research Article April 8 2025
A phase 1 trial of fully human BCMA CAR-T therapy for relapsed/refractory multiple myeloma with 5-year follow-up
Sherilyn A Tuazon,Andrew J. Portuguese,Margot J Pont,Andrew J Cowan,Gabriel O Cole,Blythe D Sather,Xiaoling Song,Sushma Thomas,Brent L. Wood,Michelle Lee Blake,Melissa G Works,Mazyar Shadman,Emily C. Liang,Qian Wu,Jenna M Voutsinas,Ted A Gooley,Cameron J Turtle,Brian G. Till,David G Coffey,David G Maloney,Stanley R. Riddell,Damian J Green
Research Article April 8 2025
Standard-of-Care Idecabtagene Vicleucel for Relapsed/Refractory Multiple Myeloma: A CIBMTR Analysis
Surbhi Sidana,Nausheen Ahmed,Othman Salim Akhtar,Ruta Brazauskas,Temitope Oloyede,Matthew Bye,Doris K Hansen,Christopher J Ferreri,Ciara L Freeman,Aimaz Afrough,Larry D. Anderson, Jr.,Binod Dhakal,Devender S. Dhanda,Lohith Gowda,Hamza Hashmi,Melanie J Harrison,Amani Kitali,Heather J Landau,Abu-sayeef Mirza,Pallavi Patwardhan,Muzaffar H Qazilbash,Saad Z Usmani,Krina K. Patel,Taiga Nishihori,Siddhartha Ganguly,Marcelo C. Pasquini
Research Article April 8 2025
Acalabrutinib-Obinutuzumab Improves Survival vs Chemoimmunotherapy in treatment-naive CLL in the 6-year Follow-up of ELEVATE-TN
Jeff P. Sharman,Miklos Egyed,Wojciech Jurczak,Alan P Skarbnik,Krish Patel,Ian W. Flinn,Manali Kamdar,Talha Munir,Renata Walewska,Marie Hughes,Laura Maria Fogliato,Yair Herishanu,Versha Banerji,George A. Follows,Patricia A Walker,Paolo Ghia,Ann MH Janssens,John C Byrd,Emmanuelle France Ferrant,Alessandra Ferrajoli,William G. Wierda,Catherine Wangui Wachira,Batul T. Suterwala,Paulo A Palhares de Miranda,Veerendra Munugalavadla,Chuan-Chuan Wun,Jennifer A. Woyach
Research Article April 7 2025
Project EVOLVE: An international analysis of postimmunotherapy lineage switch, an emergent form of relapse in leukemia
Sara K Silbert,Alexander W Rankin,Chloe N Hoang,Alexandra Semchenkova,Regina M Myers,Elena Zerkalenkova, PhD,Hao-Wei Wang,Alexandra E Kovach,Constance M Yuan,Dana Delgado Colon,Loic Vasseur,Alex Bataller,Samuel John,Kaylyn Utley Lyons,Barbara D. Friedes,Anna Alonso-Saladrigues,Hisham Abdel-Azim,Estelle Balducci,Ahmed Aljudi,Marie Balsat,D. Nathan Biery,Aghiad Chamdin,Bill H Chang,Raymund S Cuevo, MD,Barbara De Moerloose,David S. Dickens,Ulrich A Duffner,Nicolas Duployez,Firas El Chaer,Michelle Ann Elliott,Gabriele Escherich,Sneha Fernandes,Mandi R Fitzjohn,Zhubin J Gahvari,Stephan A. Grupp,Rui Rochelle He, M.D.,Cynthia Harrison,Christopher Bruce Hergott,Emily M. Hsieh,Annette S Kim,Dennis John Kuo,Daniel P Larson,Benjamin J Lee,Thibaut TL Leguay,R. Coleman Lindsley,Abhishek A. Mangaonkar,Kerstin Mezger,Holly L Pacenta,Jing Pan,Marlie R. M. Provost,Latika Puri,Sunil Sudhir Raikar,Armando Jose Martinez,Isabella Quijada Bristol,Kyle Daniel Murphy,Lauren Reiman,Michele S Redell,Kelly Reed,Gabrielle Roth Guepin,Jeremy D Rubinstein,Süreyya Savaşan,Kristian T Schafernak,Alexandra McLean Stevens,Aimee C Talleur,Naomi Torres Carapia,Jacques Vargaftig,Anant Vatsayan,Matthias Wölfl,Lipng Zhao,Susana Rives,Vanessa A. Fabrizio,Koji Sasaki,Ibrahim Aldoss,Nicolas Boissel,Susan R Rheingold,Kara L Davis,Sara Ghorashian,Elad Jacoby,Alexander Popov,Adam Joseph Lamble,Nirali N Shah
Research Article April 7 2025
Optimal MRD-based end point to support response-adapted treatment cessation in newly diagnosed multiple myeloma
Research Article April 1 2025
Diagnostic BRAFV600E blood predicts treatment failure and neurodegeneration and redefines paradigms of pediatric LCH
Howard Lin,Akanksha Batajoo,Erin Peckham-Gregory,Daniel Zinn,Olive S Eckstein,Nader K El-Mallawany,Nitya Gulati,Zachary Prudowsky,Brooks P. Scull,Jessica Velazquez,Harshal A Abhyankar,Stephen J Simko,Daria Vakula,Ryan Fleischmann,Vivekanudeep Karri,John Hicks,Kevin E. Fisher,Choladda V. Curry,Angshumoy Roy,Deborah E Schiff,Kenneth Heym,Michael E Scheurer,Donald Williams Parsons,Miriam Merad,Tsz-Kwong Man,Kenneth L McClain,Jennifer Picarsic,Carl E Allen
Research Article March 31 2025
Efficacy of a Novel BCL-xL Degrader, DT2216, in Preclinical Models of JAK2-mutated Post-MPN AML
Zhe Wang,Anna Skwarska,Gowri Poigaialwar,Sovira Chaudhry,Alba Rodriguez-Meira,Pinpin Sui,Emmanuel Olivier,Yannan Jia,Varun Gupta,Warren Fiskus,Cassandra L. Ramage,Guangrong Zheng,Alexandra Schurer,Kira Gritsman,Eirini P Papapetrou,Kapil N Bhalla,Daohong Zhou,Adam J. Mead,Raajit K. Rampal,Jeffrey W. Tyner,Hussein A. Abbas,Naveen Pemmaraju,Qi Zhang Tatarata,Marina Y. Konopleva
Research Article March 31 2025
Hallmarks of terminal T-cell exhaustion are absent in multiple myeloma from diagnosis through maintenance therapy
Research Article March 31 2025
IFN-γ promotes the progression of iMCD by activating inflammatory monocytes
Research Article March 27 2025
Use of machine learning techniques to predict poor survival after hematopoietic cell transplantation for myelofibrosis
Juan Carlos Hernandez-Boluda,Adrian Mosquera Orgueira, Dr,Luuk Gras,Linda Koster,Joe Tuffnell,Nicolaus Kröger,Massimiliano Gambella,Thomas Schroeder,Marie Robin,Katja Sockel,Jakob R Passweg,Igor Wolfgang Blau,Ibrahim Yakoub-Agha,Ruben Van Dijck,Matthias Stelljes,Henrik Sengeloev,Jan Vydra,Uwe Platzbecker,Moniek Dewitte,Frédéric Baron,Kristina Carlson,Javier Alberto Rojas Martínez,Carlos Pérez Míguez,Davide Crucitti,Kavita Raj,Joanna Drozd-Sokolowska,Giorgia Battipaglia,Nicola Polverelli,Tomasz Czerw,Donal P McLornan
Research Article March 25 2025
Tracking clusterin expression in hematopoietic stem cells reveals their heterogeneous composition across the lifespan
Shuhei Koide,Motohiko Oshima,Takahiro Kamiya,Zhiqian Zheng,Zhaoyi Liu,Ola Rizq,Akira Nishiyama,Koichi Murakami,Yuta Yamada,Yaeko Nakajima-Takagi,Bahityar Rahmutulla,Atsushi Kaneda,Kazuaki Yokoyama,Nozomi Yusa,Seiya Imoto,Fumihito Miura,Takashi Ito,Tomohiko Tamura,Claus Nerlov,Masayuki Yamashita,Atsushi Iwama
Brief Report March 25 2025
NGS-based IG/TR rearrangement profiling in acute lymphoblastic leukemia: age dependence of immunogenetic maturation
Michaela Kotrova,Constantin Proske,Nikos Darzentas,Anna Laqua,Britta Kehden,Jan Christian Kässens,Sonja Bendig,Saskia Kohlscheen,Monika Szczepanowski,Wiebke Wessels,Željko Antić,Christiane Pott,Matthias Ritgen,Jacques J.M. van Dongen,Nicola Gökbuget,Guranda Chitadze,Anke Bergmann,Lorenz Bastian,Claudia D. Baldus,Gunnar Cario,Martin Schrappe,Stefan Schwartz,Julia Alten,Rolf Koehler,Monika Brüggemann
Research Article March 24 2025
Daratumumab-Bortezomib-Thalidomide-Dexamethasone for Newly Diagnosed Myeloma: CASSIOPEIA Minimal Residual Disease Results
Jill Corre,Laure Vincent,Philippe Moreau,Benjamin Hebraud,Cyrille Hulin,Marie-Christine Béné,Annemiek Broijl,Denis Caillot,Michel Delforge,Thomas Dejoie,Thierry Facon,Jerome Lambert,Xavier Leleu,Margaret Macro, Dr,Aurore Perrot,Sonja Zweegman,Thomas Filleron,Bastien Cabarrou,Niels W.C.J. van de Donk,Sabrina Mahéo,Winnie Hua,Jianping Wang,Maria Krevvata,Véronique Vanquickelberghe,Carla de Boer,Alba Tuozzo,Fredrik Borgsten,Melissa Rowe,Robin Carson,Soraya Wuilleme,Pieter Sonneveld
Research Article March 20 2025
Clonal hematopoiesis is clonally unrelated to multiple myeloma and is associated with specific microenvironmental changes
Marta Lionetti,Margherita Scopetti,Antonio Matera,Akihiro Maeda,Alessio Marella,Francesca Lazzaroni,Giancarlo Castellano,Sonia Fabris,Stefania Pioggia,Silvia Lonati,Alfredo Marchetti,Alessandra Cattaneo,Marta Tornese,Antonino Neri, Dr,Claudia Leoni,Loredana Pettine,Valentina Traini,Ilaria Silvestris,Marzia Barbieri,Giuseppina Fabbiano,Domenica Ronchetti,Elisa Taiana,Claudio De Magistris,Matteo Claudio Da Via',Francesco Passamonti,Niccolò Bolli
Research Article March 19 2025
NKG2D-mediated cytotoxicity of CD4 cytotoxic T cells in multiple myeloma
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